-
1
-
-
0036149132
-
Safety of local delivery of low- and intermediate-dose adenovirus gene transfer vectors to individuals with a spectrum of morbid conditions
-
Harvey BG et al. Safety of local delivery of low- and intermediate-dose adenovirus gene transfer vectors to individuals with a spectrum of morbid conditions. Hum Gene Ther 2002; 13: 15-63.
-
(2002)
Hum. Gene Ther.
, vol.13
, pp. 15-63
-
-
Harvey, B.G.1
-
2
-
-
0037192311
-
Restoration of deficient membrane proteins in the cardiomyopathic hamster by in vivo cardiac gene transfer
-
Ikeda Y et al. Restoration of deficient membrane proteins in the cardiomyopathic hamster by in vivo cardiac gene transfer. Circulation 2002; 105: 502-508.
-
(2002)
Circulation
, vol.105
, pp. 502-508
-
-
Ikeda, Y.1
-
3
-
-
0032578961
-
Gene therapy for myocardial angiogenesis: Initial clinical results with direct myocardial injection of phVEGF165 as sole therapy for myocardial ischemia
-
Losordo DW et al. Gene therapy for myocardial angiogenesis: initial clinical results with direct myocardial injection of phVEGF165 as sole therapy for myocardial ischemia. Circulation 1998; 98: 2800-2804.
-
(1998)
Circulation
, vol.98
, pp. 2800-2804
-
-
Losordo, D.W.1
-
4
-
-
0036678455
-
The atomic structure of adeno-associated virus (AAV-2), a vector for human gene therapy
-
Xie Q et al. The atomic structure of adeno-associated virus (AAV-2), a vector for human gene therapy. Proc Natl Acad Sci USA 2002; 99: 10405-10410.
-
(2002)
Proc. Natl. Acad. Sci. USA
, vol.99
, pp. 10405-10410
-
-
Xie, Q.1
-
5
-
-
0028169741
-
Long-term gene expression and phenotypic correction using adeno-associated virus vectors in the mammalian brain
-
Kaplitt MG et al. Long-term gene expression and phenotypic correction using adeno-associated virus vectors in the mammalian brain. Nat Genet 1994; 8: 148-154.
-
(1994)
Nat. Genet.
, vol.8
, pp. 148-154
-
-
Kaplitt, M.G.1
-
6
-
-
0031011987
-
Adeno-associated virus 2-mediated gene transfer in vivo: Organ-tropism and expression of transduced sequences in mice
-
Ponnazhagan S et al. Adeno-associated virus 2-mediated gene transfer in vivo: organ-tropism and expression of transduced sequences in mice. Gene 1997; 190: 203-210.
-
(1997)
Gene
, vol.190
, pp. 203-210
-
-
Ponnazhagan, S.1
-
7
-
-
0031775494
-
Adeno-associated virus as a vector for liver directed gene therapy
-
Xiao W et al. Adeno-associated virus as a vector for liver directed gene therapy. J Virol 1998; 72: 10222-10226.
-
(1998)
J. Virol.
, vol.72
, pp. 10222-10226
-
-
Xiao, W.1
-
8
-
-
0027484584
-
Stable in vivo expression of the cystic fibrosis transmembrane conductance regulator with an adeno-associated virus vector
-
Flotte TR et al. Stable in vivo expression of the cystic fibrosis transmembrane conductance regulator with an adeno-associated virus vector. Proc Nat Acad Sci USA 1993; 90: 10613-10617.
-
(1993)
Proc. Nat. Acad. Sci. USA
, vol.90
, pp. 10613-10617
-
-
Flotte, T.R.1
-
9
-
-
0029843596
-
Efficient long-term gene transfer into muscle tissue of immunocompetent mice by adeno-associated virus vector
-
Xiao X, Li J, Samulski RJ. Efficient long-term gene transfer into muscle tissue of immunocompetent mice by adeno-associated virus vector. J Virol 1996; 70: 8098-8108.
