Restoration of dystrophin expression in mdx muscle cells by chimeraplast-mediated exon skipping

Human Molecular Genetics

Volumn 12, Issue 10, 2003, Pages 1087-1099

  Bertoni, Carmen ^a   Lau, Catherine ^a   Rando, Thomas A ^a,b  

^a STANFORD UNIVERSITY SCHOOL OF MEDICINE   (United States)

^b VA PALO ALTO HEALTH CARE SYSTEM   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

CHIMERIC PROTEIN; DNA; DYSTROGLYCAN; DYSTROPHIN; GENE PRODUCT; OLIGONUCLEOTIDE; RNA;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CELL DIFFERENTIATION; CHIMERAPLASTY; CONTROLLED STUDY; DISEASE SEVERITY; DNA SPLICING; DUCHENNE MUSCULAR DYSTROPHY; EXON; GENE DELETION; GENE FUNCTION; GENE TARGETING; GENETIC TRANSCRIPTION; GENETIC TRANSFORMATION; INTRON; MOUSE; MUSCLE CELL; NEWBORN; NONHUMAN; NUCLEIC ACID BASE SUBSTITUTION; NUCLEOTIDE SEQUENCE; PHENOTYPE; PRIORITY JOURNAL; PROTEIN EXPRESSION; PROTEIN LOCALIZATION; SITE DIRECTED MUTAGENESIS; WESTERN BLOTTING;

ALTERNATIVE SPLICING; ANIMALS; BASE SEQUENCE; CYTOSKELETAL PROTEINS; DYSTROGLYCANS; DYSTROPHIN; EXONS; GENE EXPRESSION REGULATION; MEMBRANE GLYCOPROTEINS; MICE; MICE, INBRED MDX; MOLECULAR SEQUENCE DATA; MUSCLE CELLS; MUSCULAR DYSTROPHY, DUCHENNE; OLIGODEOXYRIBONUCLEOTIDES; OLIGORIBONUCLEOTIDES; POINT MUTATION;

ANIMALIA;

EID: 0038440559     PISSN: 09646906     EISSN: None     Source Type: Journal    
DOI: 10.1093/hmg/ddg133     Document Type: Article

References (37)

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