-
1
-
-
38949170231
-
-
Andino, L.M., Conlon, T.J., Porvasnik, S.L., Boye, S.L., Hauswirth, W.W., and Lewin, A.S. (2007). Rapid, widespread transduction of the murine myocardium using self-complementary adeno-associated virus. Genet. Vaccines Ther. 5, 13.
-
Andino, L.M., Conlon, T.J., Porvasnik, S.L., Boye, S.L., Hauswirth, W.W., and Lewin, A.S. (2007). Rapid, widespread transduction of the murine myocardium using self-complementary adeno-associated virus. Genet. Vaccines Ther. 5, 13.
-
-
-
-
2
-
-
39449129592
-
AAV-mediated knockdown of phospholamban leads to improved contractility and calcium handling in cardiomyocytes
-
Andino, L.M., Takeda, M., Kasahara, H., Jakymiw, A., Byrne, B.J., and Lewin, A.S. (2008). AAV-mediated knockdown of phospholamban leads to improved contractility and calcium handling in cardiomyocytes. J. Gene Med. 10, 132-142.
-
(2008)
J. Gene Med
, vol.10
, pp. 132-142
-
-
Andino, L.M.1
Takeda, M.2
Kasahara, H.3
Jakymiw, A.4
Byrne, B.J.5
Lewin, A.S.6
-
3
-
-
18244394301
-
Regional intravascular delivery of AAV-2-F.IX to skeletal muscle achieves long-term correction of hemophilia B in a large animal model
-
Arruda, V.R., Stedman, H.H., Nichols, T.C., Haskins, M.E., Nicholson, M., Herzog, R.W., Couto, L.B., and High, K.A. (2005). Regional intravascular delivery of AAV-2-F.IX to skeletal muscle achieves long-term correction of hemophilia B in a large animal model. Blood 105, 3458-3464.
-
(2005)
Blood
, vol.105
, pp. 3458-3464
-
-
Arruda, V.R.1
Stedman, H.H.2
Nichols, T.C.3
Haskins, M.E.4
Nicholson, M.5
Herzog, R.W.6
Couto, L.B.7
High, K.A.8
-
4
-
-
35848961457
-
Systemic AAV-9 transduction in mice is influenced by animal age but not by the route of administration
-
Bostick, B., Ghosh, A., Yue, Y., Long, C., and Duan, D. (2007). Systemic AAV-9 transduction in mice is influenced by animal age but not by the route of administration. Gene Ther. 14, 1605-1609.
-
(2007)
Gene Ther
, vol.14
, pp. 1605-1609
-
-
Bostick, B.1
Ghosh, A.2
Yue, Y.3
Long, C.4
Duan, D.5
-
5
-
-
10344230408
-
Adeno-associated virus and the development of adeno-associated virus vectors: A historical perspective
-
Carter, B.J. (2004). Adeno-associated virus and the development of adeno-associated virus vectors: A historical perspective. Mol. Ther. 10, 981-989.
-
(2004)
Mol. Ther
, vol.10
, pp. 981-989
-
-
Carter, B.J.1
-
6
-
-
18744381849
-
Effects of adeno-associated virus DNA hairpin structure on recombination
-
Choi, V.W., Samulski, R.J., and McCarty, D.M. (2005). Effects of adeno-associated virus DNA hairpin structure on recombination. J. Virol. 79, 6801-6807.
-
(2005)
J. Virol
, vol.79
, pp. 6801-6807
-
-
Choi, V.W.1
Samulski, R.J.2
McCarty, D.M.3
-
7
-
-
4444346479
-
Differential myocardial gene delivery by recombinant serotype-specific adeno-associated viral vectors
-
Du, L., Kido, M., Lee, D.V., Rabinowitz, J.E., Samulski, R.J., Jamieson, S.W., Weitzman, M.D., and Thistlethwaite, P.A. (2004). Differential myocardial gene delivery by recombinant serotype-specific adeno-associated viral vectors. Mol. Ther. 10, 604-608.
-
(2004)
Mol. Ther
, vol.10
, pp. 604-608
-
-
Du, L.1
Kido, M.2
Lee, D.V.3
Rabinowitz, J.E.4
Samulski, R.J.5
Jamieson, S.W.6
Weitzman, M.D.7
Thistlethwaite, P.A.8
-
8
-
-
2642512201
-
Clades of adeno-associated viruses are widely disseminated in human tissues
-
Gao, G., Vandenberghe, L.H., Alvira, M.R., Lu, Y., Calcedo, R., Zhou, X., and Wilson, J.M. (2004). Clades of adeno-associated viruses are widely disseminated in human tissues. J. Virol. 78, 6381-6388.
