Rescue of Skeletal Muscles of γ-Sarcoglycan- Deficient Mice with Adeno-Associated Virus-Mediated Gene Transfer

Molecular Therapy

Volumn 1, Issue 2, 2000, Pages 119-129

  Cordier, Laurence ^a   Hack, Andrew A ^b   Scott, Marion O ^a   Barton Davis, Elisabeth R ^a   Gao, Guang Ping ^c   Wilson, James M ^c   McNally, Elizabeth M ^b   Sweeney, H Lee ^a  

^a UNIVERSITY OF PENNSYLVANIA   (United States)

^b UNIVERSITY OF CHICAGO   (United States)

^c UNIVERSITY OF PENNSYLVANIA   (United States)

Author keywords

Creatine kinase promoter; Gene therapy; Limb girdle muscular dystrophy

Indexed keywords

COMPLEMENTARY DNA; CREATINE KINASE; CYTOSKELETON PROTEIN; MEMBRANE PROTEIN; SARCOGLYCAN;

ADENO ASSOCIATED VIRUS; AGE; ANIMAL; ARTICLE; CELL LINE; ENHANCER REGION; ENZYMOLOGY; EXON; FIBROBLAST; FLUORESCENT ANTIBODY TECHNIQUE; GENE TRANSFER; GENE VECTOR; GENETIC RECOMBINATION; GENETIC TRANSDUCTION; GENETICS; HUMAN; INTRON; METABOLISM; MOUSE; MOUSE MUTANT; MUSCULAR DYSTROPHY; NEWBORN; PHENOTYPE; PROMOTER REGION; SKELETAL MUSCLE; TIME; WESTERN BLOTTING;

AGE FACTORS; ANIMALS; ANIMALS, NEWBORN; BLOTTING, WESTERN; CELL LINE; CREATINE KINASE; CYTOSKELETAL PROTEINS; DEPENDOVIRUS; DNA, COMPLEMENTARY; ENHANCER ELEMENTS (GENETICS); EXONS; FIBROBLASTS; FLUORESCENT ANTIBODY TECHNIQUE; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; HUMANS; INTRONS; MEMBRANE GLYCOPROTEINS; MICE; MICE, MUTANT STRAINS; MUSCLE, SKELETAL; MUSCULAR DYSTROPHIES; PHENOTYPE; PROMOTER REGIONS (GENETICS); RECOMBINATION, GENETIC; SARCOGLYCANS; TIME FACTORS; TRANSDUCTION, GENETIC;

EID: 0034138226     PISSN: 15250016     EISSN: None     Source Type: Journal    
DOI: 10.1006/mthe.1999.0019     Document Type: Article

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