-
(1996)
J. Virol.
, vol.70
, pp. 8098-8108
-
-
Xiao, X.1
Li, J.2
Samulski, R.J.3
-
10
-
-
0030451214
-
Gene delivery to skeletal muscle results in sustained expression and systemic delivery of a therapeutic protein
-
Kessler PD et al. Gene delivery to skeletal muscle results in sustained expression and systemic delivery of a therapeutic protein. Proc Nat Acad Sci USA 1996; 93: 14082-14087.
-
(1996)
Proc. Nat. Acad. Sci. USA
, vol.93
, pp. 14082-14087
-
-
Kessler, P.D.1
-
11
-
-
0029914677
-
Gene transfer into the mouse retina mediated by an adeno-associated viral vector
-
Ali RR et al. Gene transfer into the mouse retina mediated by an adeno-associated viral vector. Hum Mol Genet 1996; 5: 591-594.
-
(1996)
Hum. Mol. Genet.
, vol.5
, pp. 591-594
-
-
Ali, R.R.1
-
12
-
-
0031011667
-
Efficient photoreceptor-targeted gene expression in vivo by recombinant adeno-associated virus
-
Flannery JG et al. Efficient photoreceptor-targeted gene expression in vivo by recombinant adeno-associated virus. Proc Nat Acad Sci USA 1997; 94: 6916-6921.
-
(1997)
Proc. Nat. Acad. Sci. USA
, vol.94
, pp. 6916-6921
-
-
Flannery, J.G.1
-
13
-
-
0034138226
-
Rescue of skeletal muscles of gamma-sarcoglycan-deficient mice with adeno-associated virus-mediated gene transfer
-
Cordier L et al. Rescue of skeletal muscles of gamma-sarcoglycan-deficient mice with adeno-associated virus-mediated gene transfer. Mol Ther 2000; 1: 119-129.
-
(2000)
Mol. Ther.
, vol.1
, pp. 119-129
-
-
Cordier, L.1
-
14
-
-
0032924996
-
rAAV vector-mediated sarcogylcan gene transfer in a hamster model for limb girdle muscular dystrophy
-
Li J et al. rAAV vector-mediated sarcogylcan gene transfer in a hamster model for limb girdle muscular dystrophy. Gene Therapy 1999; 6: 74-82.
-
(1999)
Gene Therapy
, vol.6
, pp. 74-82
-
-
Li, J.1
-
15
-
-
0033958294
-
Full functional rescue of a complete muscle (TA) in dystrophic hamsters by adeno-associated virus vector-directed gene therapy
-
Xiao X et al. Full functional rescue of a complete muscle (TA) in dystrophic hamsters by adeno-associated virus vector-directed gene therapy. J Virol 2000; 74: 1436-1442.
-
(2000)
J. Virol.
, vol.74
, pp. 1436-1442
-
-
Xiao, X.1
-
16
-
-
0034610364
-
Adeno-associated virus vector carrying human minidystrophin genes effectively ameliorates muscular dystrophy in mdx mouse model
-
Wang B, Li J, Xiao X. Adeno-associated virus vector carrying human minidystrophin genes effectively ameliorates muscular dystrophy in mdx mouse model. Proc Natl Acad Sci USA 2000; 97: 13714-13719.
-
(2000)
Proc. Natl. Acad. Sci. USA
, vol.97
, pp. 13714-13719
-
-
Wang, B.1
Li, J.2
Xiao, X.3
-
17
-
-
0036385643
-
Adeno-associated virus vector-mediated minidystrophin gene therapy improves dystrophic muscle contractile function in mdx mice
-
Watchko J et al. Adeno-associated virus vector-mediated minidystrophin gene therapy improves dystrophic muscle contractile function in mdx mice. Hum Gene Ther 2002; 13: 1451-1460.
-
(2002)
Hum. Gene Ther.
, vol.13
, pp. 1451-1460
-
-
Watchko, J.1
-
18
-
-
0032907636
-
Stable restoration of the sarcoglycan complex in dystrophic muscle perfused with histamine and a recombinant adeno-associated viral vector
-
Greelish JP et al. Stable restoration of the sarcoglycan complex in dystrophic muscle perfused with histamine and a recombinant adeno-associated viral vector. Nat Med 1999; 5: 439-443.