-
(2004)
J. Virol
, vol.78
, pp. 6381-6388
-
-
Gao, G.1
Vandenberghe, L.H.2
Alvira, M.R.3
Lu, Y.4
Calcedo, R.5
Zhou, X.6
Wilson, J.M.7
-
9
-
-
0037015049
-
Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy
-
Gao, G.P., Alvira, M.R., Wang, L., Calcedo, R., Johnston, J., and Wilson, J.M. (2002). Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy. Proc. Natl. Acad. Sci. U.S.A. 99, 11854-11859.
-
(2002)
Proc. Natl. Acad. Sci. U.S.A
, vol.99
, pp. 11854-11859
-
-
Gao, G.P.1
Alvira, M.R.2
Wang, L.3
Calcedo, R.4
Johnston, J.5
Wilson, J.M.6
-
10
-
-
33645077592
-
AAV vector re-targeting: A small step on the way to cardiac-specific gene transfer
-
Godecke, A. (2006). AAV vector re-targeting: A small step on the way to cardiac-specific gene transfer. Cardiovasc. Res. 70, 6-8.
-
(2006)
Cardiovasc. Res
, vol.70
, pp. 6-8
-
-
Godecke, A.1
-
11
-
-
44449114156
-
Design of a phase 1/2 trial of intracoronary administration of AAV1/SERCA2a in patients with heart failure
-
Hajjar, R.J., Zsebo, K., Deckelbaum, L., Thompson, C., Rudy, J., Yaroshinsky, A., Ly, H., Kawase, Y., Wagner, K., Borow, K., Jaski, B., London, B., Greenberg, B., Pauly, D.F., Patten, R., Starling, R., Mancini, D., and Jessup, M. (2008). Design of a phase 1/2 trial of intracoronary administration of AAV1/SERCA2a in patients with heart failure. J. Card. Fail. 14, 355-367.
-
(2008)
J. Card. Fail
, vol.14
, pp. 355-367
-
-
Hajjar, R.J.1
Zsebo, K.2
Deckelbaum, L.3
Thompson, C.4
Rudy, J.5
Yaroshinsky, A.6
Ly, H.7
Kawase, Y.8
Wagner, K.9
Borow, K.10
Jaski, B.11
London, B.12
Greenberg, B.13
Pauly, D.F.14
Patten, R.15
Starling, R.16
Mancini, D.17
Jessup, M.18
-
12
-
-
0034968125
-
Hybrid vectors based on adeno-associated virus serotypes 2 and 5 for muscle-directed gene transfer
-
Hildinger, M., Auricchio, A., Gao, G., Wang, L., Chirmule, N., and Wilson, J.M. (2001). Hybrid vectors based on adeno-associated virus serotypes 2 and 5 for muscle-directed gene transfer. J. Virol. 75, 6199-6203.
-
(2001)
J. Virol
, vol.75
, pp. 6199-6203
-
-
Hildinger, M.1
Auricchio, A.2
Gao, G.3
Wang, L.4
Chirmule, N.5
Wilson, J.M.6
-
13
-
-
33745143956
-
Robust systemic transduction with AAV9 vectors in mice: Efficient global cardiac gene transfer superior to that of AAV8
-
Inagaki, K., Fuess, S., Storm, T.A., Gibson, G.A., McTiernan, C.F., Kay, M.A., and Nakai, H. (2006). Robust systemic transduction with AAV9 vectors in mice: Efficient global cardiac gene transfer superior to that of AAV8. Mol. Ther. 14, 45-53.
-
(2006)
Mol. Ther
, vol.14
, pp. 45-53
-
-
Inagaki, K.1
Fuess, S.2
Storm, T.A.3
Gibson, G.A.4
McTiernan, C.F.5
Kay, M.A.6
Nakai, H.7
-
14
-
-
19444363187
-
Widespread and early myocardial gene expression by adeno-associated virus vector type 6 with a β-actin hybrid promoter
-
Kawamoto, S., Shi, Q., Nitta, Y., Miyazaki, J., and Allen, M.D. (2005). Widespread and early myocardial gene expression by adeno-associated virus vector type 6 with a β-actin hybrid promoter. Mol. Ther. 11, 980-985.
