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Volumn 2, Issue 5, 2000, Pages 317-325

Lentivirus-mediated gene transfer of gp91phox corrects chronic granulomatous disease (CGD) phenotype in human X-CGD cells

Author keywords

Gene therapy; Lentivirus; SIN2; X linked chronic granulomatous disease

Indexed keywords

CUCUMBER MOSAIC VIRUS; CYTOMEGALOVIRUS; HUMAN IMMUNODEFICIENCY VIRUS 1; LENTIVIRUS;

EID: 0034279968     PISSN: 1099498X     EISSN: None     Source Type: Journal    
DOI: 10.1002/1521-2254(200009/10)2:5<317::aid-jgm127>3.0.co;2-p     Document Type: Article
Times cited : (19)

References (40)
  • 1
    • 0003053791 scopus 로고    scopus 로고
    • Chronic granulomatous disease
    • Ochs HD, Smith CIE, Puck JM (eds). Oxford University Press: New York and Oxford
    • Roos D, Curnutte JT. Chronic granulomatous disease. In Primary Immunodeficiency Diseases, Ochs HD, Smith CIE, Puck JM (eds). Oxford University Press: New York and Oxford, 1999; 353-374.
    • (1999) Primary Immunodeficiency Diseases , pp. 353-374
    • Roos, D.1    Curnutte, J.T.2
  • 2
    • 0029759477 scopus 로고    scopus 로고
    • Successful bone marrow transplantation in a child with X-linked chronic granulomatous disease
    • Ho CM, Vowels MR, Lockwood L, et al. Successful bone marrow transplantation in a child with X-linked chronic granulomatous disease. Bone Marrow Transplant 1996; 18: 213-215.
    • (1996) Bone Marrow Transplant , vol.18 , pp. 213-215
    • Ho, C.M.1    Vowels, M.R.2    Lockwood, L.3
  • 3
    • 0029819958 scopus 로고    scopus 로고
    • Bone marrow transplantation in chronic granulomatous disease
    • Calvino MC, Maldonado MS, Otheo E, et al. Bone marrow transplantation in chronic granulomatous disease. Eur J Pediatr 1996; 155: 877-879.
    • (1996) Eur J Pediatr , vol.155 , pp. 877-879
    • Calvino, M.C.1    Maldonado, M.S.2    Otheo, E.3
  • 4
    • 17544397132 scopus 로고    scopus 로고
    • Successful treatment of invasive aspergillosis in chronic granulomatous disease by bone marrow transplantation, granulocyte colony-stimulating factor-mobilized granulocytes, and liposomal amphotericin-B
    • Ozsahin H, Von Planta M, Muller I, et al. Successful treatment of invasive aspergillosis in chronic granulomatous disease by bone marrow transplantation, granulocyte colony-stimulating factor-mobilized granulocytes, and liposomal amphotericin-B. Blood 1998; 92: 2719-2724.
    • (1998) Blood , vol.92 , pp. 2719-2724
    • Ozsahin, H.1    Von Planta, M.2    Muller, I.3
  • 5
    • 0003318703 scopus 로고
    • X-linked carriers of gp91phox chronic granulomatous disease (CGD): Clinical and potential therapeutic implications of extreme unbalanced X chromosome inactivation
    • Woodman R, Teoh D, Johnston F, et al. X-linked carriers of gp91phox chronic granulomatous disease (CGD): clinical and potential therapeutic implications of extreme unbalanced X chromosome inactivation (Abstract). Blood 1995; 86 (Suppl. 1): 27a.
    • (1995) Blood , vol.86 , Issue.1 SUPPL.
    • Woodman, R.1    Teoh, D.2    Johnston, F.3
  • 6
    • 1842370351 scopus 로고    scopus 로고
    • Retroviral-mediated gene transfer of gp91phox into bone marrow cells rescues defect in host defense against Aspergillus fumigatus in murine X-linked chronic granulomatous disease
    • Bjorgvinsdottir H, Ding C, Pech N, et al. Retroviral-mediated gene transfer of gp91phox into bone marrow cells rescues defect in host defense against Aspergillus fumigatus in murine X-linked chronic granulomatous disease. Blood 1997; 89: 41-48.
