-
1
-
-
0035731827
-
Gene therapy for genetic haematological disorders and immunodeficiencies
-
Kohn DB. Gene therapy for genetic haematological disorders and immunodeficiencies. J Intern Med 2001;249:379-390.
-
(2001)
J Intern Med
, vol.249
, pp. 379-390
-
-
Kohn, D.B.1
-
2
-
-
0035731762
-
Gene transfer and the treatment of haematological malignancy
-
Brenner MK. Gene transfer and the treatment of haematological malignancy. J Intern Med 2001;249:345-358.
-
(2001)
J Intern Med
, vol.249
, pp. 345-358
-
-
Brenner, M.K.1
-
3
-
-
0034924965
-
Approaches to gene therapy for human immunodeficiency virus infection
-
Buchschacher GL Jr, Wong-Staal F. Approaches to gene therapy for human immunodeficiency virus infection. Hum Gene Ther 2001;12:1013-1019.
-
(2001)
Hum Gene Ther
, vol.12
, pp. 1013-1019
-
-
Buchschacher G.L., Jr.1
Wong-Staal, F.2
-
4
-
-
0028176884
-
Bone marrow extracellular matrix molecules improve gene transfer in human hematopoietic cells via retroviral vectors
-
Moritz T, Patel VP, Williams DA. Bone marrow extracellular matrix molecules improve gene transfer in human hematopoietic cells via retroviral vectors. J Clin Invest 1994;93:1451-1457.
-
(1994)
J Clin Invest
, vol.93
, pp. 1451-1457
-
-
Moritz, T.1
Patel, V.P.2
Williams, D.A.3
-
5
-
-
16044366110
-
Colocalization of retrovirus and target cells on specific fibronectin fragments increases genetic transduction of mammalian cells
-
Hanenberg H, Xiao XL, Dilloo D et al. Colocalization of retrovirus and target cells on specific fibronectin fragments increases genetic transduction of mammalian cells. Nat Med 1996;2:876-882.
-
(1996)
Nat Med
, vol.2
, pp. 876-882
-
-
Hanenberg, H.1
Xiao, X.L.2
Dilloo, D.3
-
6
-
-
0032531012
-
Improved gene transfer into baboon marrow repopulating cells using recombinant human fibronectin fragment CH-296 in combination with interleukin-6, stem cell factor, FLT-3 ligand and megakaryocyte growth and development factor
-
Kiem HP, Andrews RG, Morris J et al. Improved gene transfer into baboon marrow repopulating cells using recombinant human fibronectin fragment CH-296 in combination with interleukin-6, stem cell factor, FLT-3 ligand and megakaryocyte growth and development factor. Blood 1998;92:1878-1886.
-
(1998)
Blood
, vol.92
, pp. 1878-1886
-
-
Kiem, H.P.1
Andrews, R.G.2
Morris, J.3
-
8
-
-
0029857382
-
Gene marking and gene therapy directed at primary hematopoietic cells
-
Dunbar CE, Young NS. Gene marking and gene therapy directed at primary hematopoietic cells. Curr Opin Hematol 1996;3:430-437.
-
(1996)
Curr Opin Hematol
, vol.3
, pp. 430-437
-
-
Dunbar, C.E.1
Young, N.S.2
-
9
-
-
0034959561
-
Persistent low-level engraftment of rhesus peripheral blood progenitor cells transduced with fanconi anemia C gene after conditioning with low-dose irradiation
-
Kang EM, Hanazano Y, Frare P et al. Persistent low-level engraftment of rhesus peripheral blood progenitor cells transduced with fanconi anemia C gene after conditioning with low-dose irradiation. Mol Ther 2001;3:911-919.