-
(1999)
Nat. Med.
, vol.5
, pp. 439-443
-
-
Greelish, J.P.1
-
19
-
-
0032862984
-
Persistent expression of canine factor IX in hemophilia B canines
-
Chao H et al. Persistent expression of canine factor IX in hemophilia B canines. Gene Therapy 1999; 6: 1695-1704.
-
(1999)
Gene Therapy
, vol.6
, pp. 1695-1704
-
-
Chao, H.1
-
20
-
-
0034050904
-
Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector
-
Kay MA et al. Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector. Nat Genet 2000; 24: 257-261.
-
(2000)
Nat. Genet.
, vol.24
, pp. 257-261
-
-
Kay, M.A.1
-
21
-
-
13144305062
-
Sustained secretion of human alpha-1-antitrypsin from murine muscle transduced with adeno-associated virus vectors
-
Song S et al. Sustained secretion of human alpha-1-antitrypsin from murine muscle transduced with adeno-associated virus vectors. Proc Natl Acad Sci USA 1998; 95: 14384-14388.
-
(1998)
Proc. Natl. Acad. Sci. USA
, vol.95
, pp. 14384-14388
-
-
Song, S.1
-
22
-
-
0036099319
-
Correction of the enzymatic and functional deficits in a model of Pompe disease using adeno-associated virus vectors
-
Fraites Jr TJ et al. Correction of the enzymatic and functional deficits in a model of Pompe disease using adeno-associated virus vectors. Mol Ther 2002; 5: 571-578.
-
(2002)
Mol. Ther.
, vol.5
, pp. 571-578
-
-
Fraites T.J., Jr.1
-
23
-
-
0033559741
-
Counting muscular dystrophies in the post-molecular census
-
Hoffman EP. Counting muscular dystrophies in the post-molecular census. J Neurol Sci 1999; 164: 3-6.
-
(1999)
J. Neurol. Sci.
, vol.164
, pp. 3-6
-
-
Hoffman, E.P.1
-
24
-
-
0031722943
-
The sarcoglycan complex in limb-girdle muscular dystrophy
-
Lim LE, Campbell KP. The sarcoglycan complex in limb-girdle muscular dystrophy. Curr Opin Neurol 1998; 11: 443-452.
-
(1998)
Curr. Opin. Neurol.
, vol.11
, pp. 443-452
-
-
Lim, L.E.1
Campbell, K.P.2
-
25
-
-
0031451562
-
Sarcospan, the 25-kDa transmembrane component of the dystrophin-glycoprotein complex
-
Crosbie RH et al. Sarcospan, the 25-kDa transmembrane component of the dystrophin-glycoprotein complex. J Biol Chem 1997; 272: 31221-31224.
-
(1997)
J. Biol. Chem.
, vol.272
, pp. 31221-31224
-
-
Crosbie, R.H.1
-
26
-
-
0000357470
-
Primary, generalized polymyopathy and cardiac necrosis in an inbred line of Syrian hamsters
-
Homburger F, Baker JR, Nixon CW, Whitney R. Primary, generalized polymyopathy and cardiac necrosis in an inbred line of Syrian hamsters. Med Exp 1962; 6: 339-345.
-
(1962)
Med. Exp.
, vol.6
, pp. 339-345
-
-
Homburger, F.1
Baker, J.R.2
Nixon, C.W.3
Whitney, R.4
-
27
-
-
8244259185
-
Identification of the Syrian hamster cardiomyopathy gene
-
Nigro V et al. Identification of the Syrian hamster cardiomyopathy gene. Hum Mol Genet 1997; 6: 601-607.
-
(1997)
Hum. Mol. Genet.
, vol.6
, pp. 601-607
-
-
Nigro, V.1
-
28
-
-
0031471956
-
Both hypertrophic and dilated cardiomyopathies are caused by mutation of the same gene, delta-sarcoglycan, in hamster: An animal model of disrupted dystrophin-associated glycoprotein complex
-
Sakamoto A et al. Both hypertrophic and dilated cardiomyopathies are caused by mutation of the same gene, delta-sarcoglycan, in hamster: an animal model of disrupted dystrophin-associated glycoprotein complex. Proc Nat Acad Sci USA 1997; 94: 13873-13878.
