Dystrophin gene repair in mdx muscle precursor cells in vitro and in vivo mediated by RNA-DNA chimeric oligonucleotides

Human Gene Therapy

Volumn 13, Issue 6, 2002, Pages 707-718

  Bertoni, Carmen ^a   Rando, Thomas A ^a  

^a STANFORD UNIVERSITY MEDICAL CENTER   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

CHIMERIC PROTEIN; DYSTROPHIN; OLIGONUCLEOTIDE; RECOMBINANT DNA; RECOMBINANT RNA;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; EXON; GENE CONVERSION; GENE TARGETING; GENE THERAPY; GENETIC TRANSFECTION; IMMUNOBLOTTING; MOUSE; MUSCLE CELL; MUSCLE FIBRIL; MUSCULAR DYSTROPHY; MYOBLAST; NONHUMAN; POINT MUTATION; PROTEIN EXPRESSION; STEM CELL; TISSUE REPAIR;

ANIMALS; BASE SEQUENCE; DNA, COMPLEMENTARY; DYSTROPHIN; MICE; MICE, INBRED C57BL; MICE, INBRED MDX; MOLECULAR SEQUENCE DATA; MUSCLES; MUSCULAR DYSTROPHIES; STEM CELLS;

ANIMALIA;

EID: 0036211418     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/104303402317322276     Document Type: Article

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