Bone marrow transplantation for Maroteaux-Lamy syndrome (MPS VI): Long-term follow-up

Journal of Inherited Metabolic Disease

Volumn 22, Issue 1, 1999, Pages 50-62

  Herskhovitz, E ^a   Young, E ^a   Rainer, J ^a   Hall, C M ^a   Lidchi, V ^a   Chong, K ^a   Vellodi, A ^a  

^a GREAT ORMOND STREET HOSPITAL   (United Kingdom)

Author keywords

[No Author keywords available]

Indexed keywords

ARTICLE; BODY POSTURE; BONE MARROW TRANSPLANTATION; CARDIOMYOPATHY; CASE REPORT; CHILD; FACIES; FEMALE; FOLLOW UP; HEART DISEASE; HUMAN; JOINT MOBILITY; MALE; MAROTEAUX LAMY SYNDROME; PATIENT SELECTION; PHYSICAL ACTIVITY; QUALITY OF LIFE; SCHOOL; SKELETON MALFORMATION; SLEEP APNEA SYNDROME; SURVIVAL;

BONE MARROW TRANSPLANTATION; CHILD, PRESCHOOL; CREATININE; FEMALE; FOLLOW-UP STUDIES; GLYCOSAMINOGLYCANS; HEART; HUMANS; MAGNETIC RESONANCE IMAGING; MALE; MUCOPOLYSACCHARIDOSIS VI; MUSCULOSKELETAL SYSTEM; N-ACETYLGALACTOSAMINE-4-SULFATASE; PSYCHOLOGICAL TESTS; TIME FACTORS;

EID: 0032988760     PISSN: 01418955     EISSN: None     Source Type: Journal    
DOI: 10.1023/A:1005447232027     Document Type: Article

References (19)

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