Long-term metabolic, endocrine, and neuropsychological outcome of hematopoietic cell transplantation for Wolman disease

Bone Marrow Transplantation

Volumn 43, Issue 1, 2009, Pages 21-27

  Tolar, J ^a   Petryk, A ^b   Khan, K ^a   Bjoraker, K J ^a   Jessurun, J ^a   Dolan, M ^a   Kivisto, T ^a   Charnas, L ^a   Shapiro, E G ^a   Orchard, P J ^a  

^a UNIVERSITY OF MINNESOTA MEDICAL SCHOOL   (United States)

^b UNIVERSITY OF MINNESOTA   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

BUSULFAN; CORTICOTROPIN; CYCLOPHOSPHAMIDE; FLUDROCORTISONE; HYDROCORTISONE; PREDNISONE; THYMOCYTE ANTIBODY;

ACUTE GRAFT VERSUS HOST DISEASE; ADRENAL DISEASE; AGE DISTRIBUTION; ARTICLE; CASE REPORT; CHILD; CLINICAL FEATURE; COMPUTER ASSISTED TOMOGRAPHY; CONTROLLED STUDY; DEATH; DIARRHEA; DIFFERENTIAL DIAGNOSIS; DISEASE SEVERITY; EARLY DIAGNOSIS; FEMALE; GRAFT VERSUS HOST REACTION; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HEMOLYTIC ANEMIA; HEPATOSPLENOMEGALY; HISTOPATHOLOGY; HLA MATCHING; HUMAN; HUMAN TISSUE; IMAGE ANALYSIS; INFANT; LIVER DYSFUNCTION; MALE; NEWBORN; OUTCOME ASSESSMENT; PRIORITY JOURNAL; SURVIVAL TIME; TREATMENT DURATION; TREATMENT RESPONSE; WHOLE BODY RADIATION; WOLMAN DISEASE;

ENDOCRINE SYSTEM; FEMALE; GASTROINTESTINAL TRACT; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HEMATOPOIETIC SYSTEM; HUMANS; INFANT; INFANT, NEWBORN; LIVER; MALE; SURVIVORS; WOLMAN DISEASE;

EID: 58549097839     PISSN: 02683369     EISSN: 14765365     Source Type: Journal    
DOI: 10.1038/bmt.2008.273     Document Type: Article

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