-
(2001)
Mol Ther
, vol.3
, pp. 911-919
-
-
Kang, E.M.1
Hanazano, Y.2
Frare, P.3
-
10
-
-
0036141476
-
Transient detection of beta-galactosidase activity in hematopoietic cells, following reinjection of retrovirally marked autologous blood progenitors in patients with breast or ovarian cancer receiving high-dose chemotherapy
-
Bagnis C, Chabannon C, Gravis G et al. Transient detection of beta-galactosidase activity in hematopoietic cells, following reinjection of retrovirally marked autologous blood progenitors in patients with breast or ovarian cancer receiving high-dose chemotherapy. Exp Hematol 2002;30:108-115.
-
(2002)
Exp Hematol
, vol.30
, pp. 108-115
-
-
Bagnis, C.1
Chabannon, C.2
Gravis, G.3
-
11
-
-
0025279872
-
Gene transfer by retrovirus vectors occurs only in cells that are active replicating at the time of infection
-
Miller DG, Adam MA, Miller AD. Gene transfer by retrovirus vectors occurs only in cells that are active replicating at the time of infection. Mol Cell Biol 1990;10:4239-4242.
-
(1990)
Mol Cell Biol
, vol.10
, pp. 4239-4242
-
-
Miller, D.G.1
Adam, M.A.2
Miller, A.D.3
-
12
-
-
0028914587
-
Marrow- and spleen-seeding efficiencies of all murine hematopoietic stem cell subsets are decreased by preincubation with hematopoietic growth factors
-
Van der Loo JC, Ploemacher RE. Marrow- and spleen-seeding efficiencies of all murine hematopoietic stem cell subsets are decreased by preincubation with hematopoietic growth factors. Blood 1995;85:2598-2606.
-
(1995)
Blood
, vol.85
, pp. 2598-2606
-
-
Van der Loo, J.C.1
Ploemacher, R.E.2
-
13
-
-
0030051967
-
Ex vivo expansion of murine marrow cells with interleukin-3 (IL-3), IL-6, IL-11, and stem cell factor leads to impaired engraftment in irradiated hosts
-
Peters SO, Kittler EL, Ramshaw HS et al. Ex vivo expansion of murine marrow cells with interleukin-3 (IL-3), IL-6, IL-11, and stem cell factor leads to impaired engraftment in irradiated hosts. Blood 1996;87:30-37.
-
(1996)
Blood
, vol.87
, pp. 30-37
-
-
Peters, S.O.1
Kittler, E.L.2
Ramshaw, H.S.3
-
14
-
-
0035684026
-
Differential transduction efficiency of SCID-repopulating cells derived from umbilical cord blood and granulocyte colony-stimulating factor-mobilized peripheral blood
-
Pollok KA, Van der Loo JC, Cooper RJ et al. Differential transduction efficiency of SCID-repopulating cells derived from umbilical cord blood and granulocyte colony-stimulating factor-mobilized peripheral blood. Hum Gene Ther 2001;12:2095-2108.
-
(2001)
Hum Gene Ther
, vol.12
, pp. 2095-2108
-
-
Pollok, K.A.1
Van der Loo, J.C.2
Cooper, R.J.3
-
15
-
-
0029996147
-
In vivo gene delivery and stable transduction of nondividing cells by a lentiviral vector
-
Naldini L, Blomer U, Gallay P et al. In vivo gene delivery and stable transduction of nondividing cells by a lentiviral vector. Science 1996;272:263-267.
-
(1996)
Science
, vol.272
, pp. 263-267
-
-
Naldini, L.1
Blomer, U.2
Gallay, P.3
-
16
-
-
1842411367
-
Highly efficient and sustained gene transfer in adult neurons with a lentivirus vector
-
Blömer U, Naldini L, Kafri T et al. Highly efficient and sustained gene transfer in adult neurons with a lentivirus vector. J Virol 1997;71:6641-6649.
-
(1997)
J Virol
, vol.71
, pp. 6641-6649
-
-
Blömer, U.1
Naldini, L.2
Kafri, T.3
-
17
-
-
0030931963
-
Stable and efficient gene transfer into the retina using an HIV-based lentiviral vector
-
Miyoshi H, Takahashi M, Gage FH et al. Stable and efficient gene transfer into the retina using an HIV-based lentiviral vector. Proc Natl Acad Sci USA 1997;94:10319-10323.