-
(2005)
Mol. Ther
, vol.11
, pp. 980-985
-
-
Kawamoto, S.1
Shi, Q.2
Nitta, Y.3
Miyazaki, J.4
Allen, M.D.5
-
15
-
-
0034882826
-
Self-complementary recombinant adeno-associated virus (scAAV) vectors promote efficient transduction independently of DNA synthesis
-
McCarty, D.M., Monahan, P.E., and Samulski, R.J. (2001). Self-complementary recombinant adeno-associated virus (scAAV) vectors promote efficient transduction independently of DNA synthesis. Gene Ther. 8, 1248-1254.
-
(2001)
Gene Ther
, vol.8
, pp. 1248-1254
-
-
McCarty, D.M.1
Monahan, P.E.2
Samulski, R.J.3
-
16
-
-
0346777307
-
Adeno-associated virus terminal repeat (TR) mutant generates self-complementary vectors to overcome the rate-limiting step to transduction in vivo
-
McCarty, D.M., Fu, H., Monahan, P.E., Toulson, C.E., Naik, P., and Samulski, R.J. (2003). Adeno-associated virus terminal repeat (TR) mutant generates self-complementary vectors to overcome the rate-limiting step to transduction in vivo. Gene Ther. 10, 2112-2118.
-
(2003)
Gene Ther
, vol.10
, pp. 2112-2118
-
-
McCarty, D.M.1
Fu, H.2
Monahan, P.E.3
Toulson, C.E.4
Naik, P.5
Samulski, R.J.6
-
17
-
-
42649145845
-
Efficient and durable gene transfer to transplanted heart using adeno-associated virus 9 vector
-
Miyagi, N., Rao, V.P., Ricci, D., Du, Z., Byrne, G.W., Bailey, K.R., Nakai, H., Russell, S.J., and McGregor, C.G. (2008). Efficient and durable gene transfer to transplanted heart using adeno-associated virus 9 vector. J. Heart Lung Transplant 27, 554-560.
-
(2008)
J. Heart Lung Transplant
, vol.27
, pp. 554-560
-
-
Miyagi, N.1
Rao, V.P.2
Ricci, D.3
Du, Z.4
Byrne, G.W.5
Bailey, K.R.6
Nakai, H.7
Russell, S.J.8
McGregor, C.G.9
-
18
-
-
33645064807
-
Improved cardiac gene transfer by transcriptional and transductional targeting of adeno-associated viral vectors
-
Muller, O.J., Leuchs, B., Pleger, S.T., Grimm, D., Franz, W.M., Katus, H.A., and Kleinschmidt, J.A. (2006). Improved cardiac gene transfer by transcriptional and transductional targeting of adeno-associated viral vectors. Cardiovasc. Res. 70, 70-78.
-
(2006)
Cardiovasc. Res
, vol.70
, pp. 70-78
-
-
Muller, O.J.1
Leuchs, B.2
Pleger, S.T.3
Grimm, D.4
Franz, W.M.5
Katus, H.A.6
Kleinschmidt, J.A.7
-
19
-
-
33846155891
-
Targeting the heart with gene therapy-optimized gene delivery methods
-
Muller, O.J., Katus, H.A., and Bekeredjian, R. (2007). Targeting the heart with gene therapy-optimized gene delivery methods. Cardiovasc. Res. 73, 453-462.
-
(2007)
Cardiovasc. Res
, vol.73
, pp. 453-462
-
-
Muller, O.J.1
Katus, H.A.2
Bekeredjian, R.3
-
20
-
-
33747518710
-
Recombinant adeno-associated virus serotype 9 leads to preferential cardiac transduction in vivo
-
Pacak, C.A., Mah, C.S., Thattaliyath, B.D., Conlon, T.J., Lewis, M.A., Cloutier, D.E., Zolotukhin, I., Tarantal, A.F., and Byrne, B.J. (2006). Recombinant adeno-associated virus serotype 9 leads to preferential cardiac transduction in vivo. Circ. Res. 99, e3-e9.
