Bone marrow transplantation in metachromatic leukodystrophy caused by saposin-B deficiency: A case report with a 3-year follow-up period

Journal of Pediatrics

Volumn 133, Issue 1, 1998, Pages 129-132

  Landrieu, P ^a   Blanche, S ^a   Vanier, M T ^a   Metral, S ^a   Husson, B ^a   Sandhoff, K ^a   Fischer, A ^a  

^a BICÊTRE HOSPITAL   (France)

Author keywords

[No Author keywords available]

Indexed keywords

SAPONIN;

ARTICLE; BLOOD BRAIN BARRIER; BONE MARROW TRANSPLANTATION; BRAIN ATROPHY; CASE REPORT; ELECTROMYOGRAM; HUMAN; MALE; METACHROMATIC LEUKODYSTROPHY; NERVE CONDUCTION; NUCLEAR MAGNETIC RESONANCE IMAGING; PERIPHERAL NERVOUS SYSTEM; PHENOTYPE; PRESCHOOL CHILD; PRIORITY JOURNAL; WHITE MATTER;

EID: 0031903085     PISSN: 00223476     EISSN: None     Source Type: Journal    
DOI: 10.1016/S0022-3476(98)70191-X     Document Type: Article

References (12)

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