-
(1997)
Proc Natl Acad Sci USA
, vol.94
, pp. 10319-10323
-
-
Miyoshi, H.1
Takahashi, M.2
Gage, F.H.3
-
18
-
-
0030716959
-
Sustained expression of genes delivered directly into liver and muscle by lentiviral vectors
-
Kafri T, Blömer U, Peterson DA et al. Sustained expression of genes delivered directly into liver and muscle by lentiviral vectors. Nat Genet 1997;17:314-317.
-
(1997)
Nat Genet
, vol.17
, pp. 314-317
-
-
Kafri, T.1
Blömer, U.2
Peterson, D.A.3
-
19
-
-
0031747965
-
Human immunodeficiency virus type 1 vectors efficiently transduce human hematopoietic stem cells
-
Sutton RE, Wu HT, Rigg R et al. Human immunodeficiency virus type 1 vectors efficiently transduce human hematopoietic stem cells. J Virol 1998;72:5781-5788.
-
(1998)
J Virol
, vol.72
, pp. 5781-5788
-
-
Sutton, R.E.1
Wu, H.T.2
Rigg, R.3
-
21
-
-
0032956732
-
Transduction of human progenitor hematopoietic stem cells by human immunodeficiency virus type 1-based vectors is cell cycle dependent
-
Sutton RE, Reitsma MJ, Uchida N et al. Transduction of human progenitor hematopoietic stem cells by human immunodeficiency virus type 1-based vectors is cell cycle dependent. J Virol 1999;73:3649-3660.
-
(1999)
J Virol
, vol.73
, pp. 3649-3660
-
-
Sutton, R.E.1
Reitsma, M.J.2
Uchida, N.3
-
22
-
-
0031015915
-
1 cell cycle status of mobilized hematopoietic stem cells from peripheral blood
-
1 cell cycle status of mobilized hematopoietic stem cells from peripheral blood. Blood 1997;89:465-472.
-
(1997)
Blood
, vol.89
, pp. 465-472
-
-
Uchida, N.1
He, D.2
Friera, A.M.3
-
23
-
-
0032532361
-
Cell cycle-related changes in repopulating capacity of human mobilized peripheral blood CD34(+) cells in non-obese diabetic/severe combined immune-deficient mice
-
Gothot A, Van der Loo JC, Clapp DW et al. Cell cycle-related changes in repopulating capacity of human mobilized peripheral blood CD34(+) cells in non-obese diabetic/severe combined immune-deficient mice. Blood 1998;92:2641-2649.
-
(1998)
Blood
, vol.92
, pp. 2641-2649
-
-
Gothot, A.1
Van der Loo, J.C.2
Clapp, D.W.3
-
24
-
-
0034724857
-
Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease
-
Cavazzana-Calvo M, Hacein-Bey S, de Saint Basile G et al. Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease. Science 2000;288:669-672.
-
(2000)
Science
, vol.288
, pp. 669-672
-
-
Cavazzana-Calvo, M.1
Hacein-Bey, S.2
De Saint Basile, G.3
-
25
-
-
0037129435
-
Sustained correction of X-linked severe combined immunodeficiency by ex vivo gene therapy
-
Hacein-Bey-Abina S, Le Deist F, Carlier F et al. Sustained correction of X-linked severe combined immunodeficiency by ex vivo gene therapy. N Engl J Med 2002;346:1185-1193.
-
(2002)
N Engl J Med
, vol.346
, pp. 1185-1193
-
-
Hacein-Bey-Abina, S.1
Le Deist, F.2
Carlier, F.3
-
26
-
-
0031975088
-
Successful peripheral T-lymphocyte-directed gene transfer for a patient with severe combined immune deficiency caused by adenosine deaminase deficiency
-
Onodera M, Ariga T, Kawamura N et al. Successful peripheral T-lymphocyte-directed gene transfer for a patient with severe combined immune deficiency caused by adenosine deaminase deficiency. Blood 1998;91:30-36.
