Lentivirus vectors in β-Thalassemia

Methods in Enzymology

Volumn 507, Issue , 2012, Pages 109-124

  Payen, Emmanuel ^a,b   Colomb, Charlotte ^a,b   Negre, Olivier ^a,b,c,d   Beuzard, Yves ^a,b,c,d   Hehir, Kathleen ^c,d   Leboulch, Philippe ^a,b,e  

^a INSTITUT DE RADIOPROTECTION ET DE SÛRETÉ NUCLÉAIRE   (France)

^b Institute of Emerging Diseases and Innovative Therapies   (France)

^c BLUEBIRD BIO   (United States)

^d CEA   (France)

^e BRIGHAM AND WOMEN S HOSPITAL   (United States)

Author keywords

beta thalassemia; clinical trial; gene therapy; lentiviral vector

Indexed keywords

BETA GLOBIN; BETA GLOBIN LENTIVIRUS VECTOR; CYCLIC GMP; GUANOSINE TRIPHOSPHATE; IRON CHELATING AGENT; LENTIGLOBIN; LENTIVIRUS VECTOR; UNCLASSIFIED DRUG;

ALLOGENEIC HEMATOPOIETIC STEM CELL TRANSPLANTATION; ARTICLE; BETA THALASSEMIA; BLOOD TRANSFUSION; CD34 SELECTION; CLINICAL PROTOCOL; DRUG DESIGN; EX VIVO GENE TRANSFER; FOLLOW UP; GENE EXPRESSION; GLOBIN GENE; GRAFT VERSUS HOST REACTION; HUMAN; NONHUMAN; OUTCOME ASSESSMENT; PATIENT SELECTION; PRIORITY JOURNAL; REGULATORY DNA SEQUENCE; VIRAL GENE DELIVERY SYSTEM;

LENTIVIRUS; LONCHOCARPUS GLAUCIFOLIUS;

EID: 84857588294     PISSN: 00766879     EISSN: 15577988     Source Type: Book Series    
DOI: 10.1016/B978-0-12-386509-0.00006-5     Document Type: Chapter

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