Targeting transgene expression for cystic fibrosis gene therapy

Molecular Therapy

Volumn 4, Issue 1, 2001, Pages 58-65

  Koehler, David R ^a,c   Hannam, Vicky ^a   Belcastro, Rosetta ^a   Steer, Brent ^a   Wen, Yanxia ^a   Post, Martin ^a,b,c   Downey, Gregory ^a,b,d   Tanswell, A Keith ^a,b   Hu, Jim ^a,b,c  

^a HOSPITAL FOR SICK CHILDREN   (Canada)

^b UNIVERSITY OF TORONTO   (Canada)

^c UNIVERSITY OF TORONTO   (Canada)

^d UNIVERSITY HEALTH NETWORK   (Canada)

Author keywords

Cystic fibrosis; Cytokeratin 18; DODAC:DOPE; Systemic gene therapy

Indexed keywords

AMMONIUM DERIVATIVE; BETA GALACTOSIDASE; CATION; CYTOKERATIN 18; DIOLEOYLPHOSPHATIDYLETHANOLAMINE; ELEMENT; LIPOSOME; LUCIFERASE; PLASMID DNA; TRANSMEMBRANE CONDUCTANCE REGULATOR; VIRUS DNA; VIRUS ENZYME; VIRUS VECTOR;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; BRONCHUS MUCOSA; COMPLEX FORMATION; CONTROLLED STUDY; CYSTIC FIBROSIS; CYTOMEGALOVIRUS; DRUG ACTIVITY; DRUG DISTRIBUTION; GALLBLADDER; GENE CASSETTE; GENE EXPRESSION; GENE MUTATION; GENE TARGETING; GENE THERAPY; GENETIC ANALYSIS; INTESTINE; KIDNEY; LIVER; LUNG ALVEOLUS; MOUSE; MUCUS GLAND; NONHUMAN; NOSE MUCOSA; PANCREAS; PROMOTER REGION; RESPIRATORY TRACT MUCOSA; SUBMUCOSA; TISSUE DISTRIBUTION; TRANSGENE; TRANSGENIC MOUSE;

ANIMALIA; BRONCHUS; CYTOMEGALOVIRUS; DNA VIRUSES; MUS MUSCULUS;

EID: 0034920977     PISSN: 15250016     EISSN: None     Source Type: Journal    
DOI: 10.1006/mthe.2001.0412     Document Type: Article

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