Efficient AAV1-AAV2 hybrid vector for gene therapy of hemophilia

Human Gene Therapy

Volumn 17, Issue 1, 2006, Pages 46-54

  Hauck, Bernd ^a   Xu, Ray Ruian ^b   Xie, Jing ^a   Wu, Wenman ^c   Ding, Qiulan ^c   Sipler, Matthew ^a   Wang, Hongli ^c   Chen, Ling ^d   Wright, J Fraser ^a   Xiao, Weidong ^a,e  

^a HOSPITAL OF THE UNIVERSITY OF PENNSYLVANIA   (United States)

^b UNIVERSITY OF HONG KONG   (Hong Kong)

^c SHANGHAI SECOND MEDICAL UNIVERSITY   (China)

^d GUANGZHOU INSTITUTES OF BIOMEDICINE AND HEALTH   (China)

^e CHILDREN S HOSPITAL OF PHILADELPHIA   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

CD4 ANTIGEN; GENE PRODUCT; HEPARIN; HEPARIN BINDING PROTEIN; PARVOVIRUS VECTOR; PROTEIN FIX; SEPHAROSE; UNCLASSIFIED DRUG;

AMINO ACID SEQUENCE; ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; CONTROLLED STUDY; DNA DETERMINATION; EMBRYO; GENE EXPRESSION PROFILING; GENE TRANSFER; HEMOPHILIA; HUMAN; HUMAN CELL; IN VITRO STUDY; IN VIVO STUDY; KNOCKOUT MOUSE; MOUSE; NONHUMAN; PARVOVIRUS 1 VECTOR; PARVOVIRUS 2 VECTOR; SEROTYPE; TRANSGENE; VIRAL GENE DELIVERY SYSTEM; VIRAL GENE THERAPY; VIRUS HYBRID; VIRUS PARTICLE; VIRUS STRAIN;

ANIMALS; CAPSID PROTEINS; CELLS, CULTURED; CERCOPITHECUS AETHIOPS; COS CELLS; DEPENDOVIRUS; FACTOR IX; GENE EXPRESSION; GENE THERAPY; GENETIC VECTORS; HELA CELLS; HEMOPHILIA B; HUMANS; MICE; MICE, KNOCKOUT; MOLECULAR SEQUENCE DATA; PHENOTYPE; SEQUENCE HOMOLOGY, AMINO ACID; TRANSDUCTION, GENETIC;

ADENO-ASSOCIATED VIRUS; ANIMALIA; MIRIDAE; PARVOVIRUS;

EID: 30744476548     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/hum.2006.17.46     Document Type: Article

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