-
(1998)
Blood
, vol.91
, pp. 30-36
-
-
Onodera, M.1
Ariga, T.2
Kawamura, N.3
-
27
-
-
18444376150
-
Immune reconstitution in ADA-SCID after PBL gene therapy and discontinuation of enzyme replacement
-
Aiuti A, Vai S, Mortellaro A et al. Immune reconstitution in ADA-SCID after PBL gene therapy and discontinuation of enzyme replacement. Nat Med 2002;8:423-425.
-
(2002)
Nat Med
, vol.8
, pp. 423-425
-
-
Aiuti, A.1
Vai, S.2
Mortellaro, A.3
-
28
-
-
0037189401
-
Correction of ADA-SCID by stem cell gene therapy combined with nonmyeloablative conditioning
-
Aiuti A, Slavin S, Aker M et al. Correction of ADA-SCID by stem cell gene therapy combined with nonmyeloablative conditioning. Science 2002;296:2410-2413.
-
(2002)
Science
, vol.296
, pp. 2410-2413
-
-
Aiuti, A.1
Slavin, S.2
Aker, M.3
-
30
-
-
0032553681
-
+ cells from patients with Gaucher disease: In vivo detection of transduced cells without myelablation
-
+ cells from patients with Gaucher disease: in vivo detection of transduced cells without myelablation. Hum Gene Ther 1998;9:2629-2640.
-
(1998)
Hum Gene Ther
, vol.9
, pp. 2629-2640
-
-
Dunbar, C.E.1
Kohn, D.B.2
Schiffmann, R.3
-
31
-
-
12644293807
-
Prolonged production of NADPH oxidase-corrected granulocytes after gene therapy of chronic granulomatous disease
-
Malech HL, Maples PB, Whiting-Theobald N et al. Prolonged production of NADPH oxidase-corrected granulocytes after gene therapy of chronic granulomatous disease. Proc Natl Acad Sci USA 1997;94:12133-12138.
-
(1997)
Proc Natl Acad Sci USA
, vol.94
, pp. 12133-12138
-
-
Malech, H.L.1
Maples, P.B.2
Whiting-Theobald, N.3
-
32
-
-
0034279968
-
Lentivirus-mediated gene transfer of gp91phox corrects chronic granulomatous disease (CGD) phenotype in human X-CGD cells
-
Saulnier SO, Steinhoff D, Dinauer MC et al. Lentivirus-mediated gene transfer of gp91phox corrects chronic granulomatous disease (CGD) phenotype in human X-CGD cells. J Gene Med 2000;2:317-325.
-
(2000)
J Gene Med
, vol.2
, pp. 317-325
-
-
Saulnier, S.O.1
Steinhoff, D.2
Dinauer, M.C.3
-
33
-
-
0034322159
-
Lentiviral vectors for enhanced gene expresion in human hemaopoietic cells
-
Ramezani A, Hawley TS, Hawley RG. Lentiviral vectors for enhanced gene expresion in human hemaopoietic cells. Mol Ther 2000;2:458-469.
-
(2000)
Mol Ther
, vol.2
, pp. 458-469
-
-
Ramezani, A.1
Hawley, T.S.2
Hawley, R.G.3
-
34
-
-
0037114745
-
+ cells from patients with X-linked chronic granulomatous disease
-
+ cells from patients with X-linked chronic granulomatous disease. Blood 2002;100:4381-4390.
-
(2002)
Blood
, vol.100
, pp. 4381-4390
-
-
Roesler, J.1
Brenner, S.2
Bukovsky, A.A.3
-
35
-
-
0034985720
-
+-derived hematopoietic cells, including developing T cells and NOD/SCID mouse repopulating cells, following transduction with modified trip lentiviral vectors
-
+-derived hematopoietic cells, including developing T cells and NOD/SCID mouse repopulating cells, following transduction with modified trip lentiviral vectors. Mol Ther 2001;3:438-447.
