Ribozyme gene therapy: Applications for molecular medicine

Trends in Molecular Medicine

Volumn 7, Issue 5, 2001, Pages 221-228

  Lewin, Alfred S ^a   Hauswirth, William W ^b  

^a UNIVERSITY OF FLORIDA   (United States)

^b UNIVERSITY OF FLORIDA COLLEGE OF MEDICINE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

RIBONUCLEASE P; RIBOZYME;

ALLELE; CANCER; DOWN REGULATION; GENE THERAPY; GENETIC VARIABILITY; IN VITRO STUDY; INTRON; METABOLIC DISORDER; REVIEW; VIRUS INFECTION;

ACQUIRED IMMUNODEFICIENCY SYNDROME; ALLELES; ANIMALS; BASE SEQUENCE; CODON; DEPENDOVIRUS; DNA REPAIR; DOWN-REGULATION; GENE THERAPY; HUMANS; INTRONS; MODELS, BIOLOGICAL; MOLECULAR SEQUENCE DATA; NEOPLASMS; RNA, CATALYTIC; TRANSDUCTION, GENETIC;

HARNESS;

EID: 0034839007     PISSN: 14714914     EISSN: None     Source Type: Journal    
DOI: 10.1016/S1471-4914(01)01965-7     Document Type: Review

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4. A general 2-metal-ion mechanism for catalytic RNA
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14. Recent advances in inducible gene expression systems
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16. mRNA localization signals can enhance the intracellular effectiveness of hammerhead ribozymes
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34. Aggregation and motor neuron toxicity of an ALS-linked SOD1 mutant independent from wild-type SOD1
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