Gene Therapy in Skeletal Muscle Mediated by Adeno-Associated Virus Vectors

Methods in Molecular Biology

Volumn 807, Issue , 2011, Pages 119-140

  Qiao, Chunping ^a   Koo, Taeyoung ^b   Li, Juan ^a   Xiao, Xiao ^a   Dickson, J George ^b  

^a UNIVERSITY OF NORTH CAROLINA   (United States)

^b QUEEN MARY UNIVERSITY OF LONDON   (United Kingdom)

Author keywords

Adeno associated virus; Dystrophin; Muscle directed gene therapy; Muscular dystrophy; Sarcoglycans; Transgene expression; Vector dosage; Vector mediated gene delivery

Indexed keywords

DYSTROPHIN;

ADENO ASSOCIATED VIRUS; ANIMAL; ARTICLE; C57BL MOUSE; DOG; GENE THERAPY; GENE VECTOR; GENETICS; METABOLISM; METHODOLOGY; MOUSE; POLYMERASE CHAIN REACTION; SKELETAL MUSCLE; WESTERN BLOTTING;

ANIMALS; BLOTTING, WESTERN; DEPENDOVIRUS; DOGS; DYSTROPHIN; GENE THERAPY; GENETIC VECTORS; MICE; MICE, INBRED C57BL; MUSCLE, SKELETAL; POLYMERASE CHAIN REACTION;

EID: 83455225649     PISSN: 10643745     EISSN: 19406029     Source Type: Book Series    
DOI: 10.1007/978-1-61779-370-7_5     Document Type: Chapter

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