Dystrophin expression in myofibers of Duchenne muscular dystrophy patients following intramuscular injections of normal myogenic cells

Molecular Therapy

Volumn 9, Issue 3, 2004, Pages 475-482

  Skuk, Daniel ^a   Roy, Brigitte ^a   Goulet, Marlyne ^a   Chapdelaine, Pierre ^a   Bouchard, Jean Pierre ^a   Roy, Raynald ^a   Dugré, Francine J ^a   Lachance, Jean Guy ^a   Deschênes, Louise ^a   Senay, Hélène ^a   Sylvain, Michel ^a   Tremblay, Jacques P ^a  

^a LAVAL UNIVERSITY   (Canada)

Author keywords

Cell transplantation; Duchenne muscular dystrophy; Dystrophin; Myogenic cell; Skeletal muscle; Tacrolimus

Indexed keywords

DEFLAZACORT; DYSTROPHIN; EPITOPE; MONOCLONAL ANTIBODY; PRIMER DNA; SODIUM CHLORIDE; TACROLIMUS;

ADOLESCENT; ARTICLE; CELL COUNT; CELL TRANSPLANTATION; CLINICAL ARTICLE; CONTROLLED STUDY; DONOR; DRUG BLOOD LEVEL; DUCHENNE MUSCULAR DYSTROPHY; EXON; GENE DELETION; GENE DUPLICATION; GENE SEQUENCE; GENETIC CODE; GENETIC TRANSCRIPTION; HUMAN; HUMAN CELL; HUMAN TISSUE; IMMUNOSUPPRESSIVE TREATMENT; MUSCLE BIOPSY; MUSCLE CELL; PROTEIN EXPRESSION; REVERSE TRANSCRIPTION POLYMERASE CHAIN REACTION; SCHOOL CHILD; TIBIALIS ANTERIOR MUSCLE;

EID: 12144289797     PISSN: 15250016     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.ymthe.2003.11.023     Document Type: Review

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