Clinical outcome of hepatocyte transplantation in four pediatric patients with inherited metabolic diseases

Cell Transplantation

Volumn 21, Issue 10, 2012, Pages 2267-2282

  Ribes Koninckx, Carmen ^a,b   Ibars, Eugenia Pareja ^b   Agrasot, Maria Ángeles Calzado ^a,b   Bonora Centelles, Ana ^b   Miquel, Begoña Polo ^a   Carbó, Juan José Vila ^b   Aliaga, Ester Donat ^a   Pallardó, Jose Mir ^b   Gómez Lechón, Maria José ^b,c   Castell, Jose V ^b,c,d  

^a INSTITUTO DE INVESTIGACIÓN SANITARIA DEL HOSPITAL CLÍNICO SAN CARLOS IDISSC   (Spain)

^b HOSPITAL UNIVERSITARIO LA FE   (Spain)

^c INSTITUTO DE SALUD CARLOS III   (Spain)

^d UNIVERSITY OF VALENCIA   (Spain)

Author keywords

Crigler najjar (CNI) syndrome; Cryopreservation; Glycogen storage disease Ia (GSD Ia); Hepatocyte transplantation (HT); Human hepatocytes; Inherited metabolic diseases; Ornithine transcarbamylase (OTC) deficiency; Pediatrics; Tyrosinemia type I (TYR I)

Indexed keywords

4 PHENYLBUTYRIC ACID; AMINO ACID; AMMONIA; ANTIBIOTIC AGENT; ARGININE; BILIRUBIN; BLOOD CLOTTING FACTOR 5; BLOOD CLOTTING FACTOR 7; CHOLESTEROL; CYANOCOBALAMIN; CYTOCHROME P450; FOLIC ACID; FRESH FROZEN PLASMA; FRUCTOSE; GLUCOSE; GLUCOSE 6 PHOSPHATASE; GLUCURONOSYLTRANSFERASE 1A1; HYDROCORTISONE; LACTIC ACID; LACTOSE; METHYLPREDNISOLONE; NITISINONE; PHENYLALANINE; TACROLIMUS; TRIACYLGLYCEROL; TYROSINE; UREA; VITAMIN K GROUP;

ADOLESCENT; ADULT; AGED; AMINO ACID BLOOD LEVEL; AMMONIA BLOOD LEVEL; ANTIBIOTIC PROPHYLAXIS; ARTICLE; ASCITES; ASPERGILLOSIS; BILIRUBIN BLOOD LEVEL; BLOOD CLOTTING; CELL ADHESION; CELL FUNCTION; CELL VIABILITY; CHEMICAL PARAMETERS; CHILD; CLINICAL ARTICLE; CLINICAL FEATURE; CONTROLLED STUDY; CRIGLER NAJJAR SYNDROME; CRYOPRESERVATION; DIET THERAPY; DISEASE SEVERITY; ECHOGRAPHY; ENGRAFTMENT; ENZYME ACTIVITY; FEMALE; FOLLOW UP; GENE MUTATION; GENETIC ANALYSIS; GLUCOSE BLOOD LEVEL; GLYCOGEN STORAGE DISEASE TYPE 1; HEMANGIOMA; HEPATOCYTE TRANSPLANTATION; HISTOPATHOLOGY; HOSPITAL INFECTION; HUMAN; HUMAN TISSUE; HYPERBILIRUBINEMIA; HYPERTRIGLYCERIDEMIA; HYPERURICEMIA; HYPOCOAGULABILITY; HYPOGLYCEMIA; IMMUNOSUPPRESSIVE TREATMENT; INBORN ERROR OF METABOLISM; INFANT; INFUSION; JAUNDICE; KERNICTERUS; LACTIC ACIDOSIS; LIVER CELL; MALE; METABOLIC REGULATION; MICROBIOLOGICAL PARAMETERS; MORTALITY; MUSCLE HYPOTONIA; MYCOSIS; NOSE FEEDING; NUCLEAR MAGNETIC RESONANCE IMAGING; ORNITHINE TRANSCARBAMYLASE DEFICIENCY; OUTCOME ASSESSMENT; PEDIATRIC SURGERY; PHOTOTHERAPY; PORTAL VEIN; PORTAL VEIN BLOOD FLOW; PRIORITY JOURNAL; QUALITY OF LIFE; SAFETY; SCHOOL CHILD; SEPSIS; SEPTIC SHOCK; SPASTICITY; TYROSINEMIA; UREA CYCLE; UREA CYCLE DISORDER; URINE LEVEL;

ADOLESCENT; ADULT; AGED, 80 AND OVER; CELL TRANSPLANTATION; CRYOPRESERVATION; FEMALE; HEPATOCYTES; HUMANS; LIVER; LIVER TRANSPLANTATION; MALE; METABOLIC DISEASES; MIDDLE AGED; TREATMENT OUTCOME; YOUNG ADULT;

FUNGI;

EID: 84870434016     PISSN: 09636897     EISSN: None     Source Type: Journal    
DOI: 10.3727/096368912X637505     Document Type: Article

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