Improved Human β-globin expression from self-inactivating lentiviral vectors carrying the chicken hypersensitive site-4 (cHS4) insulator element

Molecular Therapy

Volumn 15, Issue 10, 2007, Pages 1863-1871

  Arumugam, Paritha I ^a   Scholes, Jessica ^a   Perelman, Natalya ^a   Xia, Ping ^a   Yee, Jiing Kuan ^b   Malik, Punam ^a,c,d  

^a CHILDREN S HOSPITAL LOS ANGELES   (United States)

^b CITY OF HOPE NATIONAL MEDICAL CENTER   (United States)

^c UNIVERSITY OF SOUTHERN CALIFORNIA   (United States)

^d CINCINNATI CHILDREN'S HOSPITAL MEDICAL CENTER   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

BETA GLOBULIN; CHICKEN HYPERSENSITIVE SITE 4; LENTIVIRUS VECTOR; UNCLASSIFIED DRUG;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; CELL CLONING; CELL COUNT; CONTROLLED STUDY; ERYTHROCYTE; EXPRESSION VECTOR; FEMALE; GENE THERAPY; HEMATOPOIETIC STEM CELL; HEMOGLOBINOPATHY; IN VIVO STUDY; INSULATOR ELEMENT; LEUKEMIA CELL; MOUSE; NONHUMAN; POSITION EFFECT VARIEGATION; PROBABILITY; PROGENY; THALASSEMIA MAJOR; VIRAL GENE DELIVERY SYSTEM;

ANIMALS; BASE SEQUENCE; CHICKENS; DNA PRIMERS; GENETIC VECTORS; GLOBINS; HUMANS; LENTIVIRUS; POLYMERASE CHAIN REACTION; RNA, MESSENGER;

MURINAE; MUS;

EID: 34548791721     PISSN: 15250016     EISSN: 15250024     Source Type: Journal    
DOI: 10.1038/sj.mt.6300259     Document Type: Article

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