Antisense-induced exon skipping restores dystrophin expression in DMD patient derived muscle cells

Human Molecular Genetics

Volumn 10, Issue 15, 2001, Pages 1547-1554

  Van Deutekom, Judith C T ^a   Bremmer Bout, Mattie ^a   Janson, Anneke A M ^a   Ginjaar, Ieke B ^a   Baas, Frank ^b   Den Dunnen, Johan T ^a   Van Ommen, Gert Jan B ^a  

^a LEIDEN UNIVERSITY MEDICAL CENTER   (Netherlands)

^b ACADEMIC MEDICAL CENTER   (Netherlands)

Author keywords

[No Author keywords available]

Indexed keywords

ANTISENSE OLIGONUCLEOTIDE; DYSTROPHIN; MESSENGER RNA; NUCLEOTIDE; RNA;

ALLELE; ANIMAL CELL; ARTICLE; BECKER MUSCULAR DYSTROPHY; CELL CULTURE; CONTROLLED STUDY; DISEASE SEVERITY; DUCHENNE MUSCULAR DYSTROPHY; EXON; FRAMESHIFT MUTATION; GENE DELETION; GENE MUTATION; GENE THERAPY; GENETIC DISORDER; HUMAN; HUMAN CELL; LETHALITY; MOUSE; MUSCLE ATROPHY; MUSCLE CELL; MYOTUBE; NONHUMAN; NUCLEOTIDE SEQUENCE; PHENOTYPE; PRIORITY JOURNAL; PROTEIN EXPRESSION; PROTEIN LOCALIZATION; PROTEIN TARGETING; RNA SPLICING; RNA TRANSLATION;

ANIMALIA;

EID: 0035878539     PISSN: 09646906     EISSN: None     Source Type: Journal    
DOI: 10.1093/hmg/10.15.1547     Document Type: Article

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