Modular flexibility of dystrophin: Implications for gene therapy of Duchenne muscular dystrophy

Nature Medicine

Volumn 8, Issue 3, 2002, Pages 253-261

  Harper, Scott Q ^a,b   Hauser, Michael A ^b,d   DelloRusso, Christiana ^a,b   Duan, Dongsheng ^c   Crawford, Robert W ^a   Phelps, Stephanie F ^b   Harper, Hollie A ^a   Robinson, Ann S ^b   Engelhardt, John F ^c   Brooks, Susan V ^b   Chamberlain, Jeffrey S ^a,b  

^a UNIVERSITY OF WASHINGTON SCHOOL OF MEDICINE   (United States)

^b UNIVERSITY OF MICHIGAN MEDICAL SCHOOL   (United States)

^c UNIVERSITY OF IOWA   (United States)

^d DUKE UNIVERSITY MEDICAL CENTER   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOVIRUS VECTOR; DYSTROPHIN; GENE PRODUCT;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; DUCHENNE MUSCULAR DYSTROPHY; GENE THERAPY; HISTOPATHOLOGY; HUMAN; IMMUNOCOMPETENCE; MOLECULAR CLONING; MOUSE; NONHUMAN; PATHOPHYSIOLOGY; PRIORITY JOURNAL; PROMOTER REGION; PROTEIN ANALYSIS; PROTEIN STRUCTURE; TRANSGENIC MOUSE;

ANALYSIS OF VARIANCE; ANIMALS; DEPENDOVIRUS; DYSTROPHIN; GENE THERAPY; HUMANS; IMMUNOHISTOCHEMISTRY; MALE; MICE; MICE, INBRED MDX; MICE, TRANSGENIC; MUSCLE, SKELETAL; MUSCULAR DYSTROPHY, DUCHENNE; PROTEIN CONFORMATION;

ADENO-ASSOCIATED VIRUS; ADENOVIRIDAE; ANIMALIA; MUS MUSCULUS;

EID: 0036127393     PISSN: 10788956     EISSN: None     Source Type: Journal    
DOI: 10.1038/nm0302-253     Document Type: Article

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