β-hexosaminidase lentiviral vectors: Transfer into the CNS via systemic administration

Molecular Brain Research

Volumn 133, Issue 2, 2005, Pages 286-298

  Kyrkanides, Stephanos ^a,b   Miller, Jennie H ^a   Brouxhon, Sabine M ^a   Olschowka, John A ^a   Federoff, Howard J ^a  

^a UNIVERSITY OF ROCHESTER SCHOOL OF MEDICINE AND DENTISTRY   (United States)

^b UNIVERSITY OF ROCHESTER   (United States)

Author keywords

Feline immunodeficiency virus; Gene therapy; GM2 gangliosidosis; Lysosomal storage; hexosaminidase

Indexed keywords

BETA N ACETYLHEXOSAMINIDASE; LENTIVIRUS VECTOR;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; ENCEPHALITIS; FIBROBLAST; LENTIVIRINAE; LYSOSOME; MOUSE; NEUROMUSCULAR DISEASE; NONHUMAN; PRIORITY JOURNAL; PROTEIN EXPRESSION; SANDHOFF DISEASE; TAY SACHS DISEASE;

EID: 13844250361     PISSN: 0169328X     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.molbrainres.2004.10.026     Document Type: Article

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