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Volumn 74, Issue 3, 2000, Pages 1436-1442

Full functional rescue of a complete muscle (TA) in dystrophic hamsters by adeno-associated virus vector-directed gene therapy

Author keywords

[No Author keywords available]

Indexed keywords

VIRUS VECTOR;

EID: 0033958294     PISSN: 0022538X     EISSN: None     Source Type: Journal    
DOI: 10.1128/JVI.74.3.1436-1442.2000     Document Type: Article
Times cited : (87)

References (37)
  • 1
    • 0032416479 scopus 로고    scopus 로고
    • Viral mediated expression of insulin-like growth factor 1 blocks the aging-related loss of skeletal muscle function
    • Barton-Davis, E. R., D. I. Shoturma, A. Musaro, N. Rosenthal, and H. L. Sweeney. 1998. Viral mediated expression of insulin-like growth factor 1 blocks the aging-related loss of skeletal muscle function. Proc. Natl. Acad. Sci. USA 95:15603-15607.
    • (1998) Proc. Natl. Acad. Sci. USA , vol.95 , pp. 15603-15607
    • Barton-Davis, E.R.1    Shoturma, D.I.2    Musaro, A.3    Rosenthal, N.4    Sweeney, H.L.5
  • 3
    • 0029918603 scopus 로고    scopus 로고
    • Functional protection of dystrophic mouse (mdx) muscles after adenovirus-mediated transfer of a dystrophin minigene
    • Deconinck, N., T. Ragot, G. Marechal, M. Perricaudet, and J. M. Gillis. 1996. Functional protection of dystrophic mouse (mdx) muscles after adenovirus-mediated transfer of a dystrophin minigene. Proc. Natl. Acad. Sci. USA 93:3570-3574.
    • (1996) Proc. Natl. Acad. Sci. USA , vol.93 , pp. 3570-3574
    • Deconinck, N.1    Ragot, T.2    Marechal, G.3    Perricaudet, M.4    Gillis, J.M.5
  • 4
    • 0030723508 scopus 로고    scopus 로고
    • Expression of truncated utrophin leads to major functional improvements in dystrophin-deficient muscles of mice
    • Deconinck, N., J. Tinsley, F. De Backer, R. Fisher, D. Kahn, S. Phelps, K. Davies, and J. M. Gillis. 1997. Expression of truncated utrophin leads to major functional improvements in dystrophin-deficient muscles of mice. Nat. Med. 3:1216-1221.
    • (1997) Nat. Med. , vol.3 , pp. 1216-1221
    • Deconinck, N.1    Tinsley, J.2    De Backer, F.3    Fisher, R.4    Kahn, D.5    Phelps, S.6    Davies, K.7    Gillis, J.M.8
  • 5
    • 0031691257 scopus 로고    scopus 로고
    • Circular intermediates of recombinant adeno-associated virus have defined structural characteristics responsible for long-term episomal persistence in muscle tissue
    • Erratum, 73:861, 1999
    • Duan, D., P. Sharma, J. Yang, Y. Yue, L. Dudus, Y. Zhang, K. J. Fisher, and J. F. Engelhardt. 1998. Circular intermediates of recombinant adeno-associated virus have defined structural characteristics responsible for long-term episomal persistence in muscle tissue. J. Virol. 72:8568-8577. (Erratum, 73:861, 1999.)
    • (1998) J. Virol. , vol.72 , pp. 8568-8577
    • Duan, D.1    Sharma, P.2    Yang, J.3    Yue, Y.4    Dudus, L.5    Zhang, Y.6    Fisher, K.J.7    Engelhardt, J.F.8
  • 6
    • 0032506771 scopus 로고    scopus 로고
    • Polarity influences the efficiency of recombinant adenoassociated virus infection in differentiated airway epithelia
    • Duan, D., Y. Yue, Z. Yan, P. B. McCray, Jr., and J. F. Engelhardt. 1998. Polarity influences the efficiency of recombinant adenoassociated virus infection in differentiated airway epithelia. Hum. Gene Ther. 9:2761-2776.
    • (1998) Hum. Gene Ther. , vol.9 , pp. 2761-2776
    • Duan, D.1    Yue, Y.2    Yan, Z.3    McCray P.B., Jr.4    Engelhardt, J.F.5
