Recent developments in targeting protein misfolding diseases

Bioorganic and Medicinal Chemistry Letters

Volumn 23, Issue 7, 2013, Pages 1935-1944

  Denny, Rajiah Aldrin ^a   Gavrin, Lori Krim ^a   Saiah, Eddine ^a  

^a PFIZER INC   (United States)

Author keywords

Chaperone; Cystic fibrosis; Gaucher disease; Protein misfolding; Proteostasis; Serum amyloid P (SAP); Toxic oligomer

Indexed keywords

ALPHA GALACTOSIDASE; CELASTROL; CHAPERONE; ENZYME; GLUCOSYLCERAMIDASE; GLUCOSYLCERAMIDE; GONADORELIN; ISOFAGOMINE; IVACAFTOR; LUMACAFTOR; OLIGOMER; PYRROLIDINE DERIVATIVE; RHODOPSIN; RO 63 8695; SERUM AMYLOID A; TRANSCRIPTION FACTOR; UNCLASSIFIED DRUG;

AMYLOIDOSIS; CHRONIC OBSTRUCTIVE LUNG DISEASE; CREUTZFELDT JAKOB DISEASE; CYSTIC FIBROSIS; ENZYME REPLACEMENT; FABRY DISEASE; GAUCHER DISEASE; HUMAN; HUNTINGTON CHOREA; HYPOGONADOTROPIC HYPOGONADISM; LYSOSOME STORAGE DISEASE; NON INSULIN DEPENDENT DIABETES MELLITUS; NONHUMAN; PARKINSON DISEASE; PROTEIN FOLDING; PROTEIN HOMEOSTASIS; PROTEIN TARGETING; RENAL DIABETES; RETINITIS PIGMENTOSA; REVIEW;

HUMANS; MODELS, MOLECULAR; PROTEIN FOLDING; PROTEOSTASIS DEFICIENCIES; SMALL MOLECULE LIBRARIES; THERMODYNAMICS;

EID: 84875230719     PISSN: 0960894X     EISSN: 14643405     Source Type: Journal    
DOI: 10.1016/j.bmcl.2013.01.089     Document Type: Review

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