Gene therapy strategies for X-linked adrenoleukodystrophy

Current Opinion in Molecular Therapeutics

Volumn 3, Issue 4, 2001, Pages 357-361

  Cartier, N ^a  

^a HÔPITAL SAINT VINCENT DE PAUL   (France)

Author keywords

AAV; Adrenoleukodystrophy; Hematopoietic stem cells; Lentiviral vector

Indexed keywords

ABC TRANSPORTER; MYELIN; VERY LONG CHAIN FATTY ACID; VIRUS VECTOR;

ADRENOLEUKODYSTROPHY; ADULT; AGE; ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; AUTOTRANSPLANTATION; BRAIN DISEASE; CENTRAL NERVOUS SYSTEM DISEASE; CHILD; CONTROLLED STUDY; DEMYELINATING DISEASE; DISEASE PREDISPOSITION; DISEASE SEVERITY; FEMALE; GENE MUTATION; GENE TARGETING; GENE THERAPY; GENE TRANSFER; GENETIC ANALYSIS; GENETIC CODE; GENETIC DISORDER; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMAN; HUMAN CELL; INCIDENCE; LENTIVIRINAE; MALE; MICROGLIA; MORTALITY; MOUSE; NONHUMAN; OLIGODENDROGLIA; PARAPLEGIA; PATIENT CARE; PEROXISOME; SEX DIFFERENCE; SPINAL CORD DISEASE; TARGET CELL; TREATMENT PLANNING; X CHROMOSOME LINKED DISORDER;

ADRENOLEUKODYSTROPHY; BRAIN; GENE THERAPY; GENE TRANSFER, HORIZONTAL; HEMATOPOIETIC STEM CELLS; HUMANS;

EID: 0034879599     PISSN: 14648431     EISSN: None     Source Type: Journal    
DOI: None     Document Type: Article

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