Repair of CFTR mRNA by spliceosome-mediated RNA trans-splicing

Gene Therapy

Volumn 7, Issue 22, 2000, Pages 1885-1895

  Mansfield, S G ^a   Kole, J ^b   Puttaraju, M ^a   Yang, C C ^a   Garcia Blanco, M A ^a,b   Cohn, J A ^b   Mitchell, L G ^a  

^a Intronn LLC   (United States)

^b DUKE UNIVERSITY SCHOOL OF MEDICINE   (United States)

Author keywords

CFTR protein; Gene repair; Gene therapy; Sequence deletion; Therapeutics; Trans splicing

Indexed keywords

COMPLEMENTARY DNA; CYCLIC AMP DEPENDENT PROTEIN KINASE; DNA; MESSENGER RNA; PHOSPHOPEPTIDE; TRANSMEMBRANE CONDUCTANCE REGULATOR;

ARTICLE; CELL LYSATE; CONTROLLED STUDY; CYSTIC FIBROSIS; DNA REPAIR; EXON; GENE CONSTRUCT; GENE EXPRESSION; GENE MUTATION; GENE SEQUENCE; GENE TARGETING; GENE THERAPY; GENETIC CODE; GENETIC TRANSFECTION; HUMAN; HUMAN CELL; IMMUNOPRECIPITATION; INTRON; PEPTIDE MAPPING; PRIORITY JOURNAL; PROTEIN BINDING; PROTEIN PHOSPHORYLATION; PROTEIN SYNTHESIS; RNA SPLICING; SPLICEOSOME; WESTERN BLOTTING;

EID: 0033674357     PISSN: 09697128     EISSN: None     Source Type: Journal    
DOI: 10.1038/sj.gt.3301307     Document Type: Article

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