    • (1997) Blood , vol.89 , pp. 41-48
    • Bjorgvinsdottir, H.1    Ding, C.2    Pech, N.3
  • 7
    • 17344369418 scopus 로고    scopus 로고
    • Correction of respiratory burst activity in X-linked chronic granulomatous cells to therapeutically relevant levels after gene transfer into bone marrow CD34+ cells
    • Becker S, Wasser S, Hauses M, et al. Correction of respiratory burst activity in X-linked chronic granulomatous cells to therapeutically relevant levels after gene transfer into bone marrow CD34+ cells. Hum Gen Ther 1998; 9: 1561-1570.
    • (1998) Hum Gen Ther , vol.9 , pp. 1561-1570
    • Becker, S.1    Wasser, S.2    Hauses, M.3
  • 8
    • 0344947883 scopus 로고    scopus 로고
    • Long-term correction of phagocyte NADPH oxidase activity by retroviral-mediated gene transfer in murine X-linked chronic granulomatous disease
    • Dinauer MC, Bjorgvinsdottir H, Ding C, et al. Long-term correction of phagocyte NADPH oxidase activity by retroviral-mediated gene transfer in murine X-linked chronic granulomatous disease. Blood 1999; 94: 914-922.
    • (1999) Blood , vol.94 , pp. 914-922
    • Dinauer, M.C.1    Bjorgvinsdottir, H.2    Ding, C.3
  • 9
    • 0030940510 scopus 로고    scopus 로고
    • Enhanced host defense after gene transfer in the murine p47phox-deficient model of chronic granulomatous disease
    • Mardiney MR, Jackson SH, Spratt SK, et al. Enhanced host defense after gene transfer in the murine p47phox-deficient model of chronic granulomatous disease. Blood 1997; 89: 2268-2275.
    • (1997) Blood , vol.89 , pp. 2268-2275
    • Mardiney, M.R.1    Jackson, S.H.2    Spratt, S.K.3
  • 10
    • 0028893203 scopus 로고
    • Mouse model of X-linked chronic granulomatous disease, an inherited defect in phagocyte superoxide production
    • Pollock JD, Williams DA, Gifford MA, et al. Mouse model of X-linked chronic granulomatous disease, an inherited defect in phagocyte superoxide production. Nat Genet 1995; 9: 202-209.
    • (1995) Nat Genet , vol.9 , pp. 202-209
    • Pollock, J.D.1    Williams, D.A.2    Gifford, M.A.3
  • 11
    • 12644293807 scopus 로고    scopus 로고
    • Prolonged production of NADPH oxidase-corrected granulocytes after gene therapy of chronic granulomatous disease
    • Malech HL, Maples PB, Whiting Theobald N, et al. Prolonged production of NADPH oxidase-corrected granulocytes after gene therapy of chronic granulomatous disease. Proc Natl Acad Sci U S A 1997; 94: 12133-12138.
    • (1997) Proc Natl Acad Sci U S A , vol.94 , pp. 12133-12138
    • Malech, H.L.1    Maples, P.B.2    Whiting Theobald, N.3
  • 12
    • 18544398264 scopus 로고    scopus 로고
    • Progress in gene therapy for chronic granulomatous disease
    • Malech HL. Progress in gene therapy for chronic granulomatous disease. J Infect Dis 1999; 179 (Suppl. 1); 318-325.
    • (1999) J Infect Dis , vol.179 , Issue.1 SUPPL. , pp. 318-325
    • Malech, H.L.1
  • 13
    • 0027158091 scopus 로고
    • Integration of murine leukemia virus DNA depends on mitosis
    • Roe T, Reynolds TC, Yu G, et al. Integration of murine leukemia virus DNA depends on mitosis. EMBO J 1993; 12: 2099-2108.
    • (1993) EMBO J , vol.12 , pp. 2099-2108
    • Roe, T.1    Reynolds, T.C.2    Yu, G.3
  • 14
    • 0032859385 scopus 로고    scopus 로고
    • Lentiviruses as gene delivery vectors
    • Federico M. Lentiviruses as gene delivery vectors. Curr Opin Biotechnol 1999; 10: 448-453.
    • (1999) Curr Opin Biotechnol , vol.10 , pp. 448-453
    • Federico, M.1
  • 15
    • 0033972740 scopus 로고    scopus 로고
    • Lentiviral vectors: Turning a deadly foe into a therapeutic agent
    • Trono D. Lentiviral vectors: turning a deadly foe into a therapeutic agent. Gene Ther 2000; 7: 20-23.
    • (2000) Gene Ther , vol.7 , pp. 20-23
    • Trono, D.1
  • 16
    • 0031666744 scopus 로고    scopus 로고
    • Development of a self-inactivating lentivirus vector
    • Miyoshi H, Blömer U, Takahashi M, et al. Development of a self-inactivating lentivirus vector. J Virol 1998; 72: 8150-8157.
