Trans-splicing-mediated improvement in a severe mouse model of spinal muscular atrophy

Journal of Neuroscience

Volumn 30, Issue 1, 2010, Pages 126-130

  Coady, Tristan H ^a   Lorson, Christian L ^a  

^a UNIVERSITY OF MISSOURI   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

MESSENGER RNA; RIBONUCLEOPROTEIN; SURVIVAL MOTOR NEURON PROTEIN 2;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; BRAIN VENTRICLE; CONTROLLED STUDY; DISEASE SEVERITY; GENE VECTOR; GENETIC DISORDER; IN VIVO STUDY; INJECTION; MOUSE; NEWBORN; NONHUMAN; PHENOTYPE; PRIORITY JOURNAL; PROTEIN ASSEMBLY; SPINAL MUSCULAR ATROPHY; SURVIVAL; TRANS SPLICING;

ANIMALS; ANIMALS, NEWBORN; DISEASE MODELS, ANIMAL; GENE THERAPY; GENE TRANSFER TECHNIQUES; INJECTIONS, INTRAVENTRICULAR; MICE; MICE, KNOCKOUT; MUSCULAR ATROPHY, SPINAL; SEVERITY OF ILLNESS INDEX; SURVIVAL OF MOTOR NEURON 1 PROTEIN; SURVIVAL OF MOTOR NEURON 2 PROTEIN; TRANS-SPLICING;

EID: 74849129866     PISSN: 02706474     EISSN: 15292401     Source Type: Journal    
DOI: 10.1523/JNEUROSCI.4489-09.2010     Document Type: Article

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