Dystrophin rescue by trans-splicing: A strategy for DMD genotypes not eligible for exon skipping approaches

Nucleic Acids Research

Volumn 41, Issue 17, 2013, Pages 8391-8402

  Lorain, Stéphanie ^a   Peccate, Cécile ^a   Le Hir, Maëva ^a,b   Griffith, Graziella ^a,b   Philippi, Susanne ^a,b   Précigout, Guillaume ^a,b   Mamchaoui, Kamel ^a   Jollet, Arnaud ^a   Voit, Thomas ^a   Garcia, Luis ^a,b  

^a SORBONNE UNIVERSITÉ   (France)

^b LABORATOIRE DES SCIENCES DU CLIMAT ET DE L ENVIRONNEMENT   (France)

Author keywords

[No Author keywords available]

Indexed keywords

DYSTROPHIN; MESSENGER RNA; PARVOVIRUS VECTOR;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; DUCHENNE MUSCULAR DYSTROPHY; DYSTROPHIN GENE; EMBRYO; EXON; EXON SKIPPING; GENE EXPRESSION REGULATION; GENETIC ANALYSIS; GENETIC CODE; GENETIC STABILITY; GENETIC TRANSFECTION; GENOTYPE; HUMAN; HUMAN CELL; HUMAN TISSUE; IN VITRO STUDY; INTRON; MOUSE; MYOTUBE; NONHUMAN; NONSENSE MUTATION; PRIORITY JOURNAL; REPORTER GENE; STOP CODON; TRANS SPLICING;

ANIMALS; DEPENDOVIRUS; DYSTROPHIN; EXONS; GENETIC VECTORS; GENOTYPE; HUMANS; INTRONS; MICE; MICE, INBRED MDX; MUSCLE FIBERS, SKELETAL; MUSCLES; MUSCULAR DYSTROPHY, DUCHENNE; NIH 3T3 CELLS; RNA SPLICE SITES; RNA, MESSENGER; TRANS-SPLICING;

EID: 84884913905     PISSN: 03051048     EISSN: 13624962     Source Type: Journal    
DOI: 10.1093/nar/gkt621     Document Type: Article

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