Extended β-globin locus control region elements promote consistent therapeutic expression of a γ-globin lentiviral vector in murine β-thalassemia

Blood

Volumn 104, Issue 8, 2004, Pages 2281-2290

  Hanawa, Hideki ^b   Hargrove, Phillip W ^b   Kepes, Steven ^b   Srivastava, Deo K ^b   Nienhuis, Arthur W ^b   Persons, Derek A ^a  

^a ST JUDE CHILDREN S RESEARCH HOSPITAL   (United States)

^b NONE

Author keywords

[No Author keywords available]

Indexed keywords

BETA GLOBIN; GAMMA GLOBIN; HEMOGLOBIN; HEMOGLOBIN F; LENTIVIRUS VECTOR;

ANIMAL CELL; ARTICLE; AUTOLOGOUS HEMATOPOIETIC STEM CELL TRANSPLANTATION; BETA THALASSEMIA; COLONY FORMING UNIT S; CONTROLLED STUDY; DNA SEQUENCE; ERYTHROID CELL; FLUORESCENCE ACTIVATED CELL SORTING; GENE TRANSFER; GLOBIN GENE; NONHUMAN; NORTHERN BLOTTING; NUCLEOTIDE SEQUENCE; POLYADENYLATION; POLYMERASE CHAIN REACTION; POSITION EFFECT; PRIORITY JOURNAL; PROMOTER REGION; RAT; REGULATOR GENE; SICKLE CELL ANEMIA;

EID: 4944234406     PISSN: 00064971     EISSN: None     Source Type: Journal    
DOI: 10.1182/blood-2004-03-0863     Document Type: Article

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