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Volumn 41, Issue 4, 2008, Pages 349-353

Allogeneic hematopoietic cell transplantation (HCT) in Hurler's syndrome using a reduced intensity preparative regimen

Author keywords

[No Author keywords available]

Indexed keywords

ADRENALIN; ALANINE AMINOTRANSFERASE; ALEMTUZUMAB; AMPHOTERICIN B LIPID COMPLEX; ANTIBIOTIC AGENT; BUSULFAN; CASPOFUNGIN; CHLOROTHIAZIDE; COTRIMOXAZOLE; CYCLOPHOSPHAMIDE; CYCLOSPORIN; DOPAMINE; ENALAPRIL; FLUCONAZOLE; FLUDARABINE; GRANULOCYTE COLONY STIMULATING FACTOR; LARONIDASE; LIVER ENZYME; MELPHALAN; METHOTREXATE; METHYLPREDNISOLONE; MILRINONE; PENTAMIDINE; VORICONAZOLE;

EID: 40249111835     PISSN: 02683369     EISSN: 14765365     Source Type: Journal    
DOI: 10.1038/sj.bmt.1705926     Document Type: Article
Times cited : (20)

References (33)
  • 1
    • 18444393851 scopus 로고    scopus 로고
    • Storage diseases of the reticuloendothelial system
    • Nathan DG, Orkin SH, Ginsburg D, Look AT eds, 6th edn. Saunders: Philadelphia
    • Kolodny EH, Charria-Ortiz G. Storage diseases of the reticuloendothelial system. In: Nathan DG, Orkin SH, Ginsburg D, Look AT (eds). Nathan and Oski's Hematology of Infancy and Childhood, 6th edn. Saunders: Philadelphia, 2003, pp 1399-1454.
    • (2003) Nathan and Oski's Hematology of Infancy and Childhood , pp. 1399-1454
    • Kolodny, E.H.1    Charria-Ortiz, G.2
  • 2
    • 11144326098 scopus 로고    scopus 로고
    • Hematopoietic cell transplantation for storage diseases
    • Blume KG, Forman SJ, Appelbaum FR eds, 3rd edn. Blackwell Publishing Ltd, Oxford
    • Peters C. Hematopoietic cell transplantation for storage diseases. In: Blume KG, Forman SJ, Appelbaum FR (eds). Thomas' Hematopoietic Cell Transplantation, 3rd edn. Blackwell Publishing Ltd.: Oxford, 2004, pp 1455-1470.
    • (2004) Thomas' Hematopoietic Cell Transplantation , pp. 1455-1470
    • Peters, C.1
  • 3
    • 11144325072 scopus 로고    scopus 로고
    • Allogeneic stem cell transplantation for the treatment of lysosomal and peroxisomal metabolic diseases
    • Krivit W. Allogeneic stem cell transplantation for the treatment of lysosomal and peroxisomal metabolic diseases. Springer Semin Immunopathol 2004; 26: 119-132.
    • (2004) Springer Semin Immunopathol , vol.26 , pp. 119-132
    • Krivit, W.1
  • 4
    • 0031901906 scopus 로고    scopus 로고
    • Hurler syndrome: Past, present, and future
    • Peters C, Shapiro EG, Krivit W. Hurler syndrome: Past, present, and future. J Pediatr 1998; 133: 7-9.
    • (1998) J Pediatr , vol.133 , pp. 7-9
    • Peters, C.1    Shapiro, E.G.2    Krivit, W.3
  • 6
    • 0032197968 scopus 로고    scopus 로고
    • The use of partially HLA-mismatched donors for allogeneic transplantation in patients with mucopolysaccharidosis-I
    • Fleming DR, Henslee-Downey PJ, Ciocci G, Romond EH Marciniak E, Munn RK et al. The use of partially HLA-mismatched donors for allogeneic transplantation in patients with mucopolysaccharidosis-I. Pediatr Transplant 1998; 2: 299-304.
    • (1998) Pediatr Transplant , vol.2 , pp. 299-304
    • Fleming, D.R.1    Henslee-Downey, P.J.2    Ciocci, G.3    Romond, E.H.4    Marciniak, E.5    Munn, R.K.6
  • 7
    • 9344245169 scopus 로고    scopus 로고
    • Outcome of unrelated donor bone marrow transplantation in 40 children with Hurler syndrome
    • Peters C, Balthazor M, Shapiro EG, King RJ, Kollman C, Hegland JD et al. Outcome of unrelated donor bone marrow transplantation in 40 children with Hurler syndrome. Blood 1996; 87: 4894-4902.
    • (1996) Blood , vol.87 , pp. 4894-4902
    • Peters, C.1    Balthazor, M.2    Shapiro, E.G.3    King, R.J.4    Kollman, C.5    Hegland, J.D.6
  • 8
    • 0032055564 scopus 로고    scopus 로고
