A novel SV40-based vector successfully transduces and expresses an alpha 1-antitrypsin ribozyme in a human hepatoma-derived cell line

Gene Therapy

Volumn 6, Issue 1, 1999, Pages 114-120

  Zern, M A ^a   Ozaki, I ^a,b   Duan, L ^a   Pomerantz, R ^a   Liu, S L ^a   Strayer, D S ^a  

^a THOMAS JEFFERSON UNIVERSITY   (United States)

^b SAGA UNIVERSITY   (Japan)

Author keywords

1 antitrypsin deficiency; Gene therapy; Ribozymes; SV40

Indexed keywords

ALPHA 1 ANTITRYPSIN; COMPLEMENTARY DNA; MESSENGER RNA; MUTANT PROTEIN; PLASMID VECTOR; RIBOZYME;

ALPHA 1 ANTITRYPSIN DEFICIENCY; ARTICLE; DNA SYNTHESIS INHIBITION; GENE EXPRESSION; GENE MUTATION; GENE THERAPY; GENETIC TRANSDUCTION; HEPATOMA CELL; HUMAN; HUMAN CELL; PRIORITY JOURNAL; PROTEIN SYNTHESIS; RNA CLEAVAGE; SIMIAN VIRUS 40;

ALPHA 1-ANTITRYPSIN; ALPHA 1-ANTITRYPSIN DEFICIENCY; BLOTTING, NORTHERN; CARCINOMA, HEPATOCELLULAR; DNA, COMPLEMENTARY; GENE EXPRESSION REGULATION; GENE THERAPY; GENETIC VECTORS; HUMANS; MUTATION; PHENOTYPE; RNA, CATALYTIC; SIMIAN VIRUS 40; TUMOR CELLS, CULTURED;

DNA VIRUSES; SIMIAE; SIMIAN VIRUS; SIMIAN VIRUS 40;

EID: 0032922168     PISSN: 09697128     EISSN: None     Source Type: Journal    
DOI: 10.1038/sj.gt.3300793     Document Type: Article

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