Adeno-associated virus vector-mediated minidystrophin gene therapy improves dystrophic muscle contractile function in mdx mice

Human Gene Therapy

Volumn 13, Issue 12, 2002, Pages 1451-1460

  Watchko, Jon ^a   O’day, Terry ^a   Wang, Bing ^b   Zhou, Liqiao ^b   Tang, Ying ^b   Li, Juan ^b   Xiao, Xiao ^b  

^a UNIVERSITY OF PITTSBURGH   (United States)

^b UNIVERSITY OF PITTSBURGH SCHOOL OF MEDICINE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOVIRUS VECTOR; DYSTROPHIN; MINIDYSTROPHIN; UNCLASSIFIED DRUG;

ADENO ASSOCIATED VIRUS; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; DRUG EFFICACY; FEMALE; GENE THERAPY; MOUSE; MUSCLE CONTRACTION; MUSCLE ISOMETRIC CONTRACTION; MUSCULAR DYSTROPHY; NONHUMAN; NUCLEOTIDE SEQUENCE; TIBIALIS ANTERIOR MUSCLE; TREATMENT OUTCOME;

ANIMALS; BLOTTING, WESTERN; DEPENDOVIRUS; DYSTROPHIN; FLUORESCENT ANTIBODY TECHNIQUE; GENE THERAPY; GENETIC VECTORS; MICE; MICE, INBRED C57BL; MICE, INBRED MDX; MUSCLE CONTRACTION; MUSCLE, SKELETAL; MUSCULAR DYSTROPHY, DUCHENNE;

ADENO-ASSOCIATED VIRUS; ADENOVIRIDAE; ANIMALIA; DNA VIRUSES;

EID: 0036385643     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/10430340260185085     Document Type: Article

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