AAV vectors for cardiac gene transfer: Experimental tools and clinical opportunities

Molecular Therapy

Volumn 19, Issue 9, 2011, Pages 1582-1590

  Pacak, Christina A ^a   Byrne, Barry J ^b  

^a BOSTON CHILDREN S HOSPITAL   (United States)

^b UNIVERSITY OF FLORIDA COLLEGE OF MEDICINE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ADRENOMEDULLIN; ANGIOTENSIN CONVERTING ENZYME 2; BETA ADRENERGIC RECEPTOR BLOCKING AGENT; BETA ADRENERGIC RECEPTOR KINASE INHIBITOR; BETA GLUCURONIDASE; CARDIOVASCULAR AGENT; DOUBLE STRANDED DNA; DYSTROPHIN; GAMMA SARCOGLYCAN; GENOMIC DNA; GLUCAN 1,4 ALPHA GLUCOSIDASE; HEME OXYGENASE 1; IMMUNOGLOBULIN ENHANCER BINDING PROTEIN; LONG CHAIN ACYL COENZYME A DEHYDROGENASE; NEUTRALIZING ANTIBODY; PARVOVIRUS VECTOR; PLASMID DNA; SARCOPLASMIC RETICULUM CALCIUM TRANSPORTING ADENOSINE TRIPHOSPHATASE; SINGLE STRANDED DNA; SUPPRESSOR OF CYTOKINE SIGNALING 1; TRANSFORMING GROWTH FACTOR BETA1; TUMOR NECROSIS FACTOR RECEPTOR 2; UNCLASSIFIED DRUG; VASCULOTROPIN; VIRUS DNA;

DISEASE SEVERITY; DRUG EFFICACY; DUCHENNE MUSCULAR DYSTROPHY; ENHANCER REGION; GENE EXPRESSION; GENE INACTIVATION; GENE TRANSFER; GENETIC REGULATION; GLYCOGEN STORAGE DISEASE TYPE 2; HEART DISEASE; HEART ELECTROPHYSIOLOGY; HEART FAILURE; HEART HYPERTROPHY; HEART INFARCTION; HEART INFARCTION SIZE; HEART INJURY; HEART MUSCLE ISCHEMIA; HEART PROTECTION; HUMAN; HYPERTENSION; METABOLIC DISORDER; MUCOPOLYSACCHARIDOSIS TYPE 7; NEUROMUSCULAR DISEASE; NONHUMAN; PROMOTER REGION; REPERFUSION INJURY; REVIEW; RNA INTERFERENCE; SIGNAL TRANSDUCTION; SINGLE DRUG DOSE; TISSUE SPECIFICITY; TRANSGENE; VIRAL GENE DELIVERY SYSTEM; VIRUS CAPSID; VIRUS RECOMBINANT; VIRUS RECOMBINATION; WILD TYPE;

ADENO-ASSOCIATED VIRUS; MIRIDAE;

EID: 80052399996     PISSN: 15250016     EISSN: 15250024     Source Type: Journal    
DOI: 10.1038/mt.2011.124     Document Type: Review

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