Considerations for a successful RNA Trans-splicing repair of genetic disorders

Molecular Therapy Nucleic Acids

Volumn 3, Issue , 2014, Pages e157-

  Koller, Ulrich ^a   Wally, Verena ^a   Bauer, Johann W ^a   Murauer, Eva M ^a  

^a PARACELSUS MEDICAL UNIVERSITY   (Austria)

Author keywords

[No Author keywords available]

Indexed keywords

ANTISENSE OLIGONUCLEOTIDE; COMPLEMENTARY DNA; MESSENGER RNA; MESSENGER RNA PRECURSOR;

DUCHENNE MUSCULAR DYSTROPHY; FLUORESCENCE ACTIVATED CELL SORTING; GENE EXPRESSION; GENETIC DISORDER; HUMAN; INTRON; LETTER; PRIORITY JOURNAL; RNA SPLICING;

EID: 84920517499     PISSN: None     EISSN: 21622531     Source Type: Journal    
DOI: 10.1038/mtna.2014.10     Document Type: Letter

References (15)

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