    • Hurler syndrome: II. Outcome of HLA-genotypically identical sibling and HLA-haploidentical related donor bone marrow transplantation in fifty-four children. The Storage Disease Collaborative Study Group
    • Peters C, Shapiro EG, Anderson J, Henslee-Downey PJ, Klemperer MR, Cowan MJ et al. Hurler syndrome: II. Outcome of HLA-genotypically identical sibling and HLA-haploidentical related donor bone marrow transplantation in fifty-four children. The Storage Disease Collaborative Study Group. Blood 1998; 91: 2601-2608.
    • (1998) Blood , vol.91 , pp. 2601-2608
    • Peters, C.1    Shapiro, E.G.2    Anderson, J.3    Henslee-Downey, P.J.4    Klemperer, M.R.5    Cowan, M.J.6
  • 9
    • 23844497041 scopus 로고    scopus 로고
    • Gastrointestinal and hepatic complications
    • Blume KG, Forman SJ, Appelbaum FR eds, 3rd edn. Blackwell: Malden, MA, USA
    • Strasser SI, McDonald GB. Gastrointestinal and hepatic complications. In: Blume KG, Forman SJ, Appelbaum FR (eds). Thomas' Hematopoietic Cell Transplantation, 3rd edn. Blackwell: Malden, MA, USA, 2004, pp 769-810.
    • (2004) Thomas' Hematopoietic Cell Transplantation , pp. 769-810
    • Strasser, S.I.1    McDonald, G.B.2
  • 10
    • 13944259187 scopus 로고    scopus 로고
    • Graft-vs-host disease
    • Blume KG, Forman SJ, Appelbaum FR eds, 3rd edn. Blackwell: Malden, MA, USA
    • Sullivan KM. Graft-vs-host disease. In: Blume KG, Forman SJ, Appelbaum FR (eds). Thomas' Hematopoietic Cell Transplantation, 3rd edn. Blackwell: Malden, MA, USA, 2004, pp 635-664.
    • (2004) Thomas' Hematopoietic Cell Transplantation , pp. 635-664
    • Sullivan, K.M.1
  • 11
    • 0032198225 scopus 로고    scopus 로고
    • Neuropsychological development in children with Hurler syndrome following hematopoietic stem cell transplantation
    • Peters C, Shapiro EG, Krivit W. Neuropsychological development in children with Hurler syndrome following hematopoietic stem cell transplantation. Pediatr Transplant 1998; 2: 250-253.
    • (1998) Pediatr Transplant , vol.2 , pp. 250-253
    • Peters, C.1    Shapiro, E.G.2    Krivit, W.3
  • 13
    • 0028204908 scopus 로고
    • Evaluation of the neurobehavioral functioning of patients before, during, and after bone marrow transplantation
    • Meyers CA, Weitzner M, Byrne K, Valentine A, Champlin RE, Przepiorka D. Evaluation of the neurobehavioral functioning of patients before, during, and after bone marrow transplantation. J Clin Oncol 1994; 12: 820-826.
    • (1994) J Clin Oncol , vol.12 , pp. 820-826
    • Meyers, C.A.1    Weitzner, M.2    Byrne, K.3    Valentine, A.4    Champlin, R.E.5    Przepiorka, D.6
  • 15
    • 2342535103 scopus 로고    scopus 로고
    • Cord-blood transplants from unrelated donors in patients with Hurler's syndrome
    • Staba SL, Escolar ML, Poe M, Kim Y, Martin PL, Szabolcs P et al. Cord-blood transplants from unrelated donors in patients with Hurler's syndrome. N Engl J Med 2004; 350: 1960-1969.
    • (2004) N Engl J Med , vol.350 , pp. 1960-1969
    • Staba, S.L.1    Escolar, M.L.2    Poe, M.3    Kim, Y.4    Martin, P.L.5    Szabolcs, P.6
  • 16
    • 16244393128 scopus 로고    scopus 로고
    • Non-radiotherapy conditioning with stem cell transplantation from alternative donors in children with refractory severe aplastic anemia
    • Urban C, Benesch M, Sykora KW, Schwinger W, Lackner H. Non-radiotherapy conditioning with stem cell transplantation from alternative donors in children with refractory severe aplastic anemia. Bone Marrow Transplant 2005; 35: 591-594.
    • (2005) Bone Marrow Transplant , vol.35 , pp. 591-594
    • Urban, C.1    Benesch, M.2    Sykora, K.W.3    Schwinger, W.4    Lackner, H.5
  • 17
    • 32644433461 scopus 로고    scopus 로고