    • (1998) J Virol , vol.72 , pp. 8150-8157
    • Miyoshi, H.1    Blömer, U.2    Takahashi, M.3
  • 17
    • 0031743608 scopus 로고    scopus 로고
    • Self-inactivating lentivirus vector for safe and efficient in vivo gene delivery
    • Zufferey R, Dull T, Mandel R, et al. Self-inactivating lentivirus vector for safe and efficient in vivo gene delivery. J Virol 1998; 72: 9873-9880.
    • (1998) J Virol , vol.72 , pp. 9873-9880
    • Zufferey, R.1    Dull, T.2    Mandel, R.3
  • 18
    • 0033613827 scopus 로고    scopus 로고
    • Transduction of human CD34+ cells that mediate long-term engraftment of NOD/SCID mice by HIV vectors
    • Miyoshi H, Smith KA, Mosier DE, et al. Transduction of human CD34+ cells that mediate long-term engraftment of NOD/SCID mice by HIV vectors. Science 1999; 283: 682-686.
    • (1999) Science , vol.283 , pp. 682-686
    • Miyoshi, H.1    Smith, K.A.2    Mosier, D.E.3
  • 19
    • 0032578385 scopus 로고    scopus 로고
    • HIV, but not murine leukemia virus, vectors mediate high efficiency gene transfer into freshly isolated G0/G1 human hematopoietic stem cells
    • Uchida N, Sutton RE, Friera AN, et al. HIV, but not murine leukemia virus, vectors mediate high efficiency gene transfer into freshly isolated G0/G1 human hematopoietic stem cells. Proc Natl Acad Sci U S A 1998; 95: 11939-11944.
    • (1998) Proc Natl Acad Sci U S A , vol.95 , pp. 11939-11944
    • Uchida, N.1    Sutton, R.E.2    Friera, A.N.3
  • 20
    • 0031747965 scopus 로고    scopus 로고
    • Human immunodeficiency virus type 1 vectors efficiently transduce human hematopoietic stem cells
    • Sutton RE, Wu HT, Rigg R, et al. Human immunodeficiency virus type 1 vectors efficiently transduce human hematopoietic stem cells. J Virol 1998; 72: 5781-5788.
    • (1998) J Virol , vol.72 , pp. 5781-5788
    • Sutton, R.E.1    Wu, H.T.2    Rigg, R.3
  • 21
    • 13044309472 scopus 로고    scopus 로고
    • Stable transduction of quiescent CD34(+)CD38(-) human hematopoietic cells by HIV-1-based lentiviral vectors
    • Case SS, Price MA, Jordan CT, et al. Stable transduction of quiescent CD34(+)CD38(-) human hematopoietic cells by HIV-1-based lentiviral vectors. Proc Natl Acad Sci U S A 1999; 96: 2988-2993.
    • (1999) Proc Natl Acad Sci U S A , vol.96 , pp. 2988-2993
    • Case, S.S.1    Price, M.A.2    Jordan, C.T.3
  • 22
    • 0033541513 scopus 로고    scopus 로고
    • Efficient transduction of human lymphocytes and CD34+ cells via human immunodeficiency virus-based gene transfer vectors
    • Douglas J, Kelly P, Evans JT, et al. Efficient transduction of human lymphocytes and CD34+ cells via human immunodeficiency virus-based gene transfer vectors. Hum Gene Ther 1999; 10: 935-945.
    • (1999) Hum Gene Ther , vol.10 , pp. 935-945
    • Douglas, J.1    Kelly, P.2    Evans, J.T.3
  • 23
    • 0029817964 scopus 로고    scopus 로고
    • High-level reconstitution of respiratory burst activity in a human X-linked chronic granulomatous disease (X-CGD) cell line and correction of murine X-CGD bone marrow cells by retroviral-mediated gene transfer of human gp91phox
    • Ding C, Kume A, Bjorgvinsdottir H, et al. High-level reconstitution of respiratory burst activity in a human X-linked chronic granulomatous disease (X-CGD) cell line and correction of murine X-CGD bone marrow cells by retroviral-mediated gene transfer of human gp91phox. Blood 1996; 88: 1834-1840.
