rAAV vector-mediated sarcogylcan gene transfer in a hamster model for limb girdle muscular dystrophy

Gene Therapy

Volumn 6, Issue 1, 1999, Pages 74-82

  Li, J ^a   Dressman, D ^a   Tsao, Y P ^a   Sakamoto, A ^a   Hoffman, E P ^a   Xiao, X ^a  

^a NONE

Author keywords

Bio14.6 hamster; Limb girdle muscular dystrophy; rAAV; Sarcoglycan

Indexed keywords

SARCOGLYCAN; VIRUS VECTOR;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; CYTOPLASM; GENE MUTATION; GENE THERAPY; GENE TRANSFER; HAMSTER; LIMB GIRDLE MUSCULAR DYSTROPHY; MUSCLE FIBER MEMBRANE; NONHUMAN; PRIORITY JOURNAL;

ANIMALS; BLOTTING, WESTERN; CRICETINAE; CYTOSKELETAL PROTEINS; DEPENDOVIRUS; GENE EXPRESSION; GENE THERAPY; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; HUMANS; INJECTIONS, INTRAMUSCULAR; MEMBRANE GLYCOPROTEINS; MICROSCOPY, FLUORESCENCE; MUSCLE, SKELETAL; MUSCULAR DYSTROPHIES; REGENERATION; SARCOGLYCANS;

ADENO-ASSOCIATED VIRUS; ANIMALIA; CRICETINAE;

EID: 0032924996     PISSN: 09697128     EISSN: None     Source Type: Journal    
DOI: 10.1038/sj.gt.3300830     Document Type: Article

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