-
(1997)
Proc. Nat. Acad. Sci. USA
, vol.94
, pp. 13873-13878
-
-
Sakamoto, A.1
-
29
-
-
0032062510
-
Functional rescue of the sarcoglycan complex in the BIO 14.6 hamster using delta-sarcoglycan gene transfer
-
Holt KH et al. Functional rescue of the sarcoglycan complex in the BIO 14.6 hamster using delta-sarcoglycan gene transfer. Mol Cell 1998; 1: 841-848.
-
(1998)
Mol. Cell
, vol.1
, pp. 841-848
-
-
Holt, K.H.1
-
30
-
-
0037154148
-
Rescue of hereditary form of dilated cardiomyopathy by rAAV-mediated somatic gene therapy: Amelioration of morphological findings, sarcolemmal permeability, cardiac performances, and the prognosis of TO-2 hamsters
-
Kawada T et al. Rescue of hereditary form of dilated cardiomyopathy by rAAV-mediated somatic gene therapy: amelioration of morphological findings, sarcolemmal permeability, cardiac performances, and the prognosis of TO-2 hamsters. Proc Natl Acad Sci USA 2002; 99: 901-906.
-
(2002)
Proc. Natl. Acad. Sci. USA
, vol.99
, pp. 901-906
-
-
Kawada, T.1
-
31
-
-
0014468579
-
Improved technique of heart transplantation in rats
-
Ono K, Lindsey ES. Improved technique of heart transplantation in rats. J Thorac Cardiovasc Surg 1969; 57: 225-229.
-
(1969)
J. Thorac. Cardiovasc. Surg.
, vol.57
, pp. 225-229
-
-
Ono, K.1
Lindsey, E.S.2
-
32
-
-
0034008961
-
The use of adeno-associated virus to circumvent the maturation-dependent viral transduction of muscle fibers
-
Pruchnic R et al. The use of adeno-associated virus to circumvent the maturation-dependent viral transduction of muscle fibers. Hum Gene Ther 2000; 11: 521-536.
-
(2000)
Hum. Gene Ther.
, vol.11
, pp. 521-536
-
-
Pruchnic, R.1
-
33
-
-
0029797726
-
The basal lamina is a physical barrier to herpes simplex virus-mediated gene delivery to mature muscle fibers
-
Huard J et al. The basal lamina is a physical barrier to herpes simplex virus-mediated gene delivery to mature muscle fibers. J Virol 1996; 70: 8117-8123.
-
(1996)
J. Virol.
, vol.70
, pp. 8117-8123
-
-
Huard, J.1
-
34
-
-
0030540970
-
Long-term gene transfer in porcine myocardium after coronary infusion of an adeno-associated virus vector
-
Kaplitt MG et al. Long-term gene transfer in porcine myocardium after coronary infusion of an adeno-associated virus vector. Ann Thorac Surg 1996; 62: 1669-1676.
-
(1996)
Ann. Thorac. Surg.
, vol.62
, pp. 1669-1676
-
-
Kaplitt, M.G.1
-
35
-
-
0036341380
-
Chronic suppression of heart-failure progression by a pseudophosphorylated mutant of phospholamban via in vivo cardiac rAAV gene delivery
-
Hoshijima M et al. Chronic suppression of heart-failure progression by a pseudophosphorylated mutant of phospholamban via in vivo cardiac rAAV gene delivery. Nat Med 2002; 8: 864-871.
-
(2002)
Nat. Med.
, vol.8
, pp. 864-871
-
-
Hoshijima, M.1
-
36
-
-
18744385811
-
Uniform long-term gene expression using adeno-associated virus (AAV) by ex vivo recirculation in rat-cardiac isografts
-
Asfour B et al. Uniform long-term gene expression using adeno-associated virus (AAV) by ex vivo recirculation in rat-cardiac isografts. Thorac Cardiovasc Surg 2002; 50: 347-350.
