Preclinical protocol for in vivo selection of hematopoietic stem cells corrected by gene therapy in fanconi anemia group C

Molecular Therapy

Volumn 3, Issue 1, 2001, Pages 14-23

  Noll, Meenakshi ^a   Bateman, Raynard L ^a   D'Andrea, Alan D ^b   Grompe, Markus ^a  

^a OREGON HEALTH AND SCIENCE UNIVERSITY   (United States)

^b HARVARD MEDICAL SCHOOL   (United States)

Author keywords

Cyclophosphamide; Fanconi anemia; Gene therapy; Hematopoietic cells; Retroviral vector; irradiation

Indexed keywords

CYCLOPHOSPHAMIDE; DNA; MITOMYCIN C;

ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; AUTOSOMAL RECESSIVE DISORDER; BIRTH DEFECT; BONE MARROW DEPRESSION; BONE MARROW TRANSPLANTATION; CELL MUTANT; CELL SELECTION; CLINICAL PROTOCOL; CONTROLLED STUDY; DNA CROSS LINKING; DOSE RESPONSE; FANCONI ANEMIA; FEMALE; GAMMA IRRADIATION; GENE THERAPY; HEMATOPOIETIC STEM CELL; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HYPERSENSITIVITY; IN VIVO STUDY; INCIDENCE; KNOCKOUT MOUSE; MALE; MALIGNANT NEOPLASTIC DISEASE; MOUSE; NONHUMAN; RETROVIRUS; TOXICITY;

ANIMALIA; UNIDENTIFIED RETROVIRUS;

EID: 0034981121     PISSN: 15250016     EISSN: None     Source Type: Journal    
DOI: 10.1006/mthe.2000.0226     Document Type: Article

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