    • Results of alemtuzumab-based reduced-intensity allogeneic transplantation for chronic lymphocytic leukemia: A British Society of Blood and Marrow Transplantation Study
    • Delgado J, Thomson K, Russell N, Ewing J, Stewart W, Cook G et al. Results of alemtuzumab-based reduced-intensity allogeneic transplantation for chronic lymphocytic leukemia: A British Society of Blood and Marrow Transplantation Study. Blood 2006; 107: 1724-1730.
    • (2006) Blood , vol.107 , pp. 1724-1730
    • Delgado, J.1    Thomson, K.2    Russell, N.3    Ewing, J.4    Stewart, W.5    Cook, G.6
  • 19
    • 0031036079 scopus 로고    scopus 로고
    • Developmental outcome of unrelated donor bone marrow transplantation in children with Hurler syndrome
    • Phipps S, Mulhern R. Developmental outcome of unrelated donor bone marrow transplantation in children with Hurler syndrome. Blood 1997; 89: 732-734.
    • (1997) Blood , vol.89 , pp. 732-734
    • Phipps, S.1    Mulhern, R.2
  • 20
    • 3342935078 scopus 로고    scopus 로고
    • Cord-blood transplants from unrelated donors in Hurler's syndrome
    • author reply -7
    • Fujisaki G, Kami M, Kishi Y. Cord-blood transplants from unrelated donors in Hurler's syndrome. N Engl J Med 2004; 351: 506-507 author reply -7.
    • (2004) N Engl J Med , vol.351 , pp. 506-507
    • Fujisaki, G.1    Kami, M.2    Kishi, Y.3
  • 21
    • 10744223978 scopus 로고    scopus 로고
    • Outcome of 27 patients with Hurler's syndrome transplanted from either related or unrelated haematopoietic stem cell sources
    • Souillet G, Guffon N, Maire I, Pujol M, Taylor P, Sevin F et al. Outcome of 27 patients with Hurler's syndrome transplanted from either related or unrelated haematopoietic stem cell sources. Bone Marrow Transplant 2003; 31: 1105-1117.
    • (2003) Bone Marrow Transplant , vol.31 , pp. 1105-1117
    • Souillet, G.1    Guffon, N.2    Maire, I.3    Pujol, M.4    Taylor, P.5    Sevin, F.6
  • 22
    • 13944263629 scopus 로고    scopus 로고
    • Transplantation of allogeneic CD34-selected stem cells after fludarabine-based conditioning regimen for children with mucopolysaccharidosis 1H (M. Hurler)
    • Grigull L, Beilken A, Schrappe M, Das A, Luecke T, Sander A et al. Transplantation of allogeneic CD34-selected stem cells after fludarabine-based conditioning regimen for children with mucopolysaccharidosis 1H (M. Hurler). Bone Marrow Transplant 2005; 35: 265-269.
    • (2005) Bone Marrow Transplant , vol.35 , pp. 265-269
    • Grigull, L.1    Beilken, A.2    Schrappe, M.3    Das, A.4    Luecke, T.5    Sander, A.6
  • 23
    • 0036530011 scopus 로고    scopus 로고
    • Campath-1G causes rapid depletion of circulating host dendritic cells (DCs) before allogeneic transplantation but does not delay donor DC reconstitution
    • Klangsinsirikul P, Carter GI, Byrne JL, Hale G, Russell NH. Campath-1G causes rapid depletion of circulating host dendritic cells (DCs) before allogeneic transplantation but does not delay donor DC reconstitution. Blood 2002; 99: 2586-2591.
    • (2002) Blood , vol.99 , pp. 2586-2591
    • Klangsinsirikul, P.1    Carter, G.I.2    Byrne, J.L.3    Hale, G.4    Russell, N.H.5
  • 24
    • 0037945214 scopus 로고    scopus 로고
    • T-cell depleting antibodies: New hope for induction of allograft tolerance in bone marrow transplantation?
    • Simpson D. T-cell depleting antibodies: New hope for induction of allograft tolerance in bone marrow transplantation? BioDrugs 2003; 17: 147-154.
    • (2003) BioDrugs , vol.17 , pp. 147-154
    • Simpson, D.1
  • 26
    • 14644427874 scopus 로고    scopus 로고
    • Secondary graft failure associated with parainfluenza virus infection following hematopoietic cell transplantation
