Long-Term and Significant Correction of Brain Lesions in Adult Mucopolysaccharidosis Type VII Mice Using Recombinant AAV Vectors

Molecular Therapy

Volumn 1, Issue 1, 2000, Pages 63-70

  Bosch, Assumpció ^a   Perret, Emmanuelle ^b   Desmaris, Nathalie ^a   Heard, Jean Michel ^a  

^a CNRS   (France)

^b INSTITUT PASTEUR   (France)

Author keywords

[No Author keywords available]

Indexed keywords

BETA GLUCURONIDASE; COMPLEMENTARY DNA; MESSENGER RNA;

ADENO ASSOCIATED VIRUS; ANIMAL; ARTICLE; BRAIN; CYTOCHEMISTRY; ENZYMOLOGY; GENE EXPRESSION; GENE THERAPY; GENE VECTOR; GENETICS; HUMAN; IN SITU HYBRIDIZATION; INJECTION; METABOLISM; METHODOLOGY; MOUSE; MOUSE MUTANT; MUCOPOLYSACCHARIDOSIS TYPE 7; PATHOLOGY;

ANIMALS; BRAIN; DEPENDOVIRUS; DNA, COMPLEMENTARY; GENE EXPRESSION; GENE THERAPY; GENETIC VECTORS; GLUCURONIDASE; HISTOCYTOCHEMISTRY; HUMANS; IN SITU HYBRIDIZATION; INJECTIONS; MICE; MICE, MUTANT STRAINS; MUCOPOLYSACCHARIDOSIS VII; RNA, MESSENGER;

EID: 0033642895     PISSN: 15250016     EISSN: None     Source Type: Journal    
DOI: 10.1006/mthe.1999.0005     Document Type: Article

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