Exon exchange approach to repair duchenne dystrophin transcripts

PLoS ONE

Volumn 5, Issue 5, 2010, Pages

  Lorain, Stéphanie ^a   Peccate, Cécile ^a   le Hir, Maëva ^a   Garcia, Luis ^a  

^a SORBONNE UNIVERSITÉ   (France)

Author keywords

[No Author keywords available]

Indexed keywords

DYSTROPHIN; MESSENGER RNA;

ANIMAL CELL; ARTICLE; CONTROLLED STUDY; DUCHENNE MUSCULAR DYSTROPHY; EMBRYO; ENHANCER REGION; EXON; FEASIBILITY STUDY; FIBROBLAST; GENE CONSTRUCT; GENE DELETION; GENE MUTATION; GENETIC CODE; GENETIC TRANSCRIPTION; INTRON; MOUSE; NONHUMAN; PROTEIN MOTIF; RNA SPLICING; RNA STABILITY; RNA TRANSLATION; TARGETED GENE REPAIR; TRANSLATION REGULATION; UNTRANSLATED REGION;

ANIMALS; BASE SEQUENCE; DNA MUTATIONAL ANALYSIS; DYSTROPHIN; ENHANCER ELEMENTS, GENETIC; EXONS; INTRONS; MICE; MOLECULAR SEQUENCE DATA; MUSCULAR DYSTROPHY, ANIMAL; NIH 3T3 CELLS; RNA, MESSENGER; TRANS-SPLICING;

EID: 77956509696     PISSN: None     EISSN: 19326203     Source Type: Journal    
DOI: 10.1371/journal.pone.0010894     Document Type: Article

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