Gene therapy progress and prospects: Cystic fibrosis

Gene Therapy

Volumn 9, Issue 20, 2002, Pages 1344-1350

  Griesenbach, U ^a   Ferrari, S ^a   Geddes, D M ^a   Alton, E W F W ^a  

^a NATIONAL HEART AND LUNG INSTITUTE   (United Kingdom)

Author keywords

Airway gene transfer; Cystic fibrosis; Gene therapy

Indexed keywords

ADENOVIRUS VECTOR; ANTISENSE OLIGONUCLEOTIDE; BETA GALACTOSIDASE; CHOLINERGIC RECEPTOR BLOCKING AGENT; GLYCOPYROLATE; LIPOSOME; MESSENGER RNA; MUCOLYTIC AGENT; NUCLEASE; OLIGONUCLEOTIDE; PLASMID DNA; PROTEASOME INHIBITOR; TRANSMEMBRANE CONDUCTANCE REGULATOR; UNCLASSIFIED DRUG;

ADENO ASSOCIATED VIRUS; ANIMAL EXPERIMENT; CELL NUCLEUS MEMBRANE; CLINICAL TRIAL; CONTROLLED CLINICAL TRIAL; CONTROLLED STUDY; CYSTIC FIBROSIS; CYTOPLASM; DRUG HALF LIFE; ENDOCYTOSIS; FEVER; GENE EXPRESSION; GENE THERAPY; GENE TRANSFER; GLYCOCALYX; HUMAN; MOLECULAR CLONING; MOUSE; MUCOCILIARY CLEARANCE; MUCUS; MUSCULOSKELETAL DISEASE; NONHUMAN; NONVIRAL GENE DELIVERY SYSTEM; PRIORITY JOURNAL; RESPIRATORY EPITHELIUM; REVIEW; SPLICEOSOME; TIGHT JUNCTION; TRANS SPLICING; TRANSGENE; VIRAL GENE DELIVERY SYSTEM;

ANIMALS; CLINICAL TRIALS, PHASE I; CYSTIC FIBROSIS; CYSTIC FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR; EPITHELIAL CELLS; GENE EXPRESSION; GENE TARGETING; GENE THERAPY; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; HUMANS; LUNG; OLIGONUCLEOTIDES, ANTISENSE;

ADENO-ASSOCIATED VIRUS; ADENO-ASSOCIATED VIRUS 2; ADENOVIRIDAE; ANIMALIA;

EID: 0036773525     PISSN: 09697128     EISSN: None     Source Type: Journal    
DOI: 10.1038/sj.gt.3301791     Document Type: Review

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