Cis-splicing and translation of the pre-trans-splicing molecule combine with efficiency in spliceosome-mediated RNA trans-splicing

Molecular Therapy

Volumn 22, Issue 6, 2014, Pages 1176-1187

  Monjaret, François ^a   Bourg, Nathalie ^a   Suel, Laurence ^a   Roudaut, Carinne ^a   Le Roy, Florence ^a   Richard, Isabelle ^a   Charton, Karine ^a  

^a GÉNÉTHON   (France)

Author keywords

[No Author keywords available]

Indexed keywords

COMPLEMENTARY DNA; CONNECTIN; DYSFERLIN; RNA; VIRUS VECTOR; DYSF PROTEIN, MOUSE; MEMBRANE PROTEIN; MESSENGER RNA; PROTEIN KINASE; RNA PRECURSOR; TITIN PROTEIN, MOUSE;

3' UNTRANSLATED REGION; ANIMAL CELL; ARTICLE; CONTROLLED STUDY; DYSF GENE; DYSFERLINOPATHY; GENE; GENE EXPRESSION; GENE MUTATION; HUMAN; HUMAN CELL; IN VITRO STUDY; IN VIVO STUDY; MALE; MOLECULAR CLONING; MOUSE; MUSCULAR DYSTROPHY; NONHUMAN; OPEN READING FRAME; RNA TRANSLATION; SPLICEOSOME; TITINOPATHY; TRANS SPLICING; TTN GENE; ALTERNATIVE RNA SPLICING; ANIMAL; C57BL MOUSE; CELL LINE; GENETICS; METABOLISM; MOLECULARLY TARGETED THERAPY; MUSCULAR DYSTROPHIES;

ADENO-ASSOCIATED VIRUS;

ALTERNATIVE SPLICING; ANIMALS; CELL LINE; HUMANS; MEMBRANE PROTEINS; MICE; MICE, INBRED C57BL; MOLECULAR TARGETED THERAPY; MUSCULAR DYSTROPHIES; OPEN READING FRAMES; PROTEIN KINASES; RNA PRECURSORS; RNA, MESSENGER; TRANS-SPLICING;

EID: 84902160875     PISSN: 15250016     EISSN: 15250024     Source Type: Journal    
DOI: 10.1038/mt.2014.35     Document Type: Article

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