  • 9
    • 0030902985 scopus 로고    scopus 로고
    • Stable gene transfer and expression of human blood coagulation factor IX after intramuscular injection of recombinant adeno-associated virus
    • Herzog, R. W., J. N. Hagstrom, S. H. Kung, S. J. Tai, J. M. Wilson, K. J. Fisher, and K. A. High. 1997. Stable gene transfer and expression of human blood coagulation factor IX after intramuscular injection of recombinant adeno-associated virus. Proc. Natl. Acad. Sci. USA 94:5804-5809.
    • (1997) Proc. Natl. Acad. Sci. USA , vol.94 , pp. 5804-5809
    • Herzog, R.W.1    Hagstrom, J.N.2    Kung, S.H.3    Tai, S.J.4    Wilson, J.M.5    Fisher, K.J.6    High, K.A.7
  • 10
    • 0033559741 scopus 로고    scopus 로고
    • Counting muscular dystrophies in the post-molecular census
    • Hoffman, E. P. 1999. Counting muscular dystrophies in the post-molecular census. J. Neurol. Sci. 164:3-6.
    • (1999) J. Neurol. Sci. , vol.164 , pp. 3-6
    • Hoffman, E.P.1
  • 11
    • 0026746706 scopus 로고
    • Dystrophin: The protein product of the duchene muscular dystrophy incus
    • Hoffman, E. P., R. H. Brown, and L. M. Kunkel. 1992. Dystrophin: the protein product of the Duchene muscular dystrophy Incus. Biotechnology 24:457-466.
    • (1992) Biotechnology , vol.24 , pp. 457-466
    • Hoffman, E.P.1    Brown, R.H.2    Kunkel, L.M.3
  • 13
    • 0000357470 scopus 로고
    • Primary, generalized polymyopathy and cardiac necrosis in an inbred line of Syrian hamsters
    • Homburger, F., J. R. Baker, C. W. Nixon, and R. Whitney. 1962. Primary, generalized polymyopathy and cardiac necrosis in an inbred line of Syrian hamsters. Med. Exp. 6:339-345.
    • (1962) Med. Exp. , vol.6 , pp. 339-345
    • Homburger, F.1    Baker, J.R.2    Nixon, C.W.3    Whitney, R.4
  • 14
    • 0031969428 scopus 로고
    • Transduction of dendritic cells by DNA viral vectors directs the immune response to transgene products in muscle fibers
    • Jooss, K., Y. Yang, K. J. Fisher, and J. M. Wilson. 1498. Transduction of dendritic cells by DNA viral vectors directs the immune response to transgene products in muscle fibers, J. Virol. 72:4212-4223.
    • (1498) J. Virol. , vol.72 , pp. 4212-4223
    • Jooss, K.1    Yang, Y.2    Fisher, K.J.3    Wilson, J.M.4
  • 17
    • 0032924996 scopus 로고    scopus 로고
    • rAAV vector-mediated sarcoglycan gene transfer in a hamster model for limb girdle muscular dystrophy
    • Li, J., D. Dressman, Y. P. Tsao, A. Sakamoto, E. P. Hoffman, and X. Xiao. 1999. rAAV vector-mediated sarcoglycan gene transfer in a hamster model for limb girdle muscular dystrophy. Gene Ther. 6:74-82.
    • (1999) Gene Ther. , vol.6 , pp. 74-82
    • Li, J.1    Dressman, D.2    Tsao, Y.P.3    Sakamoto, A.4    Hoffman, E.P.5    Xiao, X.6
  • 18
    • 0009057308 scopus 로고    scopus 로고
    • Stable transduetion of recomhinant adeno-associated virus into hematopoietic stem cells from normal and sickle cell patients
    • Lubovy, M., S. McCune, J. Y. Dong, J. F. Prchal, T. M. Townes, and J. T. Prchal. 1996. Stable transduetion of recomhinant adeno-associated virus into hematopoietic stem cells from normal and sickle cell patients. Biol. Blood Marrow Transplant 2:24-30.
    • (1996) Biol. Blood Marrow Transplant , vol.2 , pp. 24-30
    • Lubovy, M.1    McCune, S.2    Dong, J.Y.3    Prchal, J.F.4    Townes, T.M.5    Prchal, J.T.6
  • 19
    • 0023921967 scopus 로고
    • Regeneration of dystrophic muscle following multiple injections of hupivaccine
