CRISPR/Cas9-Mediated Genome Editing Corrects Dystrophin Mutation in Skeletal Muscle Stem Cells in a Mouse Model of Muscle Dystrophy

Molecular Therapy Nucleic Acids

Volumn 7, Issue , 2017, Pages 31-41

  Zhu, Pei ^a   Wu, Furen ^a   Mosenson, Jeffrey ^a   Zhang, Hongmei ^b   He, Tong Chuan ^b   Wu, Wen Shu ^a  

^a UNIVERSITY OF ILLINOIS AT CHICAGO   (United States)

^b NY   (United States)

Author keywords

3D fibrin gel; CRISPR Cas9; DMD; Duchenne muscular dystrophy; ex vivo expansion; genome editing; muscle stem cells

Indexed keywords

DYSTROPHIN;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; CRISPR CAS SYSTEM; DUCHENNE MUSCULAR DYSTROPHY; DYSTROPHIN GENE; FEASIBILITY STUDY; GENE; GENE EDITING; GENE EXPRESSION; GENE MUTATION; IMMUNOHISTOCHEMISTRY; MOUSE; MUSCLE STEM CELL; MUSCULAR DYSTROPHY; NONHUMAN; PRIORITY JOURNAL; RELIABILITY; SKELETAL MUSCLE STEM CELL; STEM CELL EXPANSION;

EID: 85020720585     PISSN: None     EISSN: 21622531     Source Type: Journal    
DOI: 10.1016/j.omtn.2017.02.007     Document Type: Article

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