Long-term systemic therapy of Fabry disease in a knockout mouse by adeno-associated virus-mediated muscle-directed gene transfer

Proceedings of the National Academy of Sciences of the United States of America

Volumn 99, Issue 21, 2002, Pages 13777-13782

  Takahashi, Hiroshi ^a   Hirai, Yukihiko ^a   Migita, Makoto ^a   Seino, Yoshihiko ^a   Fukuda, Yuh ^b   Sakuraba, Hitoshi ^c   Kase, Ryoichi ^c   Kobayashi, Toshihide ^d   Hashimoto, Yasuhiro ^d   Shimada, Takashi ^a,b  

^a NIPPON MEDICAL SCHOOL   (Japan)

^b NIPPON MEDICAL SCHOOL   (Japan)

^c TOKYO METROPOLITAN INSTITUTE OF MEDICAL SCIENCE   (Japan)

^d INST OF PHYS AND CHEMICAL RESEARCH   (Japan)

Author keywords

[No Author keywords available]

Indexed keywords

ALPHA GALACTOSIDASE; GLOBOTRIAOSYLCERAMIDE; LYSOSOME ENZYME;

ADENO ASSOCIATED VIRUS; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; ECHOCARDIOGRAPHY; ELECTRON MICROSCOPY; ENZYME ACTIVITY; ENZYME REPLACEMENT; EXPRESSION VECTOR; FABRY DISEASE; FEMALE; GENE THERAPY; GENE TRANSFER; HEART VENTRICLE HYPERTROPHY; IMMUNOHISTOCHEMISTRY; KNOCKOUT MOUSE; MALE; MOUSE; NONHUMAN; PRIORITY JOURNAL; QUADRICEPS FEMORIS MUSCLE; SYSTEMIC THERAPY; X CHROMOSOME LINKED DISORDER;

ALPHA-GALACTOSIDASE; ANIMALS; CELL LINE; DEPENDOVIRUS; DISEASE MODELS, ANIMAL; FABRY DISEASE; FEMALE; GENE THERAPY; GENETIC VECTORS; HELA CELLS; HUMANS; MICE; MICE, INBRED C57BL; MICE, KNOCKOUT; MUSCLE, SKELETAL; MYOCARDIUM; TRIHEXOSYLCERAMIDES;

ADENO-ASSOCIATED VIRUS; ANIMALIA; VECTORS;

EID: 0037109052     PISSN: 00278424     EISSN: None     Source Type: Journal    
DOI: 10.1073/pnas.222221899     Document Type: Article

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