Outcomes of Unrelated Umbilical Cord Blood Transplantation for X-Linked Adrenoleukodystrophy

Biology of Blood and Marrow Transplantation

Volumn 13, Issue 6, 2007, Pages 665-674

  Beam, Donald ^a   Poe, Michele D ^b   Provenzale, James M ^a   Szabolcs, Paul ^a   Martin, Paul L ^a   Prasad, Vinod ^a   Parikh, Suhag ^a   Driscoll, Tim ^a   Mukundan, Srini ^a   Kurtzberg, Joanne ^a   Escolar, Maria L ^c  

^a DUKE UNIVERSITY MEDICAL CENTER   (United States)

^b UNIVERSITY OF NORTH CAROLINA   (United States)

^c UNIVERSITY OF NORTH CAROLINA SCHOOL OF MEDICINE   (United States)

Author keywords

Adrenoleukodystrophy; Neurodevelopmental outcomes; Umbilical cord blood transplantation

Indexed keywords

ANTIBIOTIC AGENT; BUSULFAN; CYCLOPHOSPHAMIDE; CYCLOSPORIN; DACLIZUMAB; HEPARIN; HLA ANTIGEN; IMMUNOGLOBULIN; LONG CHAIN FATTY ACID; MESNA; METHYLPREDNISOLONE; PHENYTOIN; RECOMBINANT GRANULOCYTE COLONY STIMULATING FACTOR; TACROLIMUS; THYMOCYTE ANTIBODY; VERY LONG CHAIN FATTY ACID;

ACUTE GRAFT VERSUS HOST DISEASE; ADRENOLEUKODYSTROPHY; ALLOGENIC BONE MARROW TRANSPLANTATION; ARTICLE; BODY WEIGHT; CHILD; CHRONIC GRAFT VERSUS HOST DISEASE; CLINICAL ARTICLE; COGNITION; CONTINUOUS INFUSION; CONTROLLED STUDY; CORD BLOOD STEM CELL TRANSPLANTATION; CORRELATION ANALYSIS; DEATH; DEMYELINATION; DETERIORATION; DISEASE COURSE; DRUG PULSE THERAPY; DRUG SUBSTITUTION; DRUG WITHDRAWAL; ELECTROENCEPHALOGRAPHY; ENGRAFTMENT; EVOKED AUDITORY RESPONSE; EVOKED VISUAL RESPONSE; FATTY ACID METABOLISM; FEBRILE NEUTROPENIA; FOLLOW UP; GRAFT SURVIVAL; GRAFT VERSUS HOST REACTION; HEMORRHAGIC CYSTITIS; HLA MATCHING; HUMAN; INFANT; LIVER VENOOCCLUSIVE DISEASE; LOW DRUG DOSE; MALE; MOTOR PERFORMANCE; MYELOABLATIVE CONDITIONING; NERVE CELL DIFFERENTIATION; NERVE CONDUCTION; NERVE DEGENERATION; NERVOUS SYSTEM FUNCTION; NEUROIMAGING; NEUROPHYSIOLOGY; OUTCOME ASSESSMENT; OVERALL SURVIVAL; PATIENT REFERRAL; PREDICTION; SCORING SYSTEM; SEIZURE; STATISTICAL SIGNIFICANCE; SURVIVAL RATE; SYMPTOM; TREATMENT OUTCOME; UNIVERSITY HOSPITAL; X CHROMOSOME LINKED DISORDER;

ADRENOLEUKODYSTROPHY; CHILD; CHILD, PRESCHOOL; COGNITION; CORD BLOOD STEM CELL TRANSPLANTATION; GRAFT SURVIVAL; GRAFT VS HOST DISEASE; HISTOCOMPATIBILITY TESTING; HUMANS; LANGUAGE DEVELOPMENT; MALE; MOTOR ACTIVITY; MYELOABLATIVE AGONISTS; NEUROPHYSIOLOGY; PREDICTIVE VALUE OF TESTS; SURVIVAL RATE; TRANSPLANTATION CONDITIONING; TREATMENT OUTCOME;

EID: 34248668484     PISSN: 10838791     EISSN: 15236536     Source Type: Journal    
DOI: 10.1016/j.bbmt.2007.01.082     Document Type: Article

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