Full functional rescue of a complete muscle (TA) in dystrophic hamsters by adeno-associated virus vector-directed gene therapy

Journal of Virology

Volumn 74, Issue 3, 2000, Pages 1436-1442

  Xiao, Xiao ^a,e   Li, Juan ^a   Tsao, Yeou Ping ^a,c   Dressman, Devin ^a   Hoffman, Eric P ^a,d   Watchko, Jon F ^a,b  

^a UNIVERSITY OF PITTSBURGH SCHOOL OF MEDICINE   (United States)

^b UNIVERSITY OF PITTSBURGH   (United States)

^c NATIONAL DEFENSE MEDICAL CENTER   (Taiwan)

^d CHILDREN'S NATIONAL MEDICAL CENTER   (United States)

^e UNIVERSITY OF PITTSBURGH   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

VIRUS VECTOR;

ADENO ASSOCIATED VIRUS; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; GENE EXPRESSION; GENE MUTATION; GENE TARGETING; GENE THERAPY; LIMB GIRDLE MUSCULAR DYSTROPHY; MUSCLE MASS; MUSCLE STRENGTH; MUSCLE TWITCH; NONHUMAN; PRIORITY JOURNAL;

ANIMALS; CRICETINAE; CYTOSKELETAL PROTEINS; DEPENDOVIRUS; DISEASE MODELS, ANIMAL; GENE THERAPY; GENETIC VECTORS; MEMBRANE GLYCOPROTEINS; MESOCRICETUS; MUSCLE CONTRACTION; MUSCLE, SKELETAL; MUSCULAR DYSTROPHIES; SARCOGLYCANS; TREATMENT OUTCOME;

EID: 0033958294     PISSN: 0022538X     EISSN: None     Source Type: Journal    
DOI: 10.1128/JVI.74.3.1436-1442.2000     Document Type: Article

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