-
(2002)
Thorac. Cardiovasc. Surg.
, vol.50
, pp. 347-350
-
-
Asfour, B.1
-
37
-
-
0032702046
-
A simple new model of physiologically working heterotopic rat heart transplantation provides hemodynamic performance equivalent to that of an orthotopic heart
-
Asfour B et al. A simple new model of physiologically working heterotopic rat heart transplantation provides hemodynamic performance equivalent to that of an orthotopic heart. J Heart Lung Transplant 1999; 18: 927-936.
-
(1999)
J. Heart Lung Transplant.
, vol.18
, pp. 927-936
-
-
Asfour, B.1
-
38
-
-
0031906147
-
Membrane-associated heparan sulfate proteoglycan is a receptor for adeno-associated virus type 2 virions
-
Summerford C, Samulski RJ. Membrane-associated heparan sulfate proteoglycan is a receptor for adeno-associated virus type 2 virions. J Virol 1998; 72: 1438-1445.
-
(1998)
J. Virol.
, vol.72
, pp. 1438-1445
-
-
Summerford, C.1
Samulski, R.J.2
-
39
-
-
0032589751
-
AlphaVbeta5 integrin: A co-receptor for adeno-associated virus type 2 infection
-
Summerford C, Bartlett JS, Samulski RJ. AlphaVbeta5 integrin: a co-receptor for adeno-associated virus type 2 infection. Nat Med 1999; 5: 78-82.
-
(1999)
Nat. Med.
, vol.5
, pp. 78-82
-
-
Summerford, C.1
Bartlett, J.S.2
Samulski, R.J.3
-
40
-
-
0033010884
-
Human fibroblast growth factor receptor 1 is a coreceptor for infection by adeno-associated virus 2
-
Qing K et al. Human fibroblast growth factor receptor 1 is a coreceptor for infection by adeno-associated virus 2. Nat Med 1999; 5: 71-77.
-
(1999)
Nat. Med.
, vol.5
, pp. 71-77
-
-
Qing, K.1
-
41
-
-
0033588050
-
Disruption of the sarcoglycan-sarcospan complex in vascular smooth muscle: A novel mechanism for cardiomyopathy and muscular dystrophy
-
Coral-Vazquez R et al. Disruption of the sarcoglycan-sarcospan complex in vascular smooth muscle: a novel mechanism for cardiomyopathy and muscular dystrophy. Cell 1999; 98: 465-474.
-
(1999)
Cell
, vol.98
, pp. 465-474
-
-
Coral-Vazquez, R.1
-
42
-
-
0035139829
-
Prevention of cardiomyopathy in mouse models lacking the smooth muscle sarcoglycan-sarcospan complex
-
Cohn RD et al. Prevention of cardiomyopathy in mouse models lacking the smooth muscle sarcoglycan-sarcospan complex. J Clin Invest 2001; 107: R1-R7.
-
(2001)
J. Clin. Invest.
, vol.107
-
-
Cohn, R.D.1
-
43
-
-
2642642141
-
Production of high-titer recombinant adeno-associated virus vectors in the absence of helper adenovirus
-
Xiao X, Li J, Samulski RJ. Production of high-titer recombinant adeno-associated virus vectors in the absence of helper adenovirus. J Virol 1998; 72: 2224-2232.
-
(1998)
J. Virol.
, vol.72
, pp. 2224-2232
-
-
Xiao, X.1
Li, J.2
Samulski, R.J.3
-
44
-
-
0002988871
-
Production of recombinant adeno-associated viral vectors
-
Dracopoli N et al (eds). John Wiley & Sons Ltd.: New York
-
Snyder R, Xiao X, Samulski RJ. Production of recombinant adeno-associated viral vectors. In: Dracopoli N et al (eds). Current Protocols in Human Genetics. John Wiley & Sons Ltd.: New York, 1996, pp 12.11.11-12.12.23.
-
(1996)
Current Protocols in Human Genetics
-
-
Snyder, R.1
Xiao, X.2
Samulski, R.J.3
|