    • Martin, H., and M. Ontell. 1988. Regeneration of dystrophic muscle following multiple injections of hupivaccine. Muscle Nerve 11:588-596.
    • (1988) Muscle Nerve , vol.11 , pp. 588-596
    • Martin, H.1    Ontell, M.2
  • 22
    • 0031983639 scopus 로고    scopus 로고
    • Direct intramuscular injection with recombinant AAV vectors results in sustained expression in a dog model of hemophilia
    • Monahan, P. E., R. J. Samulski, J. Tazelaar, X. Xiao, T. C. Nichols, D. A. Bellinger, M. S. Read, and C. E. Walsh. 1998. Direct intramuscular injection with recombinant AAV vectors results in sustained expression in a dog model of hemophilia. Gene Ther. 5:40-49.
    • (1998) Gene Ther. , vol.5 , pp. 40-49
    • Monahan, P.E.1    Samulski, R.J.2    Tazelaar, J.3    Xiao, X.4    Nichols, T.C.5    Bellinger, D.A.6    Read, M.S.7    Walsh, C.E.8
  • 23
    • 0026525713 scopus 로고
    • Use of adeno-associated virus as a general transduclion vector for mammalian cells
    • Muzyczka, N. 1992. Use of adeno-associated virus as a general transduclion vector for mammalian cells. Curr. Top. Microbiol. Immunol. 158:97-129.
    • (1992) Curr. Top. Microbiol. Immunol. , vol.158 , pp. 97-129
    • Muzyczka, N.1
  • 24
    • 0032990410 scopus 로고    scopus 로고
    • Isolation of recombinant adeno-associated virus vector-cellular DNA junctions from mouse liver
    • Nakai, H., Y. Iwaki, M. A. Kay, and L. B. Couto. 1999. Isolation of recombinant adeno-associated virus vector-cellular DNA junctions from mouse liver. J. Virol. 73:5438-5447.
    • (1999) J. Virol. , vol.73 , pp. 5438-5447
    • Nakai, H.1    Iwaki, Y.2    Kay, M.A.3    Couto, L.B.4
  • 27
    • 0034008961 scopus 로고    scopus 로고
    • The use of adeno-associated virus to circumvent the maturation dependent viral transduction of muscle fiber
    • in press
    • Pruchnic, R., B. H. Cao, Z. Qu, X. Xiao, J. Li, R. J. Samulski, M. Epperly, and J. Huard. The use of adeno-associated virus to circumvent the maturation dependent viral transduction of muscle fiber. Hum. Gene Ther., in press.
    • Hum. Gene Ther.
    • Pruchnic, R.1    Cao, B.H.2    Qu, Z.3    Xiao, X.4    Li, J.5    Samulski, R.J.6    Epperly, M.7    Huard, J.8
  • 28
    • 0031471956 scopus 로고    scopus 로고
    • Both hypertrophic and dilated cardiomyopathies are caused by mutation of the same gene, delta-sarcoglycan, in hamster: An animal model of disrupted dystrophin-assodaled glycoprotein complex
    • Sakamoto, A., K. Ono, M. Abe, G. Jasmin, T. Eki, Y. Murakami, T. Masaki, T. Toyo-oka, and F. Hanaoka. 1997. Both hypertrophic and dilated cardiomyopathies are caused by mutation of the same gene, delta-sarcoglycan, in hamster: an animal model of disrupted dystrophin-assodaled glycoprotein complex. Proc. Natl. Acad. Sci. USA 94:13873-13878.
    • (1997) Proc. Natl. Acad. Sci. USA , vol.94 , pp. 13873-13878
    • Sakamoto, A.1    Ono, K.2    Abe, M.3    Jasmin, G.4    Eki, T.5    Murakami, Y.6    Masaki, T.7    Toyo-Oka, T.8    Hanaoka, F.9
  • 29
    • 0026070440 scopus 로고
    • Targeted integration of adeno-associated virus (AAV) into human chromosome 19
    • Erratum, 11:1228, 1992
    • Samulski, R. J., X. Zhu, X. Xiao, J. U. Brook, U. E. Housman, N. Epstein, and L. A. Hunter. 1991. Targeted integration of adeno-associated virus (AAV) into human chromosome 19. EMBO J. 10:3941-3950. (Erratum, 11:1228, 1992.)
    • (1991) EMBO J. , vol.10 , pp. 3941-3950
