Cord blood and bone marrow transplantation in inherited metabolic diseases: Scientific basis, current status and future directions

British Journal of Haematology

Volumn 148, Issue 3, 2010, Pages 356-372

  Prasad, Vinod K ^a   Kurtzberg, Joanne ^a  

^a DUKE UNIVERSITY   (United States)

Author keywords

Haematopoietic stem cell transplantation; Inherited metabolic diseases; Lysosomal and peroxisomal storage disease; Umbilical cord blood transplantation

Indexed keywords

GLYCOGEN; GLYCOPROTEIN; LYSOSOME ENZYME;

ADRENOLEUKODYSTROPHY; ALLOGENEIC HEMATOPOIETIC STEM CELL TRANSPLANTATION; ASPARTYLGLYCOSAMINURIA; BLOOD BRAIN BARRIER; BONE MARROW TRANSPLANTATION; CELL DIFFERENTIATION; CELL MIGRATION; CELL REGENERATION; CENTRAL NERVOUS SYSTEM; CENTRAL NERVOUS SYSTEM DISEASE; COGNITIVE DEFECT; CORD BLOOD STEM CELL TRANSPLANTATION; DISEASE COURSE; ENZYME REPLACEMENT; FABRY DISEASE; FARBER DISEASE; FUCOSIDOSIS; GAUCHER DISEASE; GM1 GANGLIOSIDOSIS; HEMATOPOIETIC STEM CELL; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMAN; HUNTER SYNDROME; HURLER SYNDROME; LESCH NYHAN SYNDROME; LEUKODYSTROPHY; LIPOFUSCINOSIS; LYSOSOME; MANNOSIDOSIS; MAROTEAUX LAMY SYNDROME; METABOLIC DISORDER; MORBIDITY; MORQUIO SYNDROME; MOTONEURON; MUCOLIPIDOSIS TYPE 2; MUCOPOLYSACCHARIDOSIS; NIEMANN PICK DISEASE; OUTCOME ASSESSMENT; PELIZAEUS MERZBACHER DISEASE; PRIORITY JOURNAL; QUALITY OF LIFE; REVIEW; SANDHOFF DISEASE; SANFILIPPO SYNDROME; SURVIVAL; TAY SACHS DISEASE; TREATMENT OUTCOME; TREATMENT RESPONSE; WOLMAN DISEASE;

ANIMALS; BONE MARROW TRANSPLANTATION; CHILD; CHILD, PRESCHOOL; COGNITION DISORDERS; CORD BLOOD STEM CELL TRANSPLANTATION; ENZYME REPLACEMENT THERAPY; HUMANS; INFANT; INFANT, NEWBORN; METABOLISM, INBORN ERRORS; MICE; MUCOPOLYSACCHARIDOSIS I;

EID: 74049108936     PISSN: 00071048     EISSN: 13652141     Source Type: Journal    
DOI: 10.1111/j.1365-2141.2009.07974.x     Document Type: Review

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