Adeno-associated virus vector gene transfer and sarcolemmal expression of a 144 kDa micro-dystrophin effectively restores the dystrophin-associated protein complex and inhibits myofibre degeneration in nude/mdx mice

Human Molecular Genetics

Volumn 11, Issue 7, 2002, Pages 733-741

  Fabb, Stewart A ^a   Wells, Dominic J ^b   Serpente, Patricia ^a,c   Dickson, George ^a  

^a UNIVERSITY OF LONDON   (United Kingdom)

^b CHARING CROSS HOSPITAL   (United Kingdom)

^c The Ridgeway   (United Kingdom)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOVIRUS VECTOR; COMPLEMENTARY DNA; DYSTROPHIN; FENTANYL; MIDAZOLAM; RECOMBINANT PROTEIN; RETROVIRUS VECTOR; UTROPHIN;

ADENO ASSOCIATED VIRUS; ANIMAL CELL; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; CYTOMEGALOVIRUS; DRUG TISSUE LEVEL; DUCHENNE MUSCULAR DYSTROPHY; GENE CONSTRUCT; GENE DELIVERY SYSTEM; GENE EXPRESSION; GENE MUTATION; GENE THERAPY; GENE TRANSFER; GENETIC TRANSDUCTION; IMMUNOGENICITY; IN VIVO STUDY; MOUSE; MUSCLE ATROPHY; MUSCLE FIBRIL; NONHUMAN; PRIORITY JOURNAL; SARCOLEMMA; SKELETAL MUSCLE; X CHROMOSOME RECESSIVE DISORDER;

ADENO-ASSOCIATED VIRUS; ADENOVIRIDAE; ANIMALIA; CUCUMBER MOSAIC VIRUS; CYTOMEGALOVIRUS; UNIDENTIFIED RETROVIRUS;

EID: 0036537529     PISSN: 09646906     EISSN: None     Source Type: Journal    
DOI: 10.1093/hmg/11.7.733     Document Type: Article

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