    • Samulski, R.J.1    Zhu, X.2    Xiao, X.3    Brook, J.U.4    Housman, U.E.5    Epstein, N.6    Hunter, L.A.7
  • 30
    • 0002988871 scopus 로고    scopus 로고
    • Production of recombinant adeno-associated viral vectors
    • N. Dracopoli, J. Haines, B. Krof, D. Moir, C. Seidman, and J. S. Seidman (ed.). John Wiley & Sons Ltd., New York, N.Y.
    • Snyder, R., X. Xiao, and R. J. Samulski. 1996. Production of recombinant adeno-associated viral vectors, p. 12.1.1-12.2.23. In N. Dracopoli, J. Haines, B. Krof, D. Moir, C. Seidman, and J. S. Seidman (ed.), Current protocols in human genetics. John Wiley & Sons Ltd., New York, N.Y.
    • (1996) Current Protocols in Human Genetics , pp. 1211-12223
    • Snyder, R.1    Xiao, X.2    Samulski, R.J.3
  • 32
    • 0030783172 scopus 로고    scopus 로고
    • Animal models for muscular dystrophy show different patterns of sarcolemmal disruption
    • Straub, V., J. A. Rafael, J. S. Chamberlain, and K. P. Campbell. 1997. Animal models for muscular dystrophy show different patterns of sarcolemmal disruption. J. Cell Biol. 139:375-385.
    • (1997) J. Cell Biol. , vol.139 , pp. 375-385
    • Straub, V.1    Rafael, J.A.2    Chamberlain, J.S.3    Campbell, K.P.4
  • 33
    • 0031906147 scopus 로고    scopus 로고
    • Membrane-associated heparan sulfate proteoglycan is a receptor for adeno-associated virus type 2 virions
    • Summerford, C., and R. J. Samulski. 1998. Membrane-associated heparan sulfate proteoglycan is a receptor for adeno-associated virus type 2 virions. J. Virol. 72:1438-1445.
    • (1998) J. Virol. , vol.72 , pp. 1438-1445
    • Summerford, C.1    Samulski, R.J.2
  • 34
    • 0031779697 scopus 로고    scopus 로고
    • Adeno-associated virus vector-mediated transgene integration into neurons and other nondividing cell targets
    • Wu, P., M. I. Phillips, J. Bui, and E. F. Terwilliger. 1998. Adeno-associated virus vector-mediated transgene integration into neurons and other nondividing cell targets. J. Virol. 72:5919-5926.
    • (1998) J. Virol. , vol.72 , pp. 5919-5926
    • Wu, P.1    Phillips, M.I.2    Bui, J.3    Terwilliger, E.F.4
  • 35
    • 0031104792 scopus 로고    scopus 로고
    • Gene transfer by adeno-associated virus vectors into the central nervous system
    • Xiao, X., J. Li, T. J. McCown, and R J. Samulski. 1997. Gene transfer by adeno-associated virus vectors into the central nervous system. Exp. Neurol. 144:113-124.
    • (1997) Exp. Neurol. , vol.144 , pp. 113-124
    • Xiao, X.1    Li, J.2    McCown, T.J.3    Samulski, R.J.4
  • 36
    • 0029843596 scopus 로고    scopus 로고
    • Efficient long-term gene transfer into muscle tissue of immunocompetent mice by adeno-associated virus vector
    • Xiao, X., J. Li, and R. J. Samulski. 1996. Efficient long-term gene transfer into muscle tissue of immunocompetent mice by adeno-associated virus vector. J. Virol. 70:8098-8108.
    • (1996) J. Virol. , vol.70 , pp. 8098-8108
    • Xiao, X.1    Li, J.2    Samulski, R.J.3
  • 37
    • 2642642141 scopus 로고    scopus 로고
    • Production of high-liter recombinant adeno-associated virus vectors in the absence of helper adenovirus
    • Xiao, X., J. Li, and R. J. Samulski. 1998. Production of high-liter recombinant adeno-associated virus vectors in the absence of helper adenovirus. J. Virol. 72:2224-2232.
    • (1998) J. Virol. , vol.72 , pp. 2224-2232
    • Xiao, X.1    Li, J.2    Samulski, R.J.3


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