In Vivo Delivery of CRISPR/Cas9 for Therapeutic Gene Editing: Progress and Challenges

Bioconjugate Chemistry

Volumn 28, Issue 4, 2017, Pages 880-884

  Mout, Rubul ^a   Ray, Moumita ^a   Lee, Yi Wei ^a   Scaletti, Federica ^a   Rotello, Vincent M ^a  

^a UNIVERSITY OF MASSACHUSETTS   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

IN-VIVO; PALINDROMIC; THERAPEUTIC GENES; VIVO DELIVERIES;

CLUSTERED REGULARLY INTERSPACED SHORT PALINDROMIC REPEAT; GENE EDITING; TOPICAL DRUG ADMINISTRATION; ADMINISTRATION AND DOSAGE; ANIMAL; CRISPR CAS SYSTEM; GENE EXPRESSION REGULATION; GENE THERAPY; GENE TRANSFER; GENE VECTOR; GENETICS; HUMAN; PROCEDURES; VIRUS;

ANIMALS; CLUSTERED REGULARLY INTERSPACED SHORT PALINDROMIC REPEATS; CRISPR-CAS SYSTEMS; GENE EDITING; GENE TRANSFER TECHNIQUES; GENETIC THERAPY; GENETIC VECTORS; HUMANS; MUTAGENESIS, INSERTIONAL; VIRUSES;

EID: 85018468678     PISSN: 10431802     EISSN: 15204812     Source Type: Journal    
DOI: 10.1021/acs.bioconjchem.7b00057     Document Type: Review

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