Restoration of hexosaminidase A activity in human Tay-Sachs fibroblasts via adenoviral vector-mediated gene transfer

Gene Therapy

Volumn 3, Issue 9, 1996, Pages 769-774

  Akli, S ^a,b,e   Guidotti, J E ^b   Vigne, E ^c   Perricaudet, M ^c   Sandhoff, K ^d   Kahn, A ^b   Poenaru, L ^a,b  

^a UNIVERSITÉ PARIS DESCARTES   (France)

^b INSTITUT COCHIN   (France)

^c INSTITUT GUSTAVE ROUSSY   (France)

^d UNIVERSITY OF BONN   (Germany)

^e BAYLOR COLLEGE OF MEDICINE   (United States)

Author keywords

Defective recombinant adenovirus; Hexosaminidases; Tay Sachs disease

Indexed keywords

BETA N ACETYLHEXOSAMINIDASE A; GANGLIOSIDE GM2;

ADENOVIRUS; ARTICLE; CASE REPORT; CONTROLLED STUDY; ENZYME ACTIVITY; ENZYME DEFICIENCY; ENZYME SUBSTRATE; EXPRESSION VECTOR; FIBROBLAST; GENE MUTATION; GENE THERAPY; GENE TRANSFER; HUMAN; HUMAN CELL; LYSOSOME STORAGE DISEASE; MOLECULAR CLONING; NONHUMAN; PRIORITY JOURNAL; TAY SACHS DISEASE;

ADENOVIRIDAE; BETA-N-ACETYLHEXOSAMINIDASE; DNA, COMPLEMENTARY; FIBROBLASTS; G(M2) GANGLIOSIDE; GENE EXPRESSION; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; HUMANS; LYSOSOMES; RNA, MESSENGER; TAY-SACHS DISEASE;

ADENOVIRIDAE;

EID: 0029794652     PISSN: 09697128     EISSN: None     Source Type: Journal    
DOI: None     Document Type: Article

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