Therapeutic haemoglobin synthesis in β-thalassaemic mice expressing lentivirus-encoded human β-globin

Nature

Volumn 406, Issue 6791, 2000, Pages 82-86

  Chad, May ^a,b   Rivella, Stefano ^a   Callegari, John ^a   Heller, Glenn ^a   Gaensler, Karen M L ^c   Luzzatto, Lucio ^a   Sadelain, Michel ^a,b  

^a MEMORIAL SLOAN KETTERING CANCER CENTER   (United States)

^b Weill Cornell Graduate School of Biomedical Sciences   (United States)

^c UNIVERSITY OF CALIFORNIA   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

BETA GLOBULIN;

ANIMAL CELL; ARTICLE; BETA THALASSEMIA; HEMOGLOBIN SYNTHESIS; LENTIVIRINAE; MOUSE; NONHUMAN; PRIORITY JOURNAL; PROTEIN EXPRESSION; SICKLE CELL ANEMIA;

ANIMALS; BETA-THALASSEMIA; BONE MARROW TRANSPLANTATION; CELL LINE; FEMALE; GENE THERAPY; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; GLOBINS; HEMOGLOBINS; HIV-1; HUMANS; LENTIVIRUS; MALE; MICE; RECOMBINANT PROTEINS; TRANSDUCTION, GENETIC;

ANIMALIA; LENTIVIRUS; MURINAE;

EID: 0343628721     PISSN: 00280836     EISSN: None     Source Type: Journal    
DOI: 10.1038/35017565     Document Type: Article

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