Prolonged production of NADPH oxidase-corrected granulocytes after gene therapy of chronic granulomatous disease

Proceedings of the National Academy of Sciences of the United States of America

Volumn 94, Issue 22, 1997, Pages 12133-12138

  Malech, Harry L ^a   Maples, Phillip B ^c   Whiting Theobald, Narda ^a   Linton, Gilda F ^a   Sekhsaria, Sudhir ^a   Vowells, Sarah J ^a   Li, Fei ^a   Miller, Judi A ^a   Decarlo, Ellen ^a   Holland, Steven M ^a   Leitman, Susan F ^b   Carter, Charles S ^b   Butz, Robert E ^b   Read, Elizabeth J ^b   Fleisher, Thomas A ^b   Schneiderman, Richard D ^c   Van Epps, Dennis E ^c   Spratt, S Kaye ^d   Maack, Christopher A ^d   Rokovich, Joseph A ^d   Cohen, Lawrence K ^d   Gallin, John I ^a   more..

^a NATIONAL INSTITUTE OF ALLERGY AND INFECTIOUS DISEASES   (United States)

^b NATIONAL INSTITUTES OF HEALTH   (United States)

^c BAXTER HEALTHCARE CORPORATION   (United States)

^d CELL GENESYS INC   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

CD34 ANTIGEN; COMPLEMENTARY DNA; REDUCED NICOTINAMIDE ADENINE DINUCLEOTIDE PHOSPHATE OXIDASE;

ARTICLE; CHRONIC GRANULOMATOUS DISEASE; CLINICAL ARTICLE; GENE THERAPY; GRANULOCYTE; HEMATOPOIETIC STEM CELL; HUMAN; HUMAN CELL; PHAGOCYTE DYSFUNCTION; PRIORITY JOURNAL; STEM CELL TRANSPLANTATION; TREATMENT OUTCOME;

ADOLESCENT; ADULT; ANTIGENS, CD34; BLOOD COMPONENT REMOVAL; FEMALE; FLOW CYTOMETRY; FOLLOW-UP STUDIES; GENE THERAPY; GRANULOCYTES; GRANULOMATOUS DISEASE, CHRONIC; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMANS; MALE; NADPH OXIDASE; PHOSPHOPROTEINS; RETROVIRIDAE; TRANSDUCTION, GENETIC;

ANIMALIA; UNIDENTIFIED RETROVIRUS;

EID: 12644293807     PISSN: 00278424     EISSN: None     Source Type: Journal    
DOI: 10.1073/pnas.94.22.12133     Document Type: Article

References (34)