    • (1996) Blood , vol.88 , pp. 1834-1840
    • Ding, C.1    Kume, A.2    Bjorgvinsdottir, H.3
  • 24
    • 0027374533 scopus 로고
    • Gene targeting of X chromosome-linked chronic granulomatous disease locus in a human myeloid leukemia cell line and rescue by expression of recombinant gp91phox
    • Zhen L, King AA, Xiao Y, et al. Gene targeting of X chromosome-linked chronic granulomatous disease locus in a human myeloid leukemia cell line and rescue by expression of recombinant gp91phox. Proc Natl Acad Sci U S A 1993; 90: 9832-9836.
    • (1993) Proc Natl Acad Sci U S A , vol.90 , pp. 9832-9836
    • Zhen, L.1    King, A.A.2    Xiao, Y.3
  • 25
    • 0023264655 scopus 로고
    • Characterization of a new human diploid myeloid leukemia cell line (PLB-985) with granulocytic and monocytic differentiation capacity
    • Tucker KA, Lilly MB, Heck L, et al. Characterization of a new human diploid myeloid leukemia cell line (PLB-985) with granulocytic and monocytic differentiation capacity. Blood 1987; 70: 372-378.
    • (1987) Blood , vol.70 , pp. 372-378
    • Tucker, K.A.1    Lilly, M.B.2    Heck, L.3
  • 26
    • 0029996147 scopus 로고    scopus 로고
    • In vivo gene delivery and stable transduction of nondividing cells by a lentiviral vector
    • Naldini L, Blomer U, Gallay P, et al. In vivo gene delivery and stable transduction of nondividing cells by a lentiviral vector. Science 1996; 272: 263-267.
    • (1996) Science , vol.272 , pp. 263-267
    • Naldini, L.1    Blomer, U.2    Gallay, P.3
  • 27
    • 0030819379 scopus 로고    scopus 로고
    • Multiply attenuated lentiviral vector achieves efficient gene delivery in vivo
    • Zufferey R, Nagy D, Mandel RJ, et al. Multiply attenuated lentiviral vector achieves efficient gene delivery in vivo. Nat Biotechnol 1997; 15: 871-875.
    • (1997) Nat Biotechnol , vol.15 , pp. 871-875
    • Zufferey, R.1    Nagy, D.2    Mandel, R.J.3
  • 28
    • 0023198590 scopus 로고
    • Monoclonal antibody 7D5 raised to cytochrome b558 of human neutrophils: Immunocytochemical detection of the antigen in peripheral phagocytes of normal subjects, patients with chronic granulomatous disease, and their carrier mothers
    • Nakamura M, Murakami M, Koga T, et al. Monoclonal antibody 7D5 raised to cytochrome b558 of human neutrophils: immunocytochemical detection of the antigen in peripheral phagocytes of normal subjects, patients with chronic granulomatous disease, and their carrier mothers. Blood 1987; 69: 1404-1408.
    • (1987) Blood , vol.69 , pp. 1404-1408
    • Nakamura, M.1    Murakami, M.2    Koga, T.3
  • 29
    • 0015783257 scopus 로고
    • The NBT slide test: A simple screening method for detecting chronic granulomatous disease and female carriers
    • Ochs HD, Igo RP. The NBT slide test: a simple screening method for detecting chronic granulomatous disease and female carriers. J Pediatr 1973; 83: 77-82.
    • (1973) J Pediatr , vol.83 , pp. 77-82
    • Ochs, H.D.1    Igo, R.P.2
  • 30
    • 0025294129 scopus 로고
    • A fast and easy method to determine the production of reactive oxygen intermediates by human and murine phagocytes using dihydrorhodamine 123
    • Emmendorffler A, Hecht M, Lohmann-Matthes ML, et al. A fast and easy method to determine the production of reactive oxygen intermediates by human and murine phagocytes using dihydrorhodamine 123. J Immunol Methods 1990; 131: 269-275.
    • (1990) J Immunol Methods , vol.131 , pp. 269-275
    • Emmendorffler, A.1    Hecht, M.2    Lohmann-Matthes, M.L.3
  • 31
    • 0029993858 scopus 로고    scopus 로고
    • Efficient transfer, integration and sustained long-term expression of the transgene in adult rat brains injected with a lentiviral vector
    • Naldini L, Blömer F, Gage FH, et al. Efficient transfer, integration and sustained long-term expression of the transgene in adult rat brains injected with a lentiviral vector. Proc Natl Acad Sci U S A 1996; 93: 11382-11388.