-
(2006)
Circ. Res
, vol.99
-
-
Pacak, C.A.1
Mah, C.S.2
Thattaliyath, B.D.3
Conlon, T.J.4
Lewis, M.A.5
Cloutier, D.E.6
Zolotukhin, I.7
Tarantal, A.F.8
Byrne, B.J.9
-
21
-
-
34748831166
-
Efficiency of eight different AAV serotypes in transducing rat myocardium in vivo
-
Palomeque, J., Chemaly, E.R., Colosi, P., Wellman, J.A., Zhou, S., Del Monte, F., and Hajjar, R.J. (2007). Efficiency of eight different AAV serotypes in transducing rat myocardium in vivo. Gene Ther. 14, 989-997.
-
(2007)
Gene Ther
, vol.14
, pp. 989-997
-
-
Palomeque, J.1
Chemaly, E.R.2
Colosi, P.3
Wellman, J.A.4
Zhou, S.5
Del Monte, F.6
Hajjar, R.J.7
-
22
-
-
34248570118
-
Stable myocardial-specific AAV6-S100A1 gene therapy results in chronic functional heart failure rescue
-
Pleger, S.T., Most, P., Boucher, M., Soltys, S., Chuprun, J.K., Pleger, W., Gao, E., Dasgupta, A., Rengo, G., Remppis, A., Katus, H.A., Eckhart, A.D., Rabinowitz, J.E., and Koch, W.J. (2007). Stable myocardial-specific AAV6-S100A1 gene therapy results in chronic functional heart failure rescue. Circulation 115, 2506-2515.
-
(2007)
Circulation
, vol.115
, pp. 2506-2515
-
-
Pleger, S.T.1
Most, P.2
Boucher, M.3
Soltys, S.4
Chuprun, J.K.5
Pleger, W.6
Gao, E.7
Dasgupta, A.8
Rengo, G.9
Remppis, A.10
Katus, H.A.11
Eckhart, A.D.12
Rabinowitz, J.E.13
Koch, W.J.14
-
23
-
-
34047115768
-
Restoration of mechanical and energetic function in failing aortic-banded rat hearts by gene transfer of calcium cycling proteins
-
Sakata, S., Lebeche, D., Sakata, N., Sakata, Y., Chemaly, E.R., Liang, L.F., Tsuji, T., Takewa, Y., Del Monte, F., Peluso, R., Zsebo, K., Jeong, D., Park, W.J., Kawase, Y., and Hajjar, R.J. (2007). Restoration of mechanical and energetic function in failing aortic-banded rat hearts by gene transfer of calcium cycling proteins. J. Mol. Cell Cardiol. 42, 852-861.
-
(2007)
J. Mol. Cell Cardiol
, vol.42
, pp. 852-861
-
-
Sakata, S.1
Lebeche, D.2
Sakata, N.3
Sakata, Y.4
Chemaly, E.R.5
Liang, L.F.6
Tsuji, T.7
Takewa, Y.8
Del Monte, F.9
Peluso, R.10
Zsebo, K.11
Jeong, D.12
Park, W.J.13
Kawase, Y.14
Hajjar, R.J.15
-
24
-
-
34247871536
-
Recombinant adeno-associated virus vector for gene transfer to the transplanted rat heart
-
Schirmer, J.M., Miyagi, N., Rao, V.P., Ricci, D., Federspiel, M.J., Kotin, R.M., Russell, S.J., and McGregor, C.G. (2007). Recombinant adeno-associated virus vector for gene transfer to the transplanted rat heart. Transpl. Int. 20, 550-557.
-
(2007)
Transpl. Int
, vol.20
, pp. 550-557
-
-
Schirmer, J.M.1
Miyagi, N.2
Rao, V.P.3
Ricci, D.4
Federspiel, M.J.5
Kotin, R.M.6
Russell, S.J.7
McGregor, C.G.8
-
25
-
-
34548500109
-
Differential internalization and nuclear uncoating of self-complementary adeno-associated virus pseudotype vectors as determinants of cardiac cell transduction
-
Sipo, I., Fechner, H., Pinkert, S., Suckau, L., Wang, X., Weger, S., and Poller, W. (2007). Differential internalization and nuclear uncoating of self-complementary adeno-associated virus pseudotype vectors as determinants of cardiac cell transduction. Gene Ther. 14, 1319-1329.
