mRNA trans-splicing in gene therapy for genetic diseases

Wiley Interdisciplinary Reviews: RNA

Volumn 7, Issue 4, 2016, Pages 487-498

  Berger, Adeline ^a   Maire, Séverine ^b,c   Gaillard, Marie Claude ^b,c   Sahel, José Alain ^a,d,e,f   Hantraye, Philippe ^b,c   Bemelmans, Alexis Pierre ^b,c  

^a SORBONNE UNIVERSITÉ   (France)

^b INSTITUT DE RADIOPROTECTION ET DE SÛRETÉ NUCLÉAIRE   (France)

^c CNRS   (France)

^d CENTRE HOSPITALIER NATIONAL D OPHTALMOLOGIE DES QUINZE VINGTS   (France)

^e FONDATION OPHTALMOLOGIQUE ADOLPHE DE ROTHSCHILD   (France)

^f UNIVERSITY COLLEGE LONDON   (United Kingdom)

Author keywords

[No Author keywords available]

Indexed keywords

COMPLEMENTARY DNA; PRE MESSENGER RNA TRANS SPLICING MOLECULE; RNA; SHORT HAIRPIN RNA; UNCLASSIFIED DRUG;

BINDING AFFINITY; BINDING SITE; CLINICAL EFFECTIVENESS; CLUSTERED REGULARLY INTERSPACED SHORT PALINDROMIC REPEAT; DNA FRAGMENTATION; DNA MODIFICATION; DRUG DESIGN; EXON REPETITION; GENE EXPRESSION REGULATION; GENE SILENCING; GENE TARGETING; GENE THERAPY; GENETIC ASSOCIATION; GENETIC DISORDER; GENETIC ENGINEERING; HUMAN; INTRON; MESSENGER RNA TRANS SPLICING; MOLECULAR DYNAMICS; MOLECULAR GENETICS; NONHUMAN; OPEN READING FRAME; PRIORITY JOURNAL; PROTEIN SYNTHESIS; REVIEW; RNA INTERFERENCE; SPLICEOSOME; SPLICEOSOME MEDIATED RNA TRANS SPLICING; TRANS SPLICING;

EID: 84974654809     PISSN: 17577004     EISSN: 17577012     Source Type: Journal    
DOI: 10.1002/wrna.1347     Document Type: Review

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