    • Grewal SS, van Burik JA, Peters C. Secondary graft failure associated with parainfluenza virus infection following hematopoietic cell transplantation. Bone Marrow Transplant 2005; 35: 425.
    • (2005) Bone Marrow Transplant , vol.35 , pp. 425
    • Grewal, S.S.1    van Burik, J.A.2    Peters, C.3
  • 27
    • 0041869127 scopus 로고    scopus 로고
    • Life-threatening pulmonary hemorrhages post bone marrow transplantation in Hurler syndrome. Report of three cases and review of the literature
    • Gassas A, Sung L, Doyle JJ, Clarke JT, Saunders EF. Life-threatening pulmonary hemorrhages post bone marrow transplantation in Hurler syndrome. Report of three cases and review of the literature. Bone Marrow Transplant 2003; 32: 213-215.
    • (2003) Bone Marrow Transplant , vol.32 , pp. 213-215
    • Gassas, A.1    Sung, L.2    Doyle, J.J.3    Clarke, J.T.4    Saunders, E.F.5
  • 28
    • 33644930349 scopus 로고    scopus 로고
    • Inflammatory cytokines and the development of pulmonary complications after allogeneic hematopoietic cell transplantation in patients with inherited metabolic storage disorders
    • Kharbanda S, Panoskaltsis-Mortari A, Haddad IY, Blazar BR, Orchard PJ, Cornfield DN et al. Inflammatory cytokines and the development of pulmonary complications after allogeneic hematopoietic cell transplantation in patients with inherited metabolic storage disorders. Biol Blood Marrow Transplant 2006; 12: 430-437.
    • (2006) Biol Blood Marrow Transplant , vol.12 , pp. 430-437
    • Kharbanda, S.1    Panoskaltsis-Mortari, A.2    Haddad, I.Y.3    Blazar, B.R.4    Orchard, P.J.5    Cornfield, D.N.6
  • 29
    • 0033822637 scopus 로고    scopus 로고
    • Upper airway complications in children after bone marrow transplantation
    • Drew B, Peters C, Rimell F. Upper airway complications in children after bone marrow transplantation. Laryngoscope 2000; 110: 1446-1451.
    • (2000) Laryngoscope , vol.110 , pp. 1446-1451
    • Drew, B.1    Peters, C.2    Rimell, F.3
  • 31
    • 0036838640 scopus 로고    scopus 로고
    • Nonmyeloablative transplantation with or without alemtuzumab: Comparison between 2 prospective studies in patients with lymphoproliferative disorders
    • Perez-Simon JA, Kottaridis PD, Martino R, Craddock C, Caballero D, Chopra R et al. Nonmyeloablative transplantation with or without alemtuzumab: Comparison between 2 prospective studies in patients with lymphoproliferative disorders. Blood 2002; 100: 3121-3127.
    • (2002) Blood , vol.100 , pp. 3121-3127
    • Perez-Simon, J.A.1    Kottaridis, P.D.2    Martino, R.3    Craddock, C.4    Caballero, D.5    Chopra, R.6
  • 32
    • 0032535279 scopus 로고    scopus 로고
    • Improving the outcome of bone marrow transplantation by using CD52 monoclonal antibodies to prevent graft-versus-host disease and graft rejection
    • Hale G, Zhang MJ, Bunjes D, Prentice HG, Spence D, Horowitz MM et al Improving the outcome of bone marrow transplantation by using CD52 monoclonal antibodies to prevent graft-versus-host disease and graft rejection. Blood 1998; 92: 4581-4590.
    • (1998) Blood , vol.92 , pp. 4581-4590
    • Hale, G.1    Zhang, M.J.2    Bunjes, D.3    Prentice, H.G.4    Spence, D.5    Horowitz, M.M.6
  • 33
    • 20944443759 scopus 로고    scopus 로고
    • Safety and efficacy of enzyme replacement therapy in combination with hematopoietic stem cell transplantation in Hurler syndrome
    • Grewal SS, Wynn R, Abdenur JE, Burton BK, Gharib M, Haase C et al. Safety and efficacy of enzyme replacement therapy in combination with hematopoietic stem cell transplantation in Hurler syndrome. Genet Med 2005; 7: 143-146.
    • (2005) Genet Med , vol.7 , pp. 143-146
    • Grewal, S.S.1    Wynn, R.2    Abdenur, J.E.3    Burton, B.K.4    Gharib, M.5    Haase, C.6


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