1. Curnutte, J. T. (1993) Clin. Immunol. Immunopathol. 67, Suppl., 2-15.
2. Gallin, J. I. & Malech, H. L. (1990) J. Am. Med. Assoc. 263, 1533-1537.
3. DeLeo, F. R. & Quinn, M. T. (1996) J. Leukocyte Biol. 60, 677-691.
4. Malech, H. L. (1993) Curr. Opin. Hematol. 1, 123-132.
5. Clark, R. A., Malech, H. L., Gallin, J. I., Nunoi, H., Volpp, B. D., Pearson, D. W., Nauscef, W. M. & Curnutte, J. T. (1989) N. Engl. J. Med. 321, 647-652.
6. Calvino, M. C. Maldonado, M. S., Otheo, E., Munoz, A., Couselo, J. M. & Burgaleta, C. (1996) Eur. J. Pediatr. 155, 877-879.
7. Ho, C. M., Vowels, M. R., Lockwood, L. & Ziegler, J. B. (1996) Bone Marrow Transplant 18, 213-215.
8. Sekhsaria, S., Gallin, J. I., Linton, G. F., Mallory, R. M., Mulligan, R. C. & Malech, H. L. (1993) Proc. Natl. Acad. Sci. USA 90, 7446-7450.
9. Li, F., Linton, G. L., Sekhsaria, S., Whiting-Theobald, N., Katkin, J. P., Gallin, J. I. & Malech, H. L. (1994) Blood 84, 53-58.
10. Weil, W. M., Linton, G. F., Whiting-Theobald, N., Vowells, S. J., Rafferty, S. P., Li, F. & Malech, H. L. (1997) Blood 89, 1754-1761.
11. Bjorgvinsdottir, H., Ding, C., Pech, N., Gifford, M. A., Li, L. L. & Dinauer, M. C. (1997) Blood 89, 41-48.
12. Mardiney, M., III, Jackson, S. H., Spratt, S. K., Li, F., Holland, S. M. & Malech, H. L. (1997) Blood 89, 2268-2275.
13. Stewart, M. F., Crittenden, R. B., Lowry, P. A., Pearson-White, S. & Quesenberry, P. J. (1993) Blood 10, 2566-2571.
14. Casimir, C. M., Bu-Ghanim, H. N., Rodaway, A. R., Bentley, D. L., Rowe, P. & Segal, A. W. (1991) Proc. Natl. Acad. Sci. USA 88, 2753-2757.
15. Roos, D., de Boer, M., Kuribayashi, F., Meischl, C., Weening, R. S., Segal, A. W., Ahlin, A., Nernet, K., Hossle, J. P., Bernatowska-Matuszkiewicz, E. & Middleton-Price, H. (1996) Blood 87, 1663-1681.
16. Sekhsaria, S., Fleisher, T. A., Vowells, S., Brown, M., Miller, J., Gordon, I., Blaese, R. M., Dunbar, C. E., Leitman, S. & Malech, H. L. (1996) Blood 88, 1104-1112.
17. Lomax, K. J., Leto, T. L., Nunoi, H., Gallin, J. I. & Malech, H. L. (1989) Science 245, 409-412.
18. Volpp, B. D., Nauseef, W. M., Donelson, J. E., Moser, D. R. & Clark, R. A. (1989) Proc. Natl. Acad. Sci. USA 86, 7195-7199.
19. Vowells, S. J., Sekhsaria, S., Malech, H. L., Shalit, M. & Fieisher, T. A. (1994) J. Immunol. Methods 178, 89-97.
20. Vowells, S. J., Fleisher, T. A., Sekhsaria, S., Alling, D. W., Maguire, T. E. & Malech, H. L. (1996) J. Pediatr. 128, 104-107.
21. Buescher, E. S., Alling, D. W. & Gallin, J. I. (1985) J. Clin. Invest. 76, 1581-1584.
22. Ellem, K. A., O'Rourke, M. G., Johnson, G. R., Parry, G., Misko, I. S., Schmidt, C. W., Parsons, P. G., Burrows, S. R., Cross, S., Fell, A., Li, C. L., Bell, J. R., Dubois, P. J., Moss, D. J., Good, M. F., Kelso, A., Cohen, L. K., Dranoff, G. & Mulligan, R. C. (1997) Cancer Immunol. Immunother. 44, 10-20.
23. Sambrook, J., Fritsch, E. F. & Maniatis, T. (1989) Molecular Cloning: A Laboratory Manual (Cold Spring Harbor Lab. Press, Plainview, NY), 2nd Ed., Chap. 9, pp. 9.14-9.23.
24. Shalit, M., Sekhsaria, S., Li, F., Mauhorter, S., Mahanti, S. & Malech, H. L. (1996) J. Allergy Clin. Immunol. 98, 344-354.
25. Cook, P. C., Jiang, S., Chertkov, J. L., Fan, Y., Levere, R. D. & Abraham, N. G. (1996) Acta Haematol. 96, 57-63.
26. Dunbar, C. E., Cottler-Fox, M., O'Shaughnessy, J. A., Doren, S., Carter, C., Berenson, R., Brown, S., Moen, R. C., Greenblatt, J., Stewart, F. M., Leitman, S. F., Wilson, W. H., Cowan, K., Young, N. S. & Nienhuis, A. W. (1995) Blood 85, 3048-3057.
27. Brenner, M. K. (1997) J. Pediatr. Hematol. Oncol. 19, 1-6.
28. Walsh, C. E. Grompe, M., Vanin, E., Buchwald, M., Young, N. S., Neinhuis, A. W. & Liu, J. M. (1994) Blood 84, 453-459.
29. Blaese, R. M., Culver, K. W., Miller, A. D., Carter, C. S., Fleisher, T., Clerici, M., Shearer, G., Chang, L., Chiang, Y., Tolstoshev, P., Greenblatt, J. J., Rosenberg, S. A., Klein, H., Berger, M., Mullen, C. A., Ramsey, W. J., Muul, L., Morgan, R. A. & Anderson, W. F. (1995) Science 270, 475-480.
30. Bordignon, C., Notarangelo, L. D., Nobili, N., Ferrari, G., Lasorati, G., Panina, P., Mazzolari, E., Maggioni, D., Rossi, C., Servida, P., Ugazio, A. G. & Mavilio, F. (1995) Science 270, 470-475.
31. Kohn, D. B., Weinberg, K. I., Nolta, J. A., Heiss, L. N., Lenarsky, C., Crooks, G. M., Hanley, M. E., Annett, G., Brooks, J. S., El-Khoureiy, A., Lawrence, K., Wells, S., Moen, R. C., Bastian, J., Williams-Herman, D. E., Elder, M., Wara, D., Bowen, T., Hershfield, M. S., Mullen, C. A., Blaese, R. M. & Parkman, R. (1995) Nat. Med. 1, 1017-1023.
32. Mardiney, M., III & Malech, H. L. (1996) Blood 87, 4049-4056.
33. Mullen, C. A., Snitzer, K., Culver, K. W., Morgan, R. A., Anderson, W. F. & Blaese, R. M. (1996) Hum. Gene Ther. 7, 1123-1129.
34. Selvaggi, T. A., Walker, R. E. & Fleisher, T. A. (1997) Blood 89, 776-779.