    • (1996) Proc Natl Acad Sci U S A , vol.93 , pp. 11382-11388
    • Naldini, L.1    Blömer, F.2    Gage, F.H.3
  • 32
    • 0023084783 scopus 로고
    • Analysis of mutation in human cells by using an Epstein-Barr virus shuttle system
    • DuBridge RB, Tang P, Hsia HC, et al. Analysis of mutation in human cells by using an Epstein-Barr virus shuttle system. Mol Cell Biol 1987; 7: 379-387.
    • (1987) Mol Cell Biol , vol.7 , pp. 379-387
    • DuBridge, R.B.1    Tang, P.2    Hsia, H.C.3
  • 33
    • 0031710033 scopus 로고    scopus 로고
    • A third-generation lentivirus vector with a conditional packaging system
    • Dull T, Zufferey R, Kelly M, et al. A third-generation lentivirus vector with a conditional packaging system. J Virol 1998; 72: 8463-8471.
    • (1998) J Virol , vol.72 , pp. 8463-8471
    • Dull, T.1    Zufferey, R.2    Kelly, M.3
  • 34
    • 0001221797 scopus 로고    scopus 로고
    • Marking and gene expression by a lentivirus vector in transplanted human and nonhuman primate CD34+ cells
    • An DS, Wersto RP, Agricola BA, et al. Marking and gene expression by a lentivirus vector in transplanted human and nonhuman primate CD34+ cells. J Virol 2000; 74: 1286-1295.
    • (2000) J Virol , vol.74 , pp. 1286-1295
    • An, D.S.1    Wersto, R.P.2    Agricola, B.A.3
  • 35
    • 0032796643 scopus 로고    scopus 로고
    • Interaction of human immunodeficiency virus-derived vectors with wild-type virus in transduced cells
    • Bukovsky A, Song J-P, Naldini L. Interaction of human immunodeficiency virus-derived vectors with wild-type virus in transduced cells. J Virol 1999; 73: 7087-7092.
    • (1999) J Virol , vol.73 , pp. 7087-7092
    • Bukovsky, A.1    Song, J.-P.2    Naldini, L.3
  • 36
    • 0032889454 scopus 로고    scopus 로고
    • A packaging cell line for lentivirus vectors
    • Kafri T, Van Praag H, Ouyang L, et al. A packaging cell line for lentivirus vectors. J Virol 1999; 73: 576-584.
    • (1999) J Virol , vol.73 , pp. 576-584
    • Kafri, T.1    Van Praag, H.2    Ouyang, L.3
  • 37
    • 0032956732 scopus 로고    scopus 로고
    • Transduction of human progenitor hematopoietic stem cells by human immunodeficient virus type 1-based vectors is cell cycle dependent
    • Sutton RE, Reitsma MJ, Uchida N, et al. Transduction of human progenitor hematopoietic stem cells by human immunodeficient virus type 1-based vectors is cell cycle dependent. J Virol 1999; 73: 3649-3660.
    • (1999) J Virol , vol.73 , pp. 3649-3660
    • Sutton, R.E.1    Reitsma, M.J.2    Uchida, N.3
  • 38
    • 0028170966 scopus 로고
    • Retrovirus-mediated reconstitution of respiratory burst activity in X-linked chronic granulomatous disease cells
    • Kume A, Dinauer MC. Retrovirus-mediated reconstitution of respiratory burst activity in X-linked chronic granulomatous disease cells. Blood 1994; 84: 3311-3316.
    • (1994) Blood , vol.84 , pp. 3311-3316
    • Kume, A.1    Dinauer, M.C.2
  • 39
    • 0032451162 scopus 로고    scopus 로고
    • Reconstitution of NADPH oxidase activity in human X-linked chronic granulomatous disease myeloid cells after stable gene transfer using a recombinant adeno-associated virus 2 vector
    • Li LL, Dinauer MC. Reconstitution of NADPH oxidase activity in human X-linked chronic granulomatous disease myeloid cells after stable gene transfer using a recombinant adeno-associated virus 2 vector. Blood Cells Mol Dis 1998; 24: 522-538.
    • (1998) Blood Cells Mol Dis , vol.24 , pp. 522-538
    • Li, L.L.1    Dinauer, M.C.2
  • 40
    • 0033951116 scopus 로고    scopus 로고
    • Variegation of retroviral vector gene expression in myeloid cells
    • Zentilin L, Qin G, Tafuro S, et al. Variegation of retroviral vector gene expression in myeloid cells. Gene Ther 2000; 7: 153-166.
    • (2000) Gene Ther , vol.7 , pp. 153-166
    • Zentilin, L.1    Qin, G.2    Tafuro, S.3


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