-
(2001)
Mol Ther
, vol.3
, pp. 438-447
-
-
Sirven, A.1
Ravet, E.2
Charneau, P.3
-
36
-
-
0035111667
-
+ cells in the SCID-hu Thy/Liv model of human T cell lymphopoiesis
-
+ cells in the SCID-hu Thy/Liv model of human T cell lymphopoiesis. Hum Gene Ther 2001;12:401-413.
-
(2001)
Hum Gene Ther
, vol.12
, pp. 401-413
-
-
Douglas, J.L.1
Lin, W.Y.2
Panis, M.L.3
-
38
-
-
0037195091
-
Permanent and panerythroid correction of murine beta thalassemia by multiple lentiviral integration in hematopoietic stem cells
-
Imren S, Payen E, Westerman KA et al. Permanent and panerythroid correction of murine beta thalassemia by multiple lentiviral integration in hematopoietic stem cells. Proc Natl Acad Sci USA 2002;99:14380-14385.
-
(2002)
Proc Natl Acad Sci USA
, vol.99
, pp. 14380-14385
-
-
Imren, S.1
Payen, E.2
Westerman, K.A.3
-
39
-
-
0037441587
-
Lentiviral vector transduction of NOD/SCID repopulating cells results in multiple vector integrations per transduced cell: Risk of insertional mutagenesis
-
Woods NB, Muessig A, Schmidt M et al. Lentiviral vector transduction of NOD/SCID repopulating cells results in multiple vector integrations per transduced cell: risk of insertional mutagenesis. Blood 2003;101:1284-1289.
-
(2003)
Blood
, vol.101
, pp. 1284-1289
-
-
Woods, N.B.1
Muessig, A.2
Schmidt, M.3
-
40
-
-
0037134031
-
Murine leukemia induced by retroviral gene marking
-
Li Z, Düllmann J, Schiedlmeier B et al. Murine leukemia induced by retroviral gene marking. Science 2002;296:497.
-
(2002)
Science
, vol.296
, pp. 497
-
-
Li, Z.1
Düllmann, J.2
Schiedlmeier, B.3
-
41
-
-
0037136924
-
Gene therapy for SCID - A complication after remarkable progress
-
Buckley RH. Gene therapy for SCID - a complication after remarkable progress. Lancet 2002;360:1185-1186.
-
(2002)
Lancet
, vol.360
, pp. 1185-1186
-
-
Buckley, R.H.1
-
42
-
-
0036893743
-
Risks and benefits of gene therapy for immunodeficiency: A reality check
-
Lemoine NR. Risks and benefits of gene therapy for immunodeficiency: a reality check. Gene Ther 2002;9:1561-1562.
-
(2002)
Gene Ther
, vol.9
, pp. 1561-1562
-
-
Lemoine, N.R.1
-
44
-
-
0033542427
-
- cell transduction via lentivirus-based gene transfer vectors
-
- cell transduction via lentivirus-based gene transfer vectors. Hum Gen Ther 1999;10:1479-1489.
-
(1999)
Hum Gen Ther
, vol.10
, pp. 1479-1489
-
-
Evans, J.T.1
Kelly, P.F.2
O'Neill, E.3
-
45
-
-
0036293903
-
Efficient oncoretroviral transduction of extended long-term culture-initiating cells and NOD/SCID repopulating cells: Enhanced reconstitution with gene-marked cells through an ex vivo expansion approach
-
Björgvinsdottir H, Bryder D, Sitnicka E et al. Efficient oncoretroviral transduction of extended long-term culture-initiating cells and NOD/SCID repopulating cells: enhanced reconstitution with gene-marked cells through an ex vivo expansion approach. Hum Gene Ther 2002;13:1061-1073.
-
(2002)
Hum Gene Ther
, vol.13
, pp. 1061-1073
-
-
Björgvinsdottir, H.1
Bryder, D.2
Sitnicka, E.3
|