Therapeutic hepatocyte transplant for inherited metabolic disorders: Functional considerations, recent outcomes and future prospects

Journal of Inherited Metabolic Disease

Volumn 37, Issue 2, 2014, Pages 165-176

  Vogel, Kara R ^a   Kennedy, Andrew A ^b   Whitehouse, Luke A ^b   Gibson, K Michael ^a  

^a WASHINGTON STATE UNIVERSITY   (United States)

^b MICHIGAN TECHNOLOGICAL UNIVERSITY   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

AMMONIA; APOLIPOPROTEIN B100; BILE SALT EXPORT PUMP; BILIRUBIN; COPPER EXPORTING ADENOSINE TRIPHOSPHATASE; GLYCOPROTEIN; LONG CHAIN FATTY ACID; LOW DENSITY LIPOPROTEIN RECEPTOR; NITISINONE; PHENOPTIN'; PHENYLALANINE; PHENYLALANINE AMMONIA LYASE; SAPROPTERIN; TYROSINE; UNCLASSIFIED DRUG;

BILIRUBIN BLOOD LEVEL; BIOGENESIS; BLOOD TRANSFUSION; CELL EXPANSION; CHOLESTEROL BLOOD LEVEL; CRIGLER NAJJAR SYNDROME; DIET SUPPLEMENTATION; ENGRAFTMENT; FAMILIAL HYPERCHOLESTEROLEMIA; GENE MUTATION; GENETIC DISORDER; GLYCOGEN STORAGE DISEASE TYPE 1; GUNN RAT; HEPATOCYTE TRANSPLANTATION; HUMAN; HYPERAMMONEMIA; IMMUNOSUPPRESSIVE TREATMENT; INHERITED METABOLIC DISEASE; INTRAHEPATIC CHOLESTASIS; LIVER TRANSPLANTATION; LOBECTOMY; LONG EVANS CINNAMON RAT; MAPLE SYRUP URINE DISEASE; METABOLIC DISORDER; NONHUMAN; OLIGODENDROGLIA; ORNITHINE TRANSCARBAMYLASE DEFICIENCY; OUTCOME ASSESSMENT; OXALOSIS 1; PEROXISOME; PHENYLKETONURIA; PHOTOTHERAPY; PROGRESSIVE FAMILIAL INTRAHEPATIC CHOLESTASIS; PROTEIN INTAKE; PROTEIN RESTRICTION; REFSUM DISEASE; REVIEW; TYROSINEMIA; TYROSINEMIA TYPE I; UREA BLOOD LEVEL; UREA CYCLE DISORDER; WATANABE HERITABLE HYPERLIPIDEMIC RABBIT; WILSON DISEASE; ANIMAL; LIVER CELL; LIVER DISEASES; METABOLIC DISEASES; PHYSIOLOGY; TRANSPLANTATION;

ANIMALS; HEPATOCYTES; HUMANS; LIVER DISEASES; METABOLIC DISEASES; TRANSPLANTS;

EID: 84922481376     PISSN: 01418955     EISSN: 15732665     Source Type: Journal    
DOI: 10.1007/s10545-013-9656-5     Document Type: Review

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