-
(2007)
Gene Ther
, vol.14
, pp. 1319-1329
-
-
Sipo, I.1
Fechner, H.2
Pinkert, S.3
Suckau, L.4
Wang, X.5
Weger, S.6
Poller, W.7
-
26
-
-
33845531899
-
Efficacy and safety of adeno-associated viral vectors based on serotype 8 and 9 vs. lentiviral vectors for hemophilia B gene therapy
-
Vandendriessche, T., Thorrez, L., Acosta-Sanchez, A., Petrus, I., Wang, L., Ma, L., L, De Waele, L., Iwasaki, Y., Gillijns, V., Wilson, J.M., Collen, D., and Chuah, M.K. (2007). Efficacy and safety of adeno-associated viral vectors based on serotype 8 and 9 vs. lentiviral vectors for hemophilia B gene therapy. J. Thromb. Haemost. 5, 16-24.
-
(2007)
J. Thromb. Haemost
, vol.5
, pp. 16-24
-
-
Vandendriessche, T.1
Thorrez, L.2
Acosta-Sanchez, A.3
Petrus, I.4
Wang, L.5
Ma, L.L.6
De Waele, L.7
Iwasaki, Y.8
Gillijns, V.9
Wilson, J.M.10
Collen, D.11
Chuah, M.K.12
-
27
-
-
17044383770
-
One year transgene expression with adeno-associated virus cardiac gene transfer
-
Woo, Y.J., Zhang, J.C., Taylor, M.D., Cohen, J.E., Hsu, V.M., and Sweeney, H.L. (2005). One year transgene expression with adeno-associated virus cardiac gene transfer. Int. J. Cardiol. 100, 421-426.
-
(2005)
Int. J. Cardiol
, vol.100
, pp. 421-426
-
-
Woo, Y.J.1
Zhang, J.C.2
Taylor, M.D.3
Cohen, J.E.4
Hsu, V.M.5
Sweeney, H.L.6
-
28
-
-
0035040977
-
In vivo myocardial gene transfer: Optimization, evaluation and direct comparison of gene transfer vectors
-
Wright, M.J., Wightman, L.M., Lilley, C., De Alwis, M., Hart, S.L., Miller, A., Coffin, R.S., Thrasher, A., Latchman, D.S., and Marber, M.S. (2001). In vivo myocardial gene transfer: Optimization, evaluation and direct comparison of gene transfer vectors. Basic Res. Cardiol. 96, 227-236.
-
(2001)
Basic Res. Cardiol
, vol.96
, pp. 227-236
-
-
Wright, M.J.1
Wightman, L.M.2
Lilley, C.3
De Alwis, M.4
Hart, S.L.5
Miller, A.6
Coffin, R.S.7
Thrasher, A.8
Latchman, D.S.9
Marber, M.S.10
-
29
-
-
0141841602
-
Microdystrophin gene therapy of cardiomyopathy restores dystrophin-glycoprotein complex and improves sarcolemma integrity in the mdx mouse heart
-
Yue, Y., Li, Z., Harper, S.Q., Davisson, R.L., Chamberlain, J.S., and Duan, D. (2003). Microdystrophin gene therapy of cardiomyopathy restores dystrophin-glycoprotein complex and improves sarcolemma integrity in the mdx mouse heart. Circulation 108, 1626-1632.
-
(2003)
Circulation
, vol.108
, pp. 1626-1632
-
-
Yue, Y.1
Li, Z.2
Harper, S.Q.3
Davisson, R.L.4
Chamberlain, J.S.5
Duan, D.6
-
30
-
-
0033119064
-
Efficient transmural cardiac gene transfer by intrapericardial injection in neonatal mice
-
Zhang, J.C., Woo, Y.J., Chen, J.A., Swain, J.L., and Sweeney, H.L. (1999). Efficient transmural cardiac gene transfer by intrapericardial injection in neonatal mice. J. Mol. Cell. Cardiol. 31, 721-732.
-
(1999)
J. Mol. Cell. Cardiol
, vol.31
, pp. 721-732
-
-
Zhang, J.C.1
Woo, Y.J.2
Chen, J.A.3
Swain, J.L.4
Sweeney, H.L.5
-
31
-
-
44349170706
-
Analysis of AAV serotypes 1-9 mediated gene expression and tropism in mice after systemic injection
-
Zincarelli, C., Soltys, S., Rengo, G., and Rabinowitz, J.E. (2008). Analysis of AAV serotypes 1-9 mediated gene expression and tropism in mice after systemic injection. Mol. Ther. 16, 1073-1080.
-
(2008)
Mol. Ther
, vol.16
, pp. 1073-1080
-
-
Zincarelli, C.1
Soltys, S.2
Rengo, G.